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A Study of Pirtobrutinib (LOXO-305) Versus Ibrutinib in Participants With Chronic Lymphocytic Leukemia (CLL)/Small Lymphocytic Lymphoma (SLL)

Phase 3
Active, not recruiting
Conditions
Chronic Lymphocytic Leukemia
Leukemia, B-cell
Leukemia, Lymphocytic
Small Lymphocytic Lymphoma
Interventions
Registration Number
NCT05254743
Lead Sponsor
Loxo Oncology, Inc.
Brief Summary

The purpose of Part 1 of this study is to compare the efficacy and safety of pirtobruitinib (LOXO-305) to ibrutinib in participants with CLL/SLL; participants may or may not have already had treatment for their cancer. The purpose of Part 2 of this study evaluates pirtobrutinib monotherapy in treatment-naïve participants with CLL/SLL with 17p deletions. Participation could last up to six years for Part 1. Participation could last up to 2 years for Part 2.

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
725
Inclusion Criteria
  • Confirmed diagnosis of CLL/SLL requiring therapy per iwCLL 2018 criteria

  • Part 1 - Known 17p deletion status (wildtype or deleted). Part 2 - Must have deletion of 17p as determined by FISH testing

  • Eastern Cooperative Oncology Group (ECOG) Performance Status 0-2

  • Adequate organ function

    • Platelets greater than or equal to ≥ 50 x 10⁹/liter (L) or ≥30 x 10⁹/L in participants with documented bone marrow involvement considered to impair hematopoiesis,
    • Hemoglobin ≥8 grams/deciliter (g/dL) or ≥6 g/dL in participants with documented bone marrow involvement considered to impair hematopoiesis
    • Absolute neutrophil count ≥0.75 x 10⁹/L or ≥0.50 × 10⁹/L in participants with documented bone marrow involvement considered to impair hematopoiesis
    • Kidney function: Estimated creatinine clearance ≥30 milliliters per minute (mL/min)
Exclusion Criteria
  • Known or suspected Richter's transformation to diffuse large B-cell lymphoma (DLBCL), prolymphocytic leukemia, or Hodgkin's lymphoma at any time preceding enrollment
  • Known or suspected central nervous system (CNS) involvement
  • A significant history of renal, neurologic, psychiatric, endocrine, metabolic or immunologic disease
  • Active uncontrolled auto-immune cytopenia (e.g., autoimmune hemolytic anemia [AIHA], idiopathic thrombocytopenic purpura [ITP])
  • Significant cardiovascular disease including ejection fraction < 40% and any grade ongoing atrial fibrillation or atrial flutter
  • Hepatitis B or hepatitis C testing indicating active/ongoing infection, based on Screening laboratory tests
  • Active cytomegalovirus (CMV) infection
  • Active uncontrolled systemic bacterial, viral, or fungal infection
  • Known human immunodeficiency virus (HIV) infection, regardless of cluster of differentiation 4 (CD4) count
  • Clinically significant active malabsorption syndrome or other condition likely to affect GI absorption of the oral-administered study treatments
  • Ongoing inflammatory bowel disease
  • Previous treatment for CLL/SLL - Part 1: Treatment-naïve and previously treated, except prior exposure to BTK inhibitor (covalent or noncovalent).

Part 2: participants must be treatment naïve

  • Concurrent use of investigational agent or anticancer therapy except hormonal therapy
  • Participants requiring therapeutic anticoagulation with warfarin or another Vitamin K antagonist
  • Use of > 20 mg prednisone daily or equivalent dose of steroid at the time of first dose of study drug
  • Vaccination with a live vaccine within 28 days prior to randomization
  • Participants receiving chronic therapy with a strong cytochrome P450 (CYP)3A inhibitor (except posaconazole and voriconazole) which cannot be stopped within 3-5 half lives of the CYP3A inhibitor therapy prior to start of study drug treatment
  • Participants with known hypersensitivity, including anaphylaxis, to any component or excipient of pirtobrutinib or ibrutinib

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Pirtobrutinib Part 1PirtobrutinibParticipants will receive pirtobrutinib orally.
IbrutinibIbrutinibParticipants will receive ibrutinib orally.
Pirtobrutinib Part 2PirtobrutinibParticipants will receive pirtobrutinib orally.
Primary Outcome Measures
NameTimeMethod
Percentage of Participants Achieving Complete Response (CR), Complete Remission with Incomplete Hematologic Recovery (Cri), Nodular Partial Remission (nPR) or Partial Response (PR): Overall Response Rate (ORR) Part 1Baseline to best overall response the best response recorded from Cycle 1 Day 1 until data cutoff date, PD, or start of new anticancer treatment, whichever is the earliest] (approximately 3 years and 5 months)

ORR as assessed by independent review committee (IRC) per International Workshop on Chronic Lymphocytic Leukemia (iwCLL) 2018 criteria

Percentage of Participants Achieving Complete Response (CR), Complete Remission with Incomplete Hematologic Recovery (CRi), Nodular Partial Remission (nPR) or Partial Response (PR): Overall Response Rate (ORR) Part 2Baseline to best overall response the best response recorded from Cycle 1 Day 1 until data cutoff date, PD, or start of new anticancer treatment, whichever is the earliest (Approximately 2 years and 3 months)

ORR as assessed by independent review committee (IRC) per International Workshop on Chronic Lymphocytic Leukemia (iwCLL) 2018 criteria

Secondary Outcome Measures
NameTimeMethod
IRC-assessed Progression-Free Survival (PFS)Randomization to PD (per iwCLL 2018 criteria) or death from any cause (approximately 5 years 8 months)

PFS by IRC per iwCLL 2018 criteria

Investigator assessed Progression-Free Survival (PFS)Randomization to PD (per iwCLL 2018 criteria) or death from any cause (approximately 5 years 8 months)

PFS by Investigator per iwCLL 2018 criteria

Event-Free Survival (EFS)Randomization to first occurrence of treatment discontinuation due to adverse event/toxicity, treatment-emergent atrial fibrillation or atrial flutter of any grade, progressive disease (PD) or death (approximately 4 years)

EFS by IRC per iwCLL 2018 criteria

Duration of Response (DOR)Time from the date of the first documented response of CR, CRi, nPR or PR to the earlier of documentation of definitive PD (per iwCLL 2018 criteria) or death from any cause (approximately 2 years)

DOR by IRC and Investigator by iwCLL 2018 Criteria.

Overall Survival (OS)Randomization to death from any cause (approximately 6 years)

OS

Time to Next Treatment (TTNT)Randomization to initiation of the next systemic anticancer therapy for CLL/SLL or death from any cause, whichever occurs first (approximately 6 years)

TTNT

Time to Worsening (TTW) of CLL/SLL Related SymptomsRandomization to time to worsening symptoms (approximately 4 years)

Using symptom questions identified from the EORTC item library. The range of raw scores for these items could be from 0 to 52 with highest score being worse symptoms.

Comparative TolerabilityFrom Baseline to Treatment Discontinuation for Any Reason (approximately 4 years)

Comparative Tolerability measured by proportion of time with high side-effect burden

Percentage of Participants Achieving DOR Part 2Time from the date of the first documented response of CR, CRi, nPR, or PR to the earlier of the documentation of definitive PD or death from any cause] (Approximately 2 years)

DOR as assessed by IRC and Investigator defined as the time from the date of the first documented response of CR, CRi, nPR, or PR to the earlier of the documentation of definitive PD per iwCLL 2018 criteria or death from any cause.

Trial Locations

Locations (176)

Genesis Cancer Center

🇺🇸

Hot Springs, Arkansas, United States

Pacific Cancer Medical Center, Inc

🇺🇸

Anaheim, California, United States

Alta Bates Summit Medical Center

🇺🇸

Berkeley, California, United States

TOI Clinical Research

🇺🇸

Cerritos, California, United States

Stanford School of Medicine-Cancer Clinical Trials Office

🇺🇸

Palo Alto, California, United States

Eisenhower Army Medical Center

🇺🇸

Rancho Mirage, California, United States

Sharp Memorial Hospital

🇺🇸

San Diego, California, United States

California Cancer Associates for Research and Excellence

🇺🇸

San Marcos, California, United States

Eastern Connecticut Hematology/Oncology Assoc.

🇺🇸

Norwich, Connecticut, United States

Asclepes Research Centers Florida

🇺🇸

Brooksville, Florida, United States

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Genesis Cancer Center
🇺🇸Hot Springs, Arkansas, United States
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