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Sofosbuvir in Combination With Pegylated Interferon and Ribavirin and in Treatment-Naive Hepatitis C-infected Patients

Phase 2
Completed
Conditions
Hepatitis C Virus
Interventions
Drug: Placebo to match sofosbuvir
Registration Number
NCT01188772
Lead Sponsor
Gilead Sciences
Brief Summary

Genotype 1: Participants with genotype 1 hepatitis C (HCV) infection were randomized to receive sofosbuvir (GS-7977; PSI-7977) 200 mg or 400 mg, or matching placebo, plus pegylated interferon alfa 2a (PEG) and ribavirin (RBV) for 12 weeks, followed by PEG+RBV for an up to an additional 36 weeks. Randomization was stratified by IL28B status (CC, CT, TT) and HCV RNA level (\< 800,000 IU/ml or ≥ 800,000 IU/ml) at baseline. Participants were randomized in a 2:2:1 manner; those who achieved an extended rapid virologic response (eRVR) (HCV RNA \< lower limit of detection \[15 IU/mL\] from Weeks 4 through 12) received an additional 12 weeks of PEG+RBV. Subjects not achieving eRVR received an additional 36 weeks of PEG+RBV.

Genotype 2 and 3: Participants with genotype 2 or 3 hepatitis C (HCV) received sofosbuvir 400 mg plus PEG+RBV for 12 weeks.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
147
Inclusion Criteria
  • Males or females aged 18 to 70 years, inclusive, at screening
  • Documented chronic genotype 1, 2, or 3 HCV infection
  • No previous treatment with HCV antiviral mediations
  • Body mass index (BMI) of greater than 18 kg/m2, but not exceeding 36 kg/m2.
  • Liver biopsy obtained within 3 years prior to the Day 1 visit, with a fibrosis classification of non-cirrhotic as judged by a local pathologist
  • Willing to refrain from beginning any new exercise regimens during the first 3 months of the study
  • Fasting blood glucose ≤ 300 mg/dl and/or glycosylated hemoglobin (HbA1c) ≤ 8
  • History of hypertension only if managed effectively on a stable regimen of two or fewer antihypertensives for at least three (3) months prior to screening
Exclusion Criteria
  • Females who were breastfeeding
  • Males and females of reproductive potential who are unwilling to use an "effective", protocol-specified method(s) of contraception during the study
  • Positive test at Screening for HBsAg, anti-HBc IgM Ab, or anti-HIV Ab.
  • History of any other clinically significant chronic liver disease
  • Treatment with herbal/natural remedies with antiviral activity within 30 days prior to baseline.
  • Significant history of immunologically mediated disease, cardiac or pulmonary disease, seizure disorder or anticonvulsant use
  • History of ascites, variceal hemorrhage, hepatic encephalopathy, or conditions consistent with decompensated liver disease
  • Use of medications associated with QT prolongation within 30 days prior to dosing
  • Screening electrocardiogram (ECG) QTc value greater than 450 ms and/or clinically significant ECG findings
  • Personal or family history of Torsade de pointes.
  • Positive results for drugs of abuse test at screening
  • Abnormal hematological and biochemical parameters, including alanine aminotransferase (ALT) or aspartate aminotransferase (AST) ≥ 5 times the upper limit of the normal range (ULN)
  • History of major organ transplantation with an existing functional graft
  • History of uncontrolled thyroid disease or abnormal thyroid-stimulating hormone (TSH) levels at screening
  • Clinically significant drug allergy to nucleoside/nucleotide analogs
  • History or current evidence of psychiatric illness, immunologic disorder, pulmonary, cardiac disease, seizure disorder, cancer or history of malignancy that in the opinion of the investigator makes the patient unsuitable for the study
  • History of systemic antineoplastic or immunomodulatory treatment within 6 months prior to dosing, or the expectation of such treatment during the study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo (Genotype 1)Placebo to match sofosbuvirParticipants with genotype 1 HCV infection were randomized to receive placebo to match sofosbuvir (4 tablets)+PEG+RBV for 12 weeks followed by PEG+RBV for up to an additional 36 weeks.
Sofosbuvir 200 mg (Genotype 1)Placebo to match sofosbuvirParticipants with genotype 1 HCV infection were randomized to receive sofosbuvir 200 mg (2 x 100 mg tablets)+placebo to match sofosbuvir (2 tablets)+PEG+RBV for 12 weeks followed by PEG+RBV for up to an additional 36 weeks.
Sofosbuvir 200 mg (Genotype 1)SofosbuvirParticipants with genotype 1 HCV infection were randomized to receive sofosbuvir 200 mg (2 x 100 mg tablets)+placebo to match sofosbuvir (2 tablets)+PEG+RBV for 12 weeks followed by PEG+RBV for up to an additional 36 weeks.
Sofosbuvir 200 mg (Genotype 1)PEGParticipants with genotype 1 HCV infection were randomized to receive sofosbuvir 200 mg (2 x 100 mg tablets)+placebo to match sofosbuvir (2 tablets)+PEG+RBV for 12 weeks followed by PEG+RBV for up to an additional 36 weeks.
Sofosbuvir 200 mg (Genotype 1)RBVParticipants with genotype 1 HCV infection were randomized to receive sofosbuvir 200 mg (2 x 100 mg tablets)+placebo to match sofosbuvir (2 tablets)+PEG+RBV for 12 weeks followed by PEG+RBV for up to an additional 36 weeks.
Sofosbuvir 400 mg (Genotype 1)PEGParticipants with genotype 1 HCV infection were randomized to receive sofosbuvir 400 mg (4 x 100 mg tablets)+PEG+RBV for 12 weeks followed by PEG+RBV for up to an additional 36 weeks.
Sofosbuvir 400 mg (Genotype 1)RBVParticipants with genotype 1 HCV infection were randomized to receive sofosbuvir 400 mg (4 x 100 mg tablets)+PEG+RBV for 12 weeks followed by PEG+RBV for up to an additional 36 weeks.
Placebo (Genotype 1)PEGParticipants with genotype 1 HCV infection were randomized to receive placebo to match sofosbuvir (4 tablets)+PEG+RBV for 12 weeks followed by PEG+RBV for up to an additional 36 weeks.
Placebo (Genotype 1)RBVParticipants with genotype 1 HCV infection were randomized to receive placebo to match sofosbuvir (4 tablets)+PEG+RBV for 12 weeks followed by PEG+RBV for up to an additional 36 weeks.
Sofosbuvir 400 mg (Genotype 2/3)SofosbuvirParticipants with genotype 2 or 3 HCV infection received sofosbuvir 400 mg (4 x 100 mg tablets)+PEG+RBV for 12 weeks.
Sofosbuvir 400 mg (Genotype 2/3)PEGParticipants with genotype 2 or 3 HCV infection received sofosbuvir 400 mg (4 x 100 mg tablets)+PEG+RBV for 12 weeks.
Sofosbuvir 400 mg (Genotype 2/3)RBVParticipants with genotype 2 or 3 HCV infection received sofosbuvir 400 mg (4 x 100 mg tablets)+PEG+RBV for 12 weeks.
Primary Outcome Measures
NameTimeMethod
Percentage of Participants Who Experienced Adverse Events During the Sofosbuvir Treatment PeriodBaseline to Week 12 plus 30 days

Adverse events (AEs) occurring during the sofosbuvir treatment period and for 30 days following the last dose of sofosbuvir were summarized across the participant population. A participant was counted once if they had a qualifying event.

Secondary Outcome Measures
NameTimeMethod
Change in HCV RNA From Baseline to Week 12Baseline to Week 12
Percentage of Participants With Rapid Virologic Response at Week 4Week 4

Rapid virologic response was defined as HCV RNA below the limit of detection (\< 15 IU/mL) at Week 4 (Day 29)

Percentage of Participants With Complete Early Virologic Response at Week 12Week 12

Complete early virologic response was defined as HCV RNA below the limit of detection (\< 15 IU/mL) at Week 12

Percentage of Participants With Extended Rapid Virologic ResponseWeek 4 to Week 12

Extended rapid virologic response was defined as HCV RNA below the limit of detection (\< 15 IU/mL) at Week 4 (Day 29) which was maintained through Week 12.

Percentage of Participants With Virologic Response at the End of TreatmentWeek 48 (genotype 1) or Week 12 (genotype 2/3)

End-of-treatment virologic response was defined as HCV RNA below the limit of detection (\< 15 IU/mL) at the last on-treatment visit.

Percentage of Participants With Sustained Virologic Response at Post-treatment Week 12 (SVR12) and 24 (SVR24)Post-treatment Weeks 12 and 24

SVR12 and SVR24 were defined as HCV RNA below the limit of detection (\< 15 IU/mL) at post-treatment Weeks 12 and 24, respectively.

Plasma Pharmacokinetics of GS-331007 (Cmax at Day 8)1, 2, 4, 8, and 12 hours postdose

The pharmacokinetics of sofosbuvir metabolite GS-331007 were analyzed as the maximum observed concentration of drug in plasma (Cmax) at Day 8. Blood samples were collected at 1, 2, and 4 hours postdose for all participants, and at 8 and 12 hours postdose for participants enrolled at selected sites.

Plasma Pharmacokinetics of GS-331007 (Cmax at Day 15)1, 2, 4, 8, and 12 hours postdose

The pharmacokinetics of sofosbuvir metabolite GS-331007 were analyzed as the Cmax at Day 15. Blood samples were collected at 1, 2, and 4 hours postdose for all participants, and at 8 and 12 hours postdose for participants enrolled at selected sites.

Plasma Pharmacokinetics of GS-331007 (Cmax at Day 29)1, 2, 4, 8, and 12 hours postdose

The pharmacokinetics of sofosbuvir metabolite GS-331007 were analyzed as the Cmax at Day 29. Blood samples were collected at 1, 2, and 4 hours postdose for all participants, and at 8 and 12 hours postdose for participants enrolled at selected sites.

Plasma Pharmacokinetics of GS-331007 (AUCtau at Day 8)1, 2, 4, 8, and 12 hours postdose

The pharmacokinetics of sofosbuvir metabolite GS-331007 were analyzed as the the area under the plasma concentration versus time curve over the dosing interval (AUCtau) at Day 8. Blood samples were collected at 1, 2, and 4 hours postdose for all participants, and at 8 and 12 hours postdose for participants enrolled at selected sites.

Plasma Pharmacokinetics of GS-331007 (AUCtau at Day 15)1, 2, 4, 8, and 12 hours postdose

The pharmacokinetics of sofosbuvir metabolite GS-331007 were analyzed as the the area under the plasma concentration versus time curve over the dosing interval (AUCtau) at Day 15. Blood samples were collected at 1, 2, and 4 hours postdose for all participants, and at 8 and 12 hours postdose for participants enrolled at selected sites.

Plasma Pharmacokinetics of GS-331007 (AUCtau at Day 29)1, 2, 4, 8, and 12 hours postdose

The pharmacokinetics of sofosbuvir metabolite GS-331007 were analyzed as the the area under the plasma concentration versus time curve over the dosing interval (AUCtau) at Day 29. Blood samples were collected at 1, 2, and 4 hours postdose for all participants, and at 8 and 12 hours postdose for participants enrolled at selected sites.

Percentage of Participants Who Developed Resistance to SofosbuvirBaseline to Week 12

Resistance monitoring was completed in all subjects who received sofosbuvir and who had non-response, viral rebound, virologic breakthrough, or HCV RNA plateaus between Day 0 and Week 24.

Trial Locations

Locations (23)

University of Chicago

🇺🇸

Chicago, Illinois, United States

Dr. Bruce Bacon

🇺🇸

St. Louis, Missouri, United States

Cedars Sinai Medical Center

🇺🇸

Los Angeles, California, United States

Gastrointestinal Specialists of Georgia

🇺🇸

Marietta, Georgia, United States

North Shore University Hospital

🇺🇸

Manhasset, New York, United States

Dr. David Nelson

🇺🇸

Gainesville, Florida, United States

Orlando Immunology Center

🇺🇸

Orlando, Florida, United States

Kansas City Gastroenterology and Hepatology

🇺🇸

Kansas City, Missouri, United States

Dr. Mark Sulkowski

🇺🇸

Lutherville, Maryland, United States

Dr. Ira Jacobson

🇺🇸

New York, New York, United States

Dr. Raj Reddy

🇺🇸

Philadelphia, Pennsylvania, United States

Columbia Gastroenterology and Liver Associates

🇺🇸

Columbia, South Carolina, United States

Mount Sinai School of Medicine

🇺🇸

New York, New York, United States

Liver Research Center Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

Dr. Eric Lawitz

🇺🇸

San Antonio, Texas, United States

Alabama Liver and Digestive Specialists

🇺🇸

Montgomery, Alabama, United States

Advanced Clinical Research Institute

🇺🇸

Anaheim, California, United States

Dr. Jay Lalezari

🇺🇸

San Francisco, California, United States

Dr. Natalie Bzowej

🇺🇸

San Francisco, California, United States

Dr. Jama Darling

🇺🇸

Chapel Hill, North Carolina, United States

Digestive Disease Institute Virginia Mason Medical Center

🇺🇸

Seattle, Washington, United States

Fundacion de Investigacion de Diego

🇵🇷

Santurce, Puerto Rico

SCTI Research Foundation

🇺🇸

Coronado, California, United States

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