MedPath

Rapid Infusion of Immune Globulin Intravenous (Human) In Primary Immunodeficiency Patients

Phase 3
Completed
Conditions
Immunologic Deficiency Syndrome
Agammaglobulinemia
Severe Combined Immunodeficiency
Wiskott-Aldrich Syndrome
Common Variable Immunodeficiency
Interventions
Drug: Immune Globulin Intravenous [Human], 10% Caprylate/Chromatography Purified
Drug: Dextrose, 5% in Water
Registration Number
NCT00220766
Lead Sponsor
Grifols Therapeutics LLC
Brief Summary

The objective of this study is to determine if the safety and tolerability of Immune Globulin Intravenous (Human), 10% caprylate/chromatography (IGIV-C)purified is similar when infused at two different infusion rates. The primary objective is to compare the incidence and severity of all infusion related adverse events when IGIV-C, 10% is administered at a rate of 0.14 mL/kg/min compared to a rate of 0.08 mL/kg/min after a single daily infusion.

Detailed Description

This is a prospective, single blind, randomized, multi-center cross-over trial in patients with Primary Immune Deficiency. Patients with a confirmed diagnosis of primary Immune Deficiency will be treated with two daily infusions given 3-4 weeks apart at the fixed individual IGIV dose regimen (400-600 mg/kg) established prior to entry into the study. Any subject with an established dose in the range of 200-399 mg/kg will be assigned to receive 400 mg/kg during the course of the study during the same dosing schedule established prior to entry into the study.

After a screening period lasting not more than four weeks, patients will be randomized into one of two cross-over groups. Patients randomized to Group 1 will receive their first IGIV-C, 10% dose at a rate of 0.08 mL/kg/min and their second infusion at a rate of 0.14 mL/kg/min, whereas patients randomized to Group 2 will receive IGIV-C, 10% at a rate of 0.14 mL/kg/min on the first infusion day and then 0.08 mL/kg/min on the second infusion day. All patients just prior to each IGIV-C, 10% infusion will receive the same volume of 5% dextrose as calculated for their IGIV-C, 10% infusion and given at a target rate according to the schema below.

Group 1:

* Infusion #1 (Week 0)Dextrose (0.14 mL/kg/min), then IGIV-C, 10% (0.08 mL/kg/min)

* Infusion #2 (Week 3-4)Dextrose (0.08 mL/kg/min), then IGIV-C, 10% (0.14 mL/kg/min)

Group 2:

* Infusion #1 (Week 0)Dextrose (0.08 mL/kg/min), then IGIV-C, 10% (0.14 mL/kg/min)

* Infusion #2 Dextrose (0.14 mL/kg/min), then IGIV-C, 10% (0.08 mL/kg/min)

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
100
Inclusion Criteria
  • Confirmed diagnosis of primary immune deficiency and medical records available for retrospective review for at least 3 months prior to entry into the trial
  • Signed an informed consent written informed consent prior to initiation of any study related procedures
  • Receiving regular infusions of IGIV at a fixed interval and dosage (in the range of 200-600 mg/kg given every 3-4 weeks) for at least three months prior to entry into the trial. Patients who are currently receiving less than 400 mg/kg are eligible for this trial and will be at the time of study enrollment be treated at 400 mg/kg
Exclusion Criteria
  • History or suspicion of significant allergic reaction to intravenous immune globulin, and/or blood products
  • Documented history of selective IgA deficiency (serum level <5.0 mg/dL) and known antibodies to IgA
  • Isolated IgG subclass deficiency with a normal total serum IgG level
  • Other conditions which may interfere with the trial, include the patients demeanor or mental ability to follow instruction.
  • Pretreatment with anti-pyretics or anti-histamines
  • Congestive heart failure (New York Heart Association stage greater than Class II)
  • Renal insufficiency (creatinine >2.5 mg/dL)
  • Conditions whose symptoms and effects could alter protein catabolism and/or IgG utilization (e.g. protein-losing enteropathies, nephrotic syndrome)
  • Pretreatment routinely required to control/ameliorate IGIV infusion-related adverse events (AEs)
  • Any patient who requires IGIV dosing more frequently than every 3 weeks to maintain adequate trough levels
  • Women of child bearing potential who do not practice adequate contraception (i.e. chemical or mechanical methods) and pregnant or lactating females

Study & Design

Study Type
INTERVENTIONAL
Study Design
CROSSOVER
Arm && Interventions
GroupInterventionDescription
Group 1Immune Globulin Intravenous [Human], 10% Caprylate/Chromatography PurifiedInfusion #1 (Week 0)Dextrose (0.14 mL/kg/min), then IGIV-C, 10% (0.08 mL/kg/min) ; Infusion #2 (Week 3-4)Dextrose (0.08 mL/kg/min), then IGIV-C, 10% (0.14 mL/kg/min)
Group 1Dextrose, 5% in WaterInfusion #1 (Week 0)Dextrose (0.14 mL/kg/min), then IGIV-C, 10% (0.08 mL/kg/min) ; Infusion #2 (Week 3-4)Dextrose (0.08 mL/kg/min), then IGIV-C, 10% (0.14 mL/kg/min)
Group 2Immune Globulin Intravenous [Human], 10% Caprylate/Chromatography PurifiedInfusion #1 (Week 0)Dextrose (0.08 mL/kg/min), then IGIV-C, 10% (0.14 mL/kg/min); Infusion #2 Dextrose (0.14 mL/kg/min), then IGIV-C, 10% (0.08 mL/kg/min)
Group 2Dextrose, 5% in WaterInfusion #1 (Week 0)Dextrose (0.08 mL/kg/min), then IGIV-C, 10% (0.14 mL/kg/min); Infusion #2 Dextrose (0.14 mL/kg/min), then IGIV-C, 10% (0.08 mL/kg/min)
Primary Outcome Measures
NameTimeMethod
Infusion related adverse eventswithin 72 hours after infusion
Secondary Outcome Measures
NameTimeMethod
All adverse eventswithin 72 hours after infusion

Trial Locations

Locations (13)

The Clinical Trials Center, Children's Hospital

🇺🇸

New Orleans, Louisiana, United States

National Jewish Medical and Researach Center

🇺🇸

Denver, Colorado, United States

International Center for Interdisciplinary Studies of Immunology

🇺🇸

Washington, District of Columbia, United States

University of South Florida College of Medicine

🇺🇸

St. Petersburg, Florida, United States

Departments of Medicine and Microbiology

🇺🇸

Birmingham, Alabama, United States

Allergy Associates of the Palm Beaches

🇺🇸

North Palm Beach, Florida, United States

Allergy, Asthma, and Immunology

🇺🇸

Omaha, Nebraska, United States

Optimed Research, LLC

🇺🇸

Columbus, Ohio, United States

3031 Hospital Drive Northwest

🇨🇦

Calgary, Alberta, Canada

The Hospital for Sick Children

🇨🇦

Toronto, Ontario, Canada

St. Paul's Hospital

🇨🇦

Vancouver, British Columbia, Canada

Saint Michael's Hospital

🇨🇦

Toronto, Ontario, Canada

University Hospitals of Cleveland

🇺🇸

Cleveland, Ohio, United States

© Copyright 2025. All Rights Reserved by MedPath