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Post-Marketing Non-Interventional Safety Evaluation of Obizur in the Treatment of Bleeding Episodes for Patients With Acquired Hemophilia A

Completed
Conditions
Acquired Hemophilia A
Interventions
Biological: OBIZUR
Registration Number
NCT02610127
Lead Sponsor
Baxalta now part of Shire
Brief Summary

The overall objective is to enroll patients with acquired hemophilia A (AHA) who are prescribed and treated with Obizur, to assess safety, and to describe factors related to safety, utilization and effectiveness in a real-world setting.

Detailed Description

This study is a multi-center, uncontrolled, open-label, non-interventional post-marketing safety surveillance study to describe the use of Obizur in patients with acquired hemophilia A (AHA), and secondarily, where data are available, to describe the hemostatic effectiveness and immunogenicity of Obizur.

Patients should be enrolled at the earliest possible time point after initiating Obizur.

In an attempt to collect safety and utilization data on patients treated with Obizur since Food and Drug Administration (FDA) approval in October 2014, Baxalta will make an effort to identify all persons treated with Obizur and to collect data for as many patients as possible.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
53
Inclusion Criteria
  1. Participant is ≥18 years of age at the time of informed consent.
  2. Participant has AHA, and is being treated/was treated with Obizur.
  3. Participant or the participant's legally authorized representative is willing and able to provide informed consent, unless informed consent is not required
Exclusion Criteria
  1. Participant has a known anaphylactic reaction to the active substance, to any of the excipients, or to hamster protein.
  2. Participant has a concomitant bleeding disorder(s) other than acquired hemophilia A (AHA).
  3. Participant has participated in another clinical study involving a medicinal product or device within 30 days prior to enrollment or is scheduled to participate in another clinical study involving a medicinal product or device during the course of the study.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
OBIZUR - Prospective ParticipantