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Identifying Predictors of Poor Health-Related Quality-of-Life Among Pediatric Hematopoietic Stem Cell Donors

Completed
Conditions
Quality of Life
Registration Number
NCT03718546
Lead Sponsor
Center for International Blood and Marrow Transplant Research
Brief Summary

To compare donors to their non-donor counterparts and healthy controls as well as to generate trajectory classes based on longitudinal patterns of donor HRQoL and identify predictors of poor donor HRQoL.

Detailed Description

There is limited data to show the effects that donation has on pediatric donors to their siblings. There is widespread agreement that it is critical to investigate the medical and psychosocial aspects of sibling pediatric HSC donation for multiple reasons including (a) the vulnerability of the pediatric population undergoing donation, (b) increasing use of pediatric HSC donation as a therapeutic option, (c) evidence that \~20% of pediatric HSC donors experience clinically important HRQoL deficits, and (d) the impact that improved understanding of factors predicting poor HRQoL will have on our ability to develop guidelines and/or interventions for assisting at-risk donors/families. The proposed study will help to compare donors to their non-donor counterparts and healthy controls as well as to generate trajectory classes based on longitudinal patterns of donor HRQoL and identify predictors of poor donor HRQoL.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
754
Inclusion Criteria
  • Participants must fall into one of the following categories:

    • Donor between the age of 5 and 17 who is donating to a sibling
    • Parent/caregiver of study participating donor
    • Recipient sibling aged 5 to 17 of study participating donor
    • Any of the donor's non-donor/non-recipient siblings between 5 and 17
    • Any child between 5 and 17 with a brother or sister (also between 5 and 17) receiving a transplant from an unrelated source
  • Be willing and able to provide signed informed consent:

    • Adults must give consent for their children's and, if applicable, their own participation
    • Assent will be obtained in accordance with guidelines at the participant's transplant institution
  • Be willing and able to respond to psychological assessment questions

  • Must be the donor's first donation

  • Recipient must consent to the CIBMTR research database

Exclusion Criteria
  • For families with pediatric donors aged 5 to 17, at minimum, the donor child and/or one parent must consent/assent to participation. If that minimum is not met, the family will be excluded

  • Donor or non-donor siblings who do not live in the same household as the recipient at lease half of the time

  • Unable to consent/assent or complete a phone interview in English

    • Parents may consent/assent in Spanish
  • No access to a telephone

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
HRQoL (Health Related Quality of Life)1 year

To longitudinally and quantitatively describe the HRQoL of a diverse nation-wide cohort of sibling pediatric Hematopoietic Stem Cell (HSC) donors (Peripheral Blood Stem Cell or Bone Marrow) and to compare their HRQoL to that of (1) healthy non-donor sibling from the same family, (2) siblings of children with similar diseases who receive alternate treatments (e.g., unrelated cord blood transplants), and (3) healthy age, gender, and race/ethnicity-matched controls.

Secondary Outcome Measures
NameTimeMethod
1 year post-donation1 year

To identify and examine donor HRQoL trajectories from pre- through 1 year post-donation.

Donor characteristics1 year

To determine which donor characteristics (e.g., demographic, psychosocial, and donation-related), recipient characteristics (e.g., recipient disease, transplant complications and outcomes), family characteristics (e.g., composition, cohesiveness, stress), and transplant center characteristics (e.g., presence of a donor advocate) most strongly predict membership in trajectory classes with poor HRQoL among donors.

Trial Locations

Locations (31)

Children's Hospital of Philadelphia

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Philadelphia, Pennsylvania, United States

Vanderbilt University Medical Center

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Nashville, Tennessee, United States

Children's Health (formerly Children's Medical Center Dallas)

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Dallas, Texas, United States

University of Utah Blood and Marrow Transplant Program - Pediatrics

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Salt Lake City, Utah, United States

University of Alabama at Birmingham

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Birmingham, Alabama, United States

Loma Linda University

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Loma Linda, California, United States

Phoenix Children's Hospital

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Phoenix, Arizona, United States

City of Hope

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Duarte, California, United States

University of California San Francisco Medical Center

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San Francisco, California, United States

Spectrum Health

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Grand Rapids, Michigan, United States

Children's Hospital of Los Angeles

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Los Angeles, California, United States

Methodist Healthcare System of San Antonio/Texas Transplant Institute

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San Antonio, Texas, United States

Children's Hospital of New Orleans/LSUHSC

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New Orleans, Louisiana, United States

NIH/NCI

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Bethesda, Maryland, United States

University of Louisville Hospital - James Brown Cancer Center

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Louisville, Kentucky, United States

Medical University of South Carolina

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Charleston, South Carolina, United States

University of North Carolina Hospitals

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Chapel Hill, North Carolina, United States

Westchester Medical Center

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New York, New York, United States

Fred Hutchinson Cancer Research Center

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Seattle, Washington, United States

Niklaus Children's Hospital

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Miami, Florida, United States

Rady Children's Hospital San Diego

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San Diego, California, United States

Duke University Medical Center

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Durham, North Carolina, United States

University of Michigan

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Ann Arbor, Michigan, United States

Children's Hospital Colorado

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Aurora, Colorado, United States

Yale New Haven Hospital

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New Haven, Connecticut, United States

St. Louis Children's Hospital

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Saint Louis, Missouri, United States

Children's Hospital of Wisconsin

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Milwaukee, Wisconsin, United States

Memorial Sloan-Kettering Cancer Center

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New York, New York, United States

Children's National Medical Center

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Washington, District of Columbia, United States

Children's Healthcare of Atlanta

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Atlanta, Georgia, United States

The Children's Mercy Hospitals and Clinics

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Kansas City, Missouri, United States

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