MedPath

Adapted Physical Activity Program (APA) for Effort Rehabilitation of Children and Teenagers With Osteogenesis Imperfecta

Not Applicable
Recruiting
Conditions
Osteogenesis Imperfecta
Interventions
Other: Adapted Physical Activity program
Registration Number
NCT05927389
Lead Sponsor
University Hospital, Toulouse
Brief Summary

This research study aims to evaluate the effect of a 6-month adapted physical activity program (APA) on the endurance capacities (evaluated as the maximum oxygen consumption \[VO2 peak\]) of children and adolescents with Osteogenesis Imperfecta.

Detailed Description

Osteogenesis Imperfecta (OI) is a rare genetic disease characterised mainly by bone fragility, decreased bone mass and a susceptibility to fractures of varying severity. Different forms have been described according to the severity of the bone manifestations. Although it is a genetically heterogeneous disease, approximately 90% of OI patients have a mutation in the gene encoding gene encoding type 1 collagen, a major component of the extracellular matrix.

Chronic fatigue and decreased physical endurance are almost constant complaints of patients with OI (more than 95% according to some studies), which impacts the activities of daily living and quality of life of these patients. The causes of this decrease in endurance are multifactorial involving prolonged immobilisation secondary to fractures, chronic osteoarticular pain, but also primary muscle damage.

Mechanography studies carried out in children with OI have shown a significant deficit in muscle function in terms of both strength and power.

In healthy adults, physical inactivity is an important predictor of feeling of tired. In addition, in some chronic diseases (such as multiple sclerosis, rheumatoid arthritis or systemic lupus erythematosus), physical activity and training have been shown to be effective in improving muscle strength and functional capacity as well as fatigue and quality of life. In OI, it has been reported that physical activity improves muscle function and bone mass. Patients with OI should therefore benefit from a regular exercise programme taking into account their risk of fracture.

This study aims to evaluate the effect of a life-skills physical activity (LSPA) programme on the endurance capacities and quality of life of children and adolescents with OI.

The VO2 peak evolution will be evaluated after 6 months of program. This is a recognized parameter for the evaluation of endurance and has been validated in children. The hypothesis of this study is that the implementation of a physical activity program adapted to the daily life and interests of the child with OI will efficiently improve endurance, prevent deconditioning and promote long term benefits.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
30
Inclusion Criteria
  • Diagnosed Osteogenesis Imperfecta
  • Informed and written consent signed by at least one of the two holders of parental authority
  • Patient affiliated to a social security scheme or equivalent
Exclusion Criteria
  • Non-walking children (unable to perform the effort test)
  • Pregnant or breastfeeding
  • Participation in other interventional research

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Experimental group: 6 months APA programAdapted Physical Activity programThe various assessments will be carried out during 2 visits at 6 months interval as part of the usual follow-up at the "Constitutional Bone Diseases" unit at the Toulouse University Hospital. The APA program built from the initial assessment will be returned to the child and his family during a videoconference. In addition, a regular reassessment and adjustment of this program will be made every 15 days during phone calls by the APA coach.
Primary Outcome Measures
NameTimeMethod
Change from Baseline maximum endurance capacity at 6 monthsChange from Baseline to 6 months

Maximum oxygen consumption (VO2 peak) during an exercise test will be measured

Secondary Outcome Measures
NameTimeMethod
Change from baseline quality of life questionnaire score at 6 monthsChange from Baseline to 6 months

Osteogenesis Imperfecta Specific Quality of Life Questionnaire (OIQoL). Total scores are based on a 0-100 scale, where a high score represents better quality of life

Change from baseline number of steps at 6 monthsChange from Baseline to 6 months

6-minute walk test (6MWT) assessed by connected watch

Change from baseline Weight at 6 monthsChange from Baseline to 6 months

Body Mass Index

Trial Locations

Locations (2)

CHU Montpellier Hôpital Arnaud de Villeneuve

🇫🇷

Montpellier, France

CHU Toulouse

🇫🇷

Toulouse, France

© Copyright 2025. All Rights Reserved by MedPath