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An Open-Labeled, Extended-Use of XERECEPT (hCRF) for Patients in Studies NTI 0302, 0303, or Other Designated Studies

Phase 3
Completed
Conditions
Brain Edema
Brain Tumor
Interventions
Registration Number
NCT00226655
Lead Sponsor
Celtic Pharma Development Services
Brief Summary

The purpose of this study is to examine the long-term safety and tolerability of human corticotropin-releasing factor (hCRF), XERECEPT®, in patients requiring dexamethasone (Decadron) to treat peritumoral brain edema. This open-label, extended-use study is open to all patients who participate in either of the blinded studies, NTI 0302, NTI 0303, or other designated studies, including patients who may have discontinued blinded study medication early but completed the protocol-stipulated follow-up periods.

Detailed Description

XERECEPT® is not a potential treatment for cancer, but may reduce the edema associated with tumors and as a result, decrease neurological symptoms.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
112
Inclusion Criteria
  • Participation in and completion of stipulated final follow-up periods for study NTI 0302, NTI 0303, or other designated studies.
  • Have a Karnofsky Performance of > 50 at Baseline
  • Capable of self-administration of subcutaneous injections twice daily or availability of assistance from caregiver.
  • Ability to provide written informed consent or, if unable to provide, have a legal guardian or representative provide written informed consent.
  • For women of childbearing potential: a negative serum pregnancy test at Baseline
Exclusion Criteria
  • Concurrent enrollment in any investigational drug or device study, other than NTI 0302, NTI 0303, or other designated studies.
  • Systemic steroid use for any indication other than peritumoral brain edema.
  • Use or intended use of dexamethasone as an anti-emetic during study.
  • Clinical signs and symptoms of cerebral herniation.
  • Serious concomitant cardiovascular, pulmonary, renal, gastrointestinal or endocrine metabolic disease which could put the patient at unusual risk during study participation.
  • Confounding previous or concurrent neurological disorders that would interfere with adequate clinical evaluation.
  • Clinically significant head injury or chronic seizure disorder, if the condition results in functional impairment or is likely to interfere with evaluations.(Maintenance anticonvulsant therapy is allowed)
  • Central nervous system (CNS) infection.
  • Pregnancy, breastfeeding and/or refusal to practice birth control while in study, for women of childbearing potential.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
IhCRF [XERECEPT (corticorelin acetate injection)]All patients will receive hCRF (XERECEPT) 2mg/day
Primary Outcome Measures
NameTimeMethod
Long Term Safety and Tolerability of hCRFProspective

Number of patients reporting adverse events

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (32)

Caner Centre of Southwestern Ontario/ Kingston General Hospital

🇨🇦

Kingston, Ontario, Canada

Weill Medical College of Cornell University

🇺🇸

New York, New York, United States

Stanford University Medical Center

🇺🇸

Palo Alto, California, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

University of Wisconsin

🇺🇸

Madison, Wisconsin, United States

Evanston Northwestern Healthcare

🇺🇸

Evanston, Illinois, United States

CancerCare Manitoba

🇨🇦

Winnipeg, Manitoba, Canada

Queen Elizabeth II Health Sciences Center

🇨🇦

Halifax, Nova Scotia, Canada

Dent Neurologic Institute

🇺🇸

Amherst, New York, United States

Ottawa Regional Cancer Center

🇨🇦

Ottawa, Ontario, Canada

Mayo Clinic

🇺🇸

Jacksonville, Florida, United States

Oregon Clinic

🇺🇸

Portland, Oregon, United States

Cross Cancer Institute

🇨🇦

Edmonton, Alberta, Canada

Colorado Neurological Institute Center for Brain & Spinal Tumors

🇺🇸

Englewood, Colorado, United States

Barrow Neurological Institute

🇺🇸

Phoenix, Arizona, United States

Hoag Memorial Hospital Presbyterian

🇺🇸

Newport Beach, California, United States

UC Davis Medical Center, Division of Medical Oncology

🇺🇸

Sacramento, California, United States

UC San Diego Cancer Center

🇺🇸

San Diego, California, United States

University of Colorado Cancer Center

🇺🇸

Aurora, Colorado, United States

Cancer Institute of Orlando

🇺🇸

Orlando, Florida, United States

Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

Winship Cancer Institute, Emory University

🇺🇸

Atlanta, Georgia, United States

Feinberg School of Medicine, Northwestern University

🇺🇸

Chicago, Illinois, United States

Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

Hermelin Brain Tumor Center, Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

University Hematology Oncology Care, LLC

🇺🇸

Cincinnati, Ohio, United States

Virginia Mason Clinic

🇺🇸

Seattle, Washington, United States

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

Good Samaritan Hospital

🇺🇸

Cincinnati, Ohio, United States

The Ohio State University

🇺🇸

Columbus, Ohio, United States

The Moncton Hospital

🇨🇦

Moncton, New Brunswick, Canada

Sunnybrook and Women's College Health Sciences Center

🇨🇦

Toronto, Ontario, Canada

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