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Pre-operative Immunotherapy in Stage II-III Urothelial Cancer

Phase 1
Completed
Conditions
Urothelial Carcinoma
Interventions
Registration Number
NCT04871594
Lead Sponsor
The Netherlands Cancer Institute
Brief Summary

This is a phase 1b feasibility study of pre-operative immunotherapy in PD-L1 positive resectable stage II-III urothelial cancer patients. This study can be adapted or expanded based on the results obtained.

Detailed Description

This is a phase 1b feasibility study of pre-operative immunotherapy in PD-L1 positive resectable stage II-III urothelial cancer patients.

Urothelial cancer patients will be included that are diagnosed with either:

* cT2-4aN0M0 OR

* cT1-4aN1-3M0

PD-L1 status will be determined. When PD-L1 CPS is ≥10%, patients will be treated with three cycles nivolumab 240 mg, q3wk, on day 1, 22, 43.

The primary endpoint is feasibility of pre-operative nivolumab in PD-L1 positive resectable stage II-III urothelial cancer patients.

After surgery, patients attend study visits at day 8 and at day 29. Their final study visit for physical examination and laboratory testing is at day 57 (+/- 7 days), which is scheduled to anticipate late-onset adverse events. 90 days postoperative, surgical complications according to the Clavien-dindo classification will be evaluated. Thereafter, patients will be followed according to standard clinical guidelines. Tumor biopsies/material preservation is required at baseline and during surgery.

Main secondary endpoints are:

* To identify pathological complete response rates of nivolumab in PD-L1 positive resectable stage II-III urothelial cancer patients

* To describe immune-related grade 3/4 and all grade toxicities

* To describe RFS and OS

* Translational: Effects of immunotherapy on the tumor microenvironment based on RNA signatures and changes in immune infiltrates between baseline and resection.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
15
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Nivolumab monotherapyNivolumabDay 1: nivolumab 240 mg Day 22: nivolumab 240 mg Day 43: nivolumab 240 mg
Primary Outcome Measures
NameTimeMethod
Feasibility of pre-operative nivolumab in PD-L1 positive resectable stage II-III urothelial cancer patientsAt 12 weeks

Percentage of patients that underwent surgery within 12 weeks after study start will be assessed

Secondary Outcome Measures
NameTimeMethod
Pathological complete response rates of nivolumab in PD-L1 positive resectable stage II-III urothelial cancer patientsAt 12 weeks

Efficacy of nivolumab in PD-L1 positive resectable stage II-III urothelial cancer patients, assessed by the percentage of pathological complete response rate after cystectomy according to pathological response criteria

Toxicity of pre-operative nivolumabFrom first inusion untill 100 days after the last infusion with nivolumab

All grade toxicities and immune-related toxicity of grade 3-4

Relapse free survival and overall survivalFrom first infusion untill 3 years postoperative

During follow-up, every 6 months untill 3 years postoperative, relapse free survival will be evaluated. Overall survival will be evaluated by phone calls

Monitor peri-surgical complicationsFrom surgery untill 90 days after surgery

Peri-operative complications and morbidity will be graded according to the Clavien-Dindo classification

Translational: effects of nivolumab on the tumor microenvironmentAt 12 weeks

Resistance mechanisms are explored by comparing immune (cell) infiltrates in responders and nonresponders in pre- and post treatment tissue \[Multiplex immunohistochemistry, RNA seq\]

Trial Locations

Locations (2)

Radboud Universitair Medisch Centrum

🇳🇱

Nijmegen, Netherlands

Antoni van Leeuwenhoek ziekenhuis

🇳🇱

Amsterdam, Netherlands

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