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Maridebart Cafraglutide in Heart Failure With Preserved or Mildly Reduced Ejection Fraction and Obesity

Phase 3
Not yet recruiting
Conditions
Heart Failure With Preserved Ejection Fraction
Heart Failure With Mildly Reduced Ejection Fraction
Obesity
Interventions
Registration Number
NCT07037459
Lead Sponsor
Amgen
Brief Summary

This study will examine if maridebart cafraglutide as an adjunct to standard of care will lead to a reduction in heart failure (HF) events such as HF hospitalizations and urgent HF visits, cardiovascular (CV) deaths and improvement in HF symptoms in participants with HF with preserved ejection fraction (HFpEF) and HF with mildly reduced ejection fraction (HFmrEF) who are obese. This is a phase 3, global, multicenter, 2-part study with a double-blind period and an open-label extension (OLE). The study is event-driven, and Part 1 will conclude when approximately 850 primary endpoint events have occurred.

Detailed Description

Not available

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
5056
Inclusion Criteria
  • Age ≥ 18 years.

  • BMI ≥ 30 kg/m^2.

  • HF diagnosed for at least 30 days before screening with New York Heart Association (NYHA) Class II-IV.

  • Managed with HF standard of care therapies.

  • Left ventricular ejection fraction (LVEF) of > 40%.

  • Elevated NT-proBNP.

  • Participants must have at least one of the following:

    1. Structural heart disease OR
    2. Documented hospitalization with a primary diagnosis of decompensated HF within 12 months before randomization OR
    3. Evidence of elevated filling pressures within 12 months before randomization.
Exclusion Criteria
  • History of any of the following within 60 days before screening: Type I (spontaneous) MI, valvular replacement or repair, coronary revascularization, coronary artery bypass graft surgery or other major cardiovascular surgery, stroke.

  • HF due to: hypertrophic cardiomyopathy, infiltrative cardiomyopathy, active myocarditis, constrictive pericarditis, cardiac tamponade, arrhythmogenic right ventricular or left ventricular cardiomyopathy/dysplasia, or uncorrected primary valvular heart disease, or clinically significant congenital heart disease.

  • Any lifetime history of LVEF ≤ 40%.

  • Currently hospitalized with acute decompensated HF or hospitalization with a primary diagnosis of decompensated HF within 30 days before screening.

  • Type 1 diabetes mellitus, or any type of diabetes with the exception of T2DM or history of gestational diabetes.

  • For participants with a prior diagnosis of T2DM at screening:

    1. HbA1c > 10.0%
    2. Uncontrolled diabetes requiring immediate therapy
    3. History of diabetic ketoacidosis or hyperosmolar state/coma
    4. One or more episodes of severe hypoglycemia within 6 months before screening and/or history of hypoglycemia unawareness
    5. History of proliferative diabetic retinopathy, diabetic maculopathy, or severe non-proliferative diabetic retinopathy.
  • SBP ≥ 180 mmHg , or on three or more blood pressure-lowering drugs with a SBP > 160 mmHg.

  • History of chronic pancreatitis or acute pancreatitis in the 180 days before screening.

  • Family (or personal) history of medullary thyroid carcinoma or MEN-2.

  • eGFR < 20 mL/min/1.73 m^2 (CKD-EPI creatinine (Cr)-cystatin C equation) or receiving dialysis at screening.

  • Calcitonin ≥ 50 ng/L (pg/mL) at screening.

  • Acute or chronic hepatitis.

  • Any of the following psychiatric history:

    1. History of unstable major depressive disorder or other severe psychiatric disorder within 2 years before screening
    2. Lifetime history of suicide attempt
    3. History of non-suicidal self-injury within 5 years before screening.
  • History of any other condition that, in the opinion of the investigator, may preclude the participant from following the protocol and completing the study.

  • Use of any glucagon-like peptide 1 receptor agonist (GLP-1 RA), glucose-dependent insulinotropic polypeptide (GIP) agonists or antagonists, or amylin analogs within 90 days before randomization or planned use during the conduct of the study.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Maridebart CafraglutideMaridebart cafraglutideParticipants will receive maridebart cafraglutide subcutaneously (SC)
PlaceboPlaceboParticipants will receive placebo SC
Primary Outcome Measures
NameTimeMethod
Time to First Occurrence of a Composite Endpoint Consisting of: CV Death or HF EventsUp to approximately 35 months

Heart Failure events include: hospitalization for HF or urgent HF visits.

Secondary Outcome Measures
NameTimeMethod
Change From Baseline in Kansas City Cardiomyopathy Questionnaire (KCCQ) Clinical Summary Score (CSS) for Participants with Baseline KCCQ-CSS Score ≤ 80Baseline and Week 48

The KCCQ is a 23-item disease-specific measure for participants with HF, measuring the participant's perception of their health status. The KCCQ-CSS assesses symptoms and physical limitations, ranging from 0 to 100, with higher scores indicating better functioning and quality of life.

Change from Baseline in the KCCQ Total Symptom Score (TSS) for Participants with Baseline KCCQ-CSS Score ≤ 80Baseline and Week 48

The KCCQ is a 23-item disease-specific measure for participants with HF, measuring the participant's perception of their health status. The KCCQ-TSS assesses symptom frequency and burden, ranging from 0 to 100, with higher scores indicating better functioning and quality of life.

