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Post Authorisation Safety Study With Raxone in LHON Patients

Completed
Conditions
Leber's Hereditary Optic Neuropathy (LHON)
Interventions
Registration Number
NCT02771379
Lead Sponsor
Santhera Pharmaceuticals
Brief Summary

This study is a multicentre, prospective, non-interventional post-authorisation safety study (PASS) of the clinical outcomes for patients with LHON treated with Raxone®.

No medication will be provided as part of this study. Raxone® will be obtained through commercial channels.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
229
Inclusion Criteria
  • Patient prescribed Raxone® for the treatment of LHON;
  • Patient has completed an Informed Consent Form (ICF) indicating that he/she (or a legally acceptable representative) has been informed of all pertinent aspects of the study and has agreed to participate in the study;
  • Patient is not participating in any interventional study.
Exclusion Criteria
  • No explicit exclusion criteria exist to avoid selection bias and to allow for documentation of routine clinical practice.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Patients who are treated with Raxone®Idebenone-
Primary Outcome Measures
NameTimeMethod
Long-term safety profile of Raxone® in the treatment of patients with LHON when used under conditions of routine clinical care.up to 5 years

Safety will be assessed by the collection and analysis of adverse events of special interest (AESIs), frequency and nature of AEs and serious adverse events (SAEs), adverse drug reactions (ADRs) and serious adverse drug reactions (SADRs)

Secondary Outcome Measures
NameTimeMethod
Long-term effectiveness of Raxone® in the treatment of patients with LHON when used under conditions of routine clinical careup to 5 years

According to the Summary of Product Characteristics (SmPC) a patient's vision should be continually monitored therefore effectiveness will be assessed by measuring on-therapy changes in patients' visual acuity (VA), visual fields (VF), colour contrast sensitivity and Retinal Nerve Fibre Layer thickness (RNFL) where available.

Trial Locations

Locations (26)

Ospedale San Raffaele

🇮🇹

Milano, Italy

Universitaetsklinikum Essen

🇩🇪

Essen, Germany

CHU Amiens - Centre Saint Victor

🇫🇷

Amiens, Somme, France

CHU de Nîmes - Hôpital Carémeau

🇫🇷

Nîmes, Gard, France

Universitaetsklinikum Graz

🇦🇹

Graz, Austria

Hopital Roger Salengro - CHU Lille

🇫🇷

Lille, Nord, France

Azienda Ospedaliera S. Camillo Forlanini

🇮🇹

Rome, Italy

Centre Hospitalier National d'Ophtalmologie (CHNO) des Quinze-Vingts

🇫🇷

Paris, France

Hopital Neurologique Pierre Wertheimer

🇫🇷

Lyon Cedex, France

Medical University of Vienna

🇦🇹

Vienna, Austria

Hospices Civils de Lyon

🇫🇷

Lyon, France

CHU Angers - Hôpital Hôtel Dieu

🇫🇷

Angers, Maine Et Loire, France

Hôpital Européen Georges Pompidou

🇫🇷

Paris, Paris Cedex 15, France

Julius Maximilians University

🇩🇪

Wuerzburg, Bavaria, Germany

Fondation Ophtalmologique Adolphe de Rothschild

🇫🇷

Paris, France

Universitaetsklinikum Freiburg

🇩🇪

Freiburg, Germany

Friedrich-Baur-Institut

🇩🇪

Munich, Germany

Universitaetsklinikum Regensburg

🇩🇪

Regensburg, Germany

Athens Ophthalmological Center

🇬🇷

Athens, Greece

Universitaetsklinikum Hamburg-Eppendorf

🇩🇪

Hamburg, Germany

Universitaetsklinikum Heidelberg

🇩🇪

Heidelberg, Germany

Università di Bologna-Clinica Neurologica-Dipartimento di Scienze Neurologiche

🇮🇹

Bologna, Italy

Universitair Medisch Centrum Groningen

🇳🇱

Groningen, Netherlands

Maastricht University Medical Center

🇳🇱

Maastricht, Netherlands

Dietrich-Bonhoeffer-Klinikum Neubrandenburg

🇩🇪

Neubrandenburg, Germany

Universitaetsklinikum Muenster

🇩🇪

Munster, Germany

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