MedPath

Anti-HIV Drug Regimens With or Without Protease Inhibitors and Drug Level Monitoring in HIV Infected Adolescents

Phase 3
Completed
Conditions
HIV Infections
Registration Number
NCT00075907
Lead Sponsor
National Institute of Allergy and Infectious Diseases (NIAID)
Brief Summary

The purpose of this study is to compare the effectiveness of anti-HIV drug regimens with or without a protease inhibitor (PI) in HIV infected adolescents. It will also determine if monitoring drug levels and adjusting the dose as necessary improves the effectiveness of these regimens.

Detailed Description

HIV infected adolescents may have a significantly higher capacity for immune reconstitution following highly active antiretroviral therapy (HAART), compared to adults. Despite this advantage, HIV infected adolescents are often reluctant to get proper medical care, follow through with doctor appointments, and adhere to medication schedules and regimens necessary to keep their infection under control. Lopinavir/ritonavir (LPV/r), a PI, and efavirenz (EFV), a non-nucleoside reverse transcriptase inhibitor (NNRTI), both have long half-lives that make them ideal drugs for the adolescent population, as they are more forgiving if patients miss or sleep through doses. The availability of once-daily dosing of LPV/r will reduce pill burden and offers more flexibility in medication scheduling, also helping to promote treatment adherence among this age group. This study will examine the effectiveness of two HAART regimens, one with the PI LPV/r and two nucleoside reverse transcriptase inhibitors (NRTIs), and the other with the NNRTI EFV and two NRTIs. The efficacy of therapeutic drug monitoring (TDM) and subsequent dose adjustment will also be assessed with both regimens.

Patients will be enrolled in this study for 96 weeks and will be randomly assigned into one of two groups. Group 1 will receive LPV/r and 2 NRTIs. Treatment naive patients in Group 1 will have the option of receiving either once-daily dosing or twice-daily dosing of LPV/r. Treatment experienced patients will receive twice-daily dosing of LPV/r. Patients on once-daily dosing of LPV/r who become intolerant to the regimen will be permitted to switch to twice-daily dosing. Group 2 will receive EFV and 2 NRTIs. All patients will be independently and simultaneously randomly assigned to undergo either TDM with subsequent dose adjustment if necessary or no TDM.

Patient medical history and physical exam will be conducted at screening, entry, Weeks 2, 4, 8, every 8 weeks until Week 48, and every 12 weeks thereafter. Blood collection will occur at all study visits. Self-reported pill counts and MEMS TrackCap readings (on LPV/r and EFV bottles) will be noted at most visits. Patients will be asked to complete adherence questionnaires at selected study visits.

Patients enrolled in PACTG 390 (Different Combination Regimens and Treatment-Switching Guidelines in HIV Infected Children 18 Years of Age and Younger) are encouraged to coenroll simultaneously in this study and in PACTG 219C (Long-Term Effects of HIV Exposure and Infection in Children).

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
240
Inclusion Criteria
  • HIV infected
  • HIV RNA viral load of 10,000 copies/ml or more at screening
  • Weigh 35 kg (77.2 lbs) or more
  • HAART naive or received a single regimen of combination therapy consisting of NRTIs with or without a single PI (except LPV). Patients who received zidovudine monotherapy during pregnancy or used low-dose ritonavir (RTV) as a PI boost are not excluded.
  • For PI experienced patients, have sensitivity to LPV at screening
  • Able to receive, as part of background HAART chosen by their physician, at least one new NRTI that is likely to be active against the patient's virus and unlikely to have cross-resistance with previously used NRTIs
  • Willing to use acceptable forms of contraception
  • Parent or legal guardian willing to provide informed consent, if applicable
Exclusion Criteria
  • Prior receipt of any NNRTI or LPV
  • Require certain medications
  • Grade 3 or 4 clinical or laboratory toxicity, as defined by the Division of AIDS Toxicity Table for Grading Severity of Pediatric Adverse Effects
  • Chemotherapy for active malignancy
  • Acute opportunistic or serious bacterial infection requiring therapy at study entry
  • Investigational treatment within 30 days of study entry
  • Score of 20 or more on Beck Depression Inventory (BDI-II) or suicidal thoughts on BDI-II (score of 2 or 3 on Question 9), regardless of total score
  • Pregnant within 48 hours of starting EFV
  • Breastfeeding

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Primary Outcome Measures
NameTimeMethod
Proportion of patients achieving viral suppression (viral load less than 1,000 copies/ml) at Week 24 and maintaining suppression through Week 48 while remaining on study treatment
Secondary Outcome Measures
NameTimeMethod
HIV viral load at each study visit
Proportion of patients achieving virologic suppression (viral load less than 1,000 copies/ml) at Week 24 and maintaining suppression through Week 96 while remaining on study treatment
adherence measured by MEMS TrackCap Monitors (percentage of doses taken, estimated using the frequency of bottle openings recorded by the MEMS TrackCap Monitors, the MEMS TrackCap Monitor tracking form, and the information recorded on the questionnaires)
adherence measured by patient self-report (binary variable of perfect adherence measured 3 days prior to any study visit reported on the adherence questionnaires and the numbers of visits with reported perfect adherence up to Week 24, 48, and 96)
time to virologic failure (first time viral load is measured to be 1,000 copies/ml or more after Week 24, time before discontinuing study treatment for any reason before Week 96, or time before terminating study for any reason before Week 96)
adherence measured by pill count (percentage of pills taken, determined by counting the pills left in the bottles)
number and severity of symptoms of distress and central nervous system (CNS) side effects
number and severity of all adverse events of Grade 3 or more attributed to study treatment
changes from baseline to Weeks 24, 48, and 96 for percentage and total number of CD19 (B cells), total T cells (CD3 T cells), CD4 (T helper cells), CD8 (cytotoxic T cells), naive CD4 T cells (CD62L/CD45RA/CD4), and activated CD8 T cells (HLADR/CD38/CD8)
HIV resistance mutations at baseline and at time of virologic failure (viral load returning to 1,000 copies/ml or more)
baseline values for percentage and total number of CD19 (B cells), total T cells (CD3 T cells), CD4 (T helper cells), CD8 (cytotoxic T cells), naive CD4 T cells (CD62L/CD45RA/CD4), and activated CD8 T cells (HLADR/CD38/CD8)

Trial Locations

Locations (13)

Children's Med. Ctr. Dallas

🇺🇸

Dallas, Texas, United States

Children's Hosp.

🇺🇸

New Orleans, Louisiana, United States

St. Jude/UTHSC CRS

🇺🇸

Memphis, Tennessee, United States

Usc La Nichd Crs

🇺🇸

Alhambra, California, United States

SUNY Stony Brook NICHD CRS

🇺🇸

Stony Brook, New York, United States

Chicago Children's CRS

🇺🇸

Chicago, Illinois, United States

Bronx-Lebanon Hosp. IMPAACT CRS

🇺🇸

Bronx, New York, United States

Tulane/LSU Maternal/Child CRS

🇺🇸

New Orleans, Louisiana, United States

Children's Hospital of Los Angeles NICHD CRS

🇺🇸

Los Angeles, California, United States

Texas Children's Hosp. CRS

🇺🇸

Houston, Texas, United States

Univ. of Colorado Denver NICHD CRS

🇺🇸

Aurora, Colorado, United States

Long Beach Memorial Med. Ctr., Miller Children's Hosp.

🇺🇸

Long Beach, California, United States

Johns Hopkins Hosp. & Health System - Dept. of Peds., Div. of Infectious Diseases

🇺🇸

Baltimore, Maryland, United States

© Copyright 2025. All Rights Reserved by MedPath