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DOTAREM Pharmacokinetics and Safety Study in Pediatric Subjects Aged < 2 Years

Phase 4
Completed
Conditions
Magnetic Resonance Imaging
Interventions
Registration Number
NCT02411201
Lead Sponsor
Guerbet
Brief Summary

The main purpose of the study is to evaluate the pharmacokinetics of DOTAREM® in the body of children aged less than 2 years thanks to several blood samples (3 ml in total) taken following the administration of DOTAREM®.

DOTAREM® is a contrast agent commonly used for enhancement of Magnetic Resonance Imaging (MRI) to potentially improve the quality of the images and help the diagnosis. Children aged less than 2 years scheduled to undergo routine gadolinium-enhanced MRI of any body region may take part in the study. In this case they will receive DOTAREM®, a solution injected at the standard dose of 0.2mL/kg (0.1 mmol/kg) of body weight.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
51
Inclusion Criteria
  • Pediatric subject aged <2 years (term newborn infants to toddlers 23 months of age inclusive). Term is defined as ≥37 weeks of amenorrhea
  • Subject is scheduled to undergo routine gadolinium-enhanced MRI of any body region (e.g. CNS, cardiac) at the dose of 0.1 mmol/kg BW (0.2 mL/kg BW)
  • Subject with normal renal function for its age, estimated glomerular filtration rate calculated based on the Schwartz formula
Exclusion Criteria
  • Subject planned for intervention (e.g. surgery) between the screening visit and up to 24 hours after DOTAREM injection
  • Subject whose preceding or subsequent treatment to DOTAREM injection (e.g., blood loss or receiving blood, treatment with diuretics, etc...) would alter DOTAREM pharmacokinetics parameters
  • Subject with subsequent planned treatment after DOTAREM injection that would prevent obtaining the required blood samples (e.g., emergency surgery, etc...)
  • Subject with a history of a bleeding disorder
  • Subject with severe liver disease (Child's Pugh Classification B or greater or serum direct bilirubin greater than 0.3 mg/dL, age adjusted)
  • Subject with electrolyte or fluid imbalance that presents undue risk
  • Subject undergoing a change in chemotherapy within 48 hours prior to and up to 24 hours after DOTAREM injection
  • Subject who received or will receive any other contrast agent within 72 hours prior to DOTAREM injection or up to 24 hours after DOTAREM injection
  • Subject with contraindication for MRI such as iron metal implants (e.g. aneurysm clips)
  • Subject with history of anaphylactoid or anaphylactic reaction to any allergen including drugs and contrast agents
  • Subject having participated within 30 days in a clinical study involving an investigational drug or device
  • Subject planned to participate simultaneously to another clinical study

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
DOTAREMDOTAREM-
Primary Outcome Measures
NameTimeMethod
Rate Constant of the Terminal Phase of DOTAREMBlood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Rate constant of the terminal phase was determined from typical and individual DOTAREM concentration-time profiles.

Total Clearance of DOTAREM From PlasmaBlood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Total clearance was determined from typical and individual DOTAREM concentration-time profiles.

Area Under the Curve of DOTAREM in PlasmaBlood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Area under the curve was determined from typical and individual DOTAREM concentration-time profiles.

Terminal Elimination Half-life of DOTAREM From PlasmaBlood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Terminal elimination half-life was determined from typical and individual DOTAREM concentration-time profiles.

Volume of Distribution of DOTAREM at Steady StateBlood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Volume of distribution at steady state was determined from typical and individual DOTAREM concentration-time profiles.

Secondary Outcome Measures
NameTimeMethod
Simulated Plasma Concentration of DOTAREMat 10 and 20 min post-injection

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method.

MRI Lesion Visualization at Subject LevelPre-injection and post-injection (estimated between 5 and 20 minutes after injection)

Lesion visualization was assessed on up to five most representative lesions per subject based on scoring of 3 co-endpoints:

* border delineation (based on a 3-point scale where 1=none; 2=moderate and 3=clear and complete)

* internal morphology (based on a 3-point scale where 1=poorly visible; 2=moderately visible and 3=sufficiently visible)

* contrast enhancement (based on a 3-point scale where 1=none; 2=weak and 3=clear and bright)

For each co-endpoint, a sum of scores was calculated at subject level as follows: sum of scores = score of the lesion 1 (+ score of the lesion 2 + score of the lesion 3 + score of the lesion 4 + score of the lesion 5, when applicable)

Trial Locations

Locations (9)

CHU

🇫🇷

Bordeaux, France

Uniwersytecki Szpital Dziecięcy w Lublinie

🇵🇱

Lublin, Poland

Hôpital de Hautepierre

🇫🇷

Strasbourg, France

CHRU

🇫🇷

Lille, France

Department of Molecular and Neurological Clinical and Research Center

🇭🇺

Budapest, Hungary

Borsod-Abaúj-Zemplén University County Hospital

🇭🇺

Miskolc, Hungary

Landes-Frauen-und Kinderklinik Linz

🇦🇹

Linz, Austria

University of Debrecen Medical Center

🇭🇺

Debrecen, Hungary

Instytut Pomnik -Centrum Zdrowia Dziecka

🇵🇱

Warszawa, Poland

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