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Adapted Physical Activity Program (APA) for Effort Rehabilitation of Children and Teenagers With Marfan Syndrome

Not Applicable
Not yet recruiting
Conditions
Marfan Syndrome
Interventions
Other: Adapted Physical Activity program
Registration Number
NCT05838235
Lead Sponsor
University Hospital, Toulouse
Brief Summary

This research study aims to evaluate the effect of a 6-month adapted physical activity program (APA) on the endurance capacities (evaluated as the maximum oxygen consumption \[VO2 peak\] on a cardiopulmonary exercise test) of children and adolescents with Marfan syndrome or related.

Detailed Description

Marfan syndrome (MFS) is characterized by the association of multisystem damage related to connective tissue fragility. The risk of aortic dissection has diverted attention from significant musculoskeletal damage despite commonly reported extreme fatigue and pain with impact on the patient's quality of life. In a recent study (Marfanpower, NCT03236571), investigators have observed reduced endurance capacities in children and teenagers with MFS (average VO2 peak at 60% of expected), which were significantly increased by an intensive rehabilitation program. Based on this experience, investigators aim to evaluate the effect of a physical activity program adapted to the daily life of the young patients on their endurance capacities and their quality of life. This program will be set up by an adapted physical activity (APA) coach after a complete assessment, including a cardiopulmonary exercise test with VO2 peak measurement, which will be carried out in the Reference Centre for Marfan syndrome at the Toulouse University Hospital. The VO2 peak evolution will be evaluated after 6 months of program. This is a recognized parameter for the evaluation of endurance and has been validated in children. Investigators hypothesize that the implementation of a physical activity program adapted to the daily life and interests of the child with MFS will efficiently improve endurance, prevent deconditioning and promote long term benefits.

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
30
Inclusion Criteria
  • Genetically confirmed Marfan syndrome or related syndrome
  • Girl or boy aged 7 to 17
  • Informed and written consent signed by at least one of the two holders of parental authority
  • Patient affiliated to a social security scheme or equivalent
Exclusion Criteria
  • Cardiac contraindications to the APA program:

    • Severe aortic dilation (aortic diameter > 45 mm)
    • and/or left ventricular failure (left ventricular ejection fraction <45%)
    • and/or severe mitral leakage ≥ grade 3
  • Pregnancy

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
6 month adapted physical activityAdapted Physical Activity programThe various assessments will be carried out during 2 visits at 6 months interval as part of the usual follow-up at the Toulouse University Hospital. Standard cardiopulmonary exercise test assessment will be coupled with an assessment by an APA coach on the same day. The APA program built from the initial assessment will be returned to the child and his family during a videoconference. In addition, a regular reassessment and adjustment of this program will be made every 15 days during phone calls by the APA coach.
Primary Outcome Measures
NameTimeMethod
Measurement of maximum enduranceUp to 6 month

maximum oxygen consumption (VO2 peak) during a cardiopulmonary exercise test will be measured

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

CHU Toulouse

🇫🇷

Toulouse, France

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