MedPath

The HeLiX (Hemorrhage During Liver Resection: traneXamic Acid) Trial

Phase 3
Active, not recruiting
Conditions
Cancer
Tumour
Surgery
Interventions
Drug: Tranexamic acid (TXA)
Drug: Normal saline
Registration Number
NCT02261415
Lead Sponsor
Sunnybrook Health Sciences Centre
Brief Summary

This is a Phase III multicentre randomized controlled trial (RCT) to evaluate the impact of tranexamic acid (TXA) on perioperative blood transfusion in patients undergoing liver resection. The rationale for this study includes: (1) experimental evidence supporting the use of TXA in other surgical populations; (2) lack of evidence in patients undergoing liver resection; (3) clinical uncertainty and extensive support amongst hepatobiliary surgeons, anaesthesiologists, and hematologists for this proposed trial; (4) a feasible and efficient study design; and (5) the importance of the question: incidence of blood transfusion in patients undergoing liver resection is high, and the consequences serious. The sample size for this study is 1230 participants.Participants enrolled in the prior Vanguard study will proceed directly into the RCT.

Detailed Description

Purpose Compelling biological rationale and indirect evidence from other settings suggest that there is potential benefit to administering TXA to patients undergoing liver resection. A lack of consensus in the hepatobiliary community and lack of direct evidence in patients undergoing liver resection mandate a RCT.

Hypothesis To determine the impact of perioperative administration of TXA to patients undergoing liver resection on the need for blood transfusion and long-term survival.

Justification If TXA use in liver resection resulted in an important decrease in blood transfusions, clinical practice worldwide would be likely to change. Over 2000 patients in Canada undergo liver resection annually and could benefit from this simple, low-cost intervention. This intervention could easily be implemented in other countries, where many more patients undergo liver resection annually. Furthermore, TXA may be beneficial in other operative fields where bleeding is a major problem, including thoracic surgery, colorectal surgery, and many others.

Objectives

The primary outcome of the RCT will be:

1) Receipt of blood transfusion (% transfused): 7 days

The secondary outcomes of the RCT are:

1. Intraoperative blood loss will be assessed by adding the net weight of sponges and fluid suction (minus irrigation and intraoperative bile or other fluids in suction/sponge)

2. Total blood loss (postoperative day (POD)0 - POD7) will be assessed by Gross' formula, which uses the maximum postoperative decrease in the level of hemoglobin adjusted for the weight and height of the patient

3. Number of packed red blood cells (PRBC) units transfused (POD0 - POD7)

4. Postoperative incidence of symptomatic venous thromboembolic event confirmed with either computed tomography (CT) angiogram (for pulmonary embolism) or venous Doppler ultrasound (for deep venous thrombosis) (within 90 days of surgery)

5. Postoperative complications (within 90 days of surgery) will be determined using the Clavien-Dindo classification

6. Recurrence free survival (within 5 years of surgery) will be determined by review of patient medical record every 6 months until 5 years post-surgery

a. Recurrence free survival is defined as the time from POD0 to the first event that is recurrent (local or distal) cancer or death (from any cause)

7. Overall survival (within 5 years of surgery) will be determined by review of patient medical record every 6 months until 5 years post-surgery

a. Overall survival is defined as the time from date of POD0 to death from any cause

8. QOL will be determined by administering European Organization for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire (QLQ) -C30 and the QLQ- Liver Metastases Colorectal (LMC) 21 at baseline, 30 and 90 days following surgery

9. Perioperative mortality will be recorded between POD0 and POD7

10. Economic analysis will assess impact of TXA incorporation on health care resources and strategies for systematic utilization of TXA

Research Method This is a Phase III multicentre randomized controlled trial (RCT) to evaluate the impact of tranexamic acid (TXA) on perioperative blood transfusion in patients undergoing liver resection. The trial will conceal allocation, maximize possible blinding, independently assess the appropriateness of transfusion, use strategies to limit loss to follow-up and crossovers, and use a conservative stopping rule. Patients will be administered a single dose of study drug intravenously immediately after induction of anaesthesia, followed by infusion over eight hours.

Statistical Analysis Primary analysis will include only patients who underwent liver resection; patients who are randomized but do not receive liver resection (usually due to more advanced disease identified intraoperatively) will be excluded. A sensitivity analysis will be conducted whereby all randomized patients are included in the assessment of the primary outcome.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
1386
Inclusion Criteria
  • Patient scheduled for open or laparoscopic liver surgery
  • Age ≥18 years
  • Cancer related diagnosis or indication (e.g. pre-cancer, suspicion of cancer, definite cancer)
Exclusion Criteria
  • Severe anemia (hemoglobin (Hgb) levels <90 g/l)
  • Documented arterial or venous thrombosis at screening or in past three months (not including therapeutic portal vein embolization)
  • Anticoagulants (other than low-molecular-weight heparin (LMWH) or heparin in prophylactic doses to prevent deep vein thrombosis), direct thrombin inhibitors or thrombolytic therapy administered or completed within last week
  • Known disseminated intravascular coagulation
  • Severe renal insufficiency (creatinine clearance (CrCl) <30 ml/min)
  • History of seizure disorder
  • Pregnant or lactating (a negative urine pregnancy test must be obtained for women of child bearing potential during the pretreatment evaluation)
  • Acquired disturbance of colour vision
  • Hypersensitivity to TXA or any of the ingredients
  • Unable to receive blood products (i.e. difficulty with cross matching, refuses blood transfusion, or a past history of unexplained severe transfusion reaction)
  • Previously enrolled in this study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Tranexamic acid (TXA)Tranexamic acid (TXA)1 g TXA bolus injection + 1 g TXA infusion from induction over 8 hours
Normal saline (0.9% sodium chloride)Normal saline1 g saline bolus injection + 1 g saline infusion from induction over 8 hours
Primary Outcome Measures
NameTimeMethod
Receipt of blood transfusion (% transfused): 7 days7 days

Receipt of one or more RBC transfusions between Day 0 and Day 7

Secondary Outcome Measures
NameTimeMethod
Perioperative mortality7 days

Perioperative mortality will be recorded between POD0 and POD7

Intraoperative blood loss7 days

Intraoperative blood loss will be assessed by adding the net weight of sponges and fluid suction (minus irrigation and intraoperative bile or other fluids in suction/sponge)

Number of packed red blood cells (PRBC) units transfused7 days

Number of packed red blood cells (PRBC) units transfused (POD0 - POD7)

Postoperative incidence of symptomatic venous thromboembolic event90 days

Postoperative incidence of symptomatic venous thromboembolic event confirmed with either computed tomography (CT) angiogram (for pulmonary embolism) or venous Doppler ultrasound (for deep venous thrombosis) (within 90 days of surgery)

Recurrence Free Survival (within 5 years of surgery)60 months

Disease recurrence is defined as the clinical presence of cancer that has either been confirmed by biopsy, has had treatment initiated, or is documented in the treating physician's notes. Five year disease recurrence from day of surgery will be evaluated approximately every 6 months until 5 years via medical record review.

Overall Survival (within 5 years of surgery)60 months

Overall survival is defined as the time from date of surgery to death from any cause. It will be determined by review of patient medical record every 6 months until 5 years post-surgery.

Quality of Life (QOL) Assessment using European Organization for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire (QLQ)-C30Baseline, 30 days, 90 days

QOL will be determined by administering the EORTC QLQ-C30 at baseline, 30 and 90 days following surgery.

Postoperative complications assessed using Clavien-Dindo Grading System90 days

Postoperative complications (within 90 days of surgery) will be determined using the Clavien-Dindo classification

Total blood loss7 days

Total blood loss (postoperative day (POD)0 - POD7) will be assessed by Gross' formula, which uses the maximum postoperative decrease in the level of hemoglobin adjusted for the weight and height of the patient

Quality of Life (QOL) Assessment using European Organization for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire (QLQ)-Liver Module (LM)C21 QuestionnaireBaseline, 30 days, 90 days

QOL will be determined by administering QLQ-LMC21 at baseline, 30 and 90 days following surgery.

Compare the cost of tranexamic acid (TXA) versus placebo on perioperative blood transfusion in patients undergoing liver resection90 days

Economic analysis will assess impact of TXA incorporation on health care resources and strategies for systematic utilization of TXA. The analysis will be using data collected in the randomized controlled trial from a societal perspective.The output of the economic analysis is the incremental cost of TXA compared to placebo (control group).

Trial Locations

Locations (11)

University Health Network

🇨🇦

Toronto, Ontario, Canada

McGill University Health Centre

🇨🇦

Montreal, Quebec, Canada

Foothills Hospital

🇨🇦

Calgary, Alberta, Canada

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

Kelowna General Hospital

🇨🇦

Kelowna, British Colombia, Canada

Hamilton Health Sciences

🇨🇦

Hamilton, Ontario, Canada

London Health Sciences Centre

🇨🇦

London, Ontario, Canada

Sunnybrook Health Sciences Centre

🇨🇦

Toronto, Ontario, Canada

Kingston General Health Research Institute

🇨🇦

Kingston, Ontario, Canada

St. Joseph's Health Centre

🇨🇦

Toronto, Ontario, Canada

Queen Elizabeth II Health Sciences Centre

🇨🇦

Halifax, Nova Scotia, Canada

© Copyright 2025. All Rights Reserved by MedPath