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Screening Strategies for People With a High Risk of Anal Cancer

Not Applicable
Recruiting
Conditions
Neoplasms
HPV-Related Anal Squamous Cell Carcinoma
Interventions
Diagnostic Test: HRA + Biopsy
Diagnostic Test: Anal Cytology
Diagnostic Test: Genotyping of anal hrHPV infection
Diagnostic Test: CINtec®PLUS
Registration Number
NCT06628570
Lead Sponsor
Lisa Flowers
Brief Summary

The goal of the proposed research is to 1) examine the performance of emerging screening methods for anal high-grade squamous intraepithelial lesion (aHSIL), a precancerous condition of anal cancer, among minorities with a high risk of anal cancer and 2) characterize DNA methylation, immunologic response, and social determinants associated with aHSIL.

Detailed Description

Anal cancer, caused by persistent infection with high-risk human papillomavirus (hrHPV), is typically preceded by anal high-grade squamous intraepithelial lesions (aHSIL). The incidence and mortality of advanced anal cancer has been increasing in the U.S., with the greatest burden of disease and mortality in individuals living with HIV. The study is important because the incidence of anal cancer is particularly high among certain groups; health disparity further contributes to this high risk among minorities. Findings will provide much-needed evidence for anal cancer screening strategies to reduce health disparities, improve screening outcomes, and decrease the incidence of anal cancer among high-risk minorities. The study population includes Black or Latinx, males - men having sex with men (MSM) only - and females with a known history of high-grade lower genital tract neoplasia.

The study procedures include filling out self-reported questionnaires and collecting biosamples for study-related assays. HRA is part of the standard clinic procedure for this group of participants.

Collected biosamples will be banked for future research use. In-person or remote signed consent may occur for the study.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
500
Inclusion Criteria
  • 30 years of age and older
  • Identifies as Black or Latinx,
  • Males (MSM only) and females with a known history of high-grade lower genital tract neoplasia (LGTN), Zubrod Performance Status of 0-2;
  • Women with Human Papillomavirus (HPV) related cervical, vaginal, or vulvar high-grade precancer or cancer
Exclusion Criteria
  • Patients treated for aHSIL less than 6 months before screening,
  • History of anal cancer and pregnant women.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
HIV Negative MSM with high grade LGTNAnal CytologyAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Positive MSM with high grade LGTNHRA + BiopsyAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Positive MSM with high grade LGTNAnal CytologyAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Positive MSM with high grade LGTNGenotyping of anal hrHPV infectionAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Negative women with high grade LGTNAnal CytologyAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Positive MSM with high grade LGTNCINtec®PLUSAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Negative MSM with high grade LGTNHRA + BiopsyAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Negative MSM with high grade LGTNGenotyping of anal hrHPV infectionAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Negative MSM with high grade LGTNCINtec®PLUSAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Positive women with high grade LGTNHRA + BiopsyAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Positive women with high grade LGTNAnal CytologyAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Positive women with high grade LGTNGenotyping of anal hrHPV infectionAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Positive women with high grade LGTNCINtec®PLUSAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Negative women with high grade LGTNHRA + BiopsyAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Negative women with high grade LGTNGenotyping of anal hrHPV infectionAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
HIV Negative women with high grade LGTNCINtec®PLUSAt each study visit, participants will receive a digital anorectal examination followed by HRA, with directed biopsies of suspicious lesions. An HRA-certified physician will collect anal swabs and HRA-directed biopsies for histological confirmation of disease and biomarker assays.
Primary Outcome Measures
NameTimeMethod
Specificity and Sensitivity of screening markersBaseline

Sensitivity and specificity will be calculated for each of the proposed screening markers separately and a combination of two and three markers for the detection of aHSIL at baseline. The combination of the two and three markers of primary interest includes CINtec®PLUS +hrHPV, CINtec®PLUS+anal cytology, hrHPV+anal cytology, and CINtec®PLUS+hrHPV+anal cytology. The analysis will be performed for the four high-risk groups together and stratified by the four high-risk categories.

Secondary Outcome Measures
NameTimeMethod
DNA methylation markersBaseline, 1 year, 2 years

In these models, aHSIL status at baseline will be considered as the response, and each anal DNA methylation marker will be the predictor. Separate models will be performed for each methylation marker (ZNF582, ASCL1, ZIC1, SST, LHX8, WDR17, and ST6GALNAC5)

Anal immune modulationsBaseline, 1 year, 2 years

High-risk HPV 16 persistent patients (N=10) vs. patients with no HPV at least two consecutive times (N=10). Each of the groups will also include aHSIL+ (N=5) vs. \<aLSIL (N=5).

aHSIL prevalenceBaseline

The prevalence of HSIL will be estimated as the proportion of participants who are HRA positive for HSIL at entry and its 95% confidence interval. Logistic regression analysis will be used to evaluate the association of potential risk factors with diagnosis of HSIL.

aHSIL clearance1 year, 2 years

Only people treated with aHSIL will be used for the clearance analysis. Clearance (HRA biopsy-proven) will be defined as no detectable aHSIL at the immediate one-year (for those with baseline aHSIL) or two-year (for those with newly diagnosed aHSIL cases at the one-year visit) follow-up visit after aHSIL treatment.

Inflammatory Markers (Il-1RA, IL1β, IL6, IL6sr, TNF-α, and IL-10)Baseline, 1 year, 2 years

Anal swab concentrations of inflammatory markers (IL1ra, IL1β, IL6, IL6sr, TNF-α, and IL-10) will be determined using multiplex assays (Meso Scale Discovery, Rockville, MD) according to the manufacturer's protocol. All samples will be run in duplicates, and mean intra- and inter-assay CVs will be calculated and expected to be \<10%. These inflammatory markers have been reliably found to be elevated in inflammatory-associated diseases including anal inflammation.

Inflammatory Markers (sTNFR2 and interferon (IFN)-γ)Baseline, 1 year, 2 years

Anal swab concentrations of inflammatory markers of inflammatory markers (sTNFR2 and interferon (IFN)-γ) will be determined using multiplex assays (Meso Scale Discovery, Rockville, MD) according to the manufacturer's protocol.

Inflammatory Marker (CRP)Baseline, 1 year, 2 years

Anal swab concentrations of inflammatory markers (CRP) will be determined using multiplex assays (Meso Scale Discovery, Rockville, MD) according to the manufacturer's protocol. All samples will be run in duplicates, and mean intra- and inter-assay CVs will be calculated and expected to be \<10%.

Trial Locations

Locations (4)

University of Miami Miller School of Medicine-Sylvester Cancer Center

🇺🇸

Miami, Florida, United States

Grady Memorial Hospital

🇺🇸

Atlanta, Georgia, United States

The Ponce Center

🇺🇸

Atlanta, Georgia, United States

University of Miami School of Medicine at Jackson Memorial Hospital (JMH)

🇺🇸

Miami, Florida, United States

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