Total Number of HF Events Including First and Recurrent HF EventsUp to approximately 35 months
Time to First Occurrence of a Composite Endpoint Consisting of: Myocardial Infarction (MI), Ischemic Stroke, CV Death (Major Adverse Cardiac Events), or HF EventsUp to approximately 35 months
Time to First Event of a Composite Nephropathy EndpointUp to approximately 35 months

The composite nephropathy endpoint consists of: persistent macroalbuminuria, persistent ≥ 40% reduction in estimated glomerular filtration rate (eGFR), onset of persistent eGFR \< 15 mL/min/1.73 m\^2, initiation of chronic renal replacement therapy (dialysis or transplantation), CV or renal death.

Change in eGFR Slope (Total)Baseline up to approximately 35 months
Change in eGFR Slope (Chronic)From 4 months up to approximately 35 months
Time to Onset of Type 2 Diabetes Mellitus (T2DM) in Participants with PrediabetesUp to approximately 35 months
Time to the First HF EventUp to approximately 35 months
Change from Baseline in the Systolic Blood Pressure (SBP) and Diastolic Blood Pressure (DBP)Baseline and Week 72
Change from Baseline in the Waist Circumference (cm)Baseline and Week 72
Change from Baseline in the Urine Albumin-to-creatinine Ratio (uACR)Baseline and Week 72
Change from Baseline in the Hemoglobin A1c (HbA1c [%, mmol/mol]) in Participants with T2DMBaseline and Week 72
Percent Change from Baseline in the High-sensitivity C Reactive Protein (hs-CRP)Baseline and Week 72
Percent Change from Baseline in the Body Weight (kg)Baseline and Week 72
Percent Change from Baseline in Total CholesterolBaseline and Week 72
Percent Change from Baseline in Non-high-density Lipoprotein Cholesterol (non-HDL-C)Baseline and Week 72
Percent Change from Baseline in Low-density Lipoprotein Cholesterol (LDL-C), HDL-C, Triglycerides (TG), Very Low-density Lipoprotein Cholesterol (VLDL-C)Baseline and Week 72
Total All-cause Hospitalizations (First and Recurrent Time to Event)Up to approximately 35 months
Number of Participants Achieving ≥ 5-point Change in KCCQ-CSS Score from Baseline for Participants with Baseline KCCQ-CSS Score ≤ 80Baseline and Week 48

The KCCQ is a 23-item disease-specific measure for participants with HF, measuring the participant's perception of their health status. The KCCQ-CSS assesses symptoms and physical limitations, ranging from 0 to 100, with higher scores indicating better functioning and quality of life.

Number of Participants Achieving ≥ 10-point Change in KCCQ-CSS Score from Baseline for Participants with Baseline KCCQ-CSS Score ≤ 80Baseline and Week 48

The KCCQ is a 23-item disease-specific measure for participants with HF, measuring the participant's perception of their health status. The KCCQ-CSS assesses symptoms and physical limitations, ranging from 0 to 100, with higher scores indicating better functioning and quality of life.

Number of Participants Achieving an Anchor-based Change in KCCQ-CSS Score From Baseline for Participants with Baseline KCCQ-CSS Score ≤ 80Baseline and Week 48

The KCCQ is a 23-item disease-specific measure for participants with HF, measuring the participant's perception of their health status. The KCCQ-CSS assesses symptoms and physical limitations, ranging from 0 to 100, with higher scores indicating better functioning and quality of life. The Patient Global Impression of Severity (PGI-S) and Patient Global Impression of Change (PGI-C) can be used as anchors to estimate within-patient change in the KCCQ-CSS score.

Number of Participants Achieving ≥ 5-point Change in KCCQ-TSS Score from Baseline for Participants with Baseline KCCQ-CSS Score ≤ 80Baseline and Week 48

The KCCQ is a 23-item disease-specific measure for participants with HF, measuring the participant's perception of their health status. The KCCQ-TSS assesses symptom frequency and burden, ranging from 0 to 100, with higher scores indicating better functioning and quality of life. The KCCQ-CSS assesses symptoms and physical limitations, ranging from 0 to 100, with higher scores indicating better functioning and quality of life.

Number of Participants Achieving ≥ 10-point Change in KCCQ-TSS Score from Baseline for Participants with Baseline KCCQ-CSS Score ≤ 80Baseline and Week 48

The KCCQ is a 23-item disease-specific measure for participants with HF, measuring the participant's perception of their health status. The KCCQ-TSS assesses symptom frequency and burden, ranging from 0 to 100, with higher scores indicating better functioning and quality of life. The KCCQ-CSS assesses symptoms and physical limitations, ranging from 0 to 100, with higher scores indicating better functioning and quality of life.

Number of Participants Achieving an Anchor-based Change in KCCQ-TSS Score from Baseline for Participants with Baseline KCCQ-CSS Score ≤ 80Baseline and Week 48

The KCCQ is a 23-item disease-specific measure for participants with HF, measuring the participant's perception of their health status. The KCCQ-TSS assesses symptom frequency and burden, ranging from 0 to 100, with higher scores indicating better functioning and quality of life. The KCCQ-CSS assesses symptoms and physical limitations, ranging from 0 to 100, with higher scores indicating better functioning and quality of life. The PGI-S and PGI-C can be used as anchors to estimate within-patient change in the KCCQ-CSS score.

Time to All-cause DeathUp to approximately 35 months
Time to CV DeathUp to Approximately 35 Months
Number of Participants with Treatment-emergent Adverse Events and Serious Adverse EventsUp to approximately 35 months
Plasma Concentration of Maridebart CafraglutideWeek 72
Change from Baseline in N-terminal Pro B Type Natriuretic Peptide (NT-proBNP)Baseline and Week 72
Time to New Onset of Atrial Fibrillation (AF) or Atrial Flutter (AFL) in Participants Without a History of AF or AFL at BaselineBaseline and up to approximately 35 months
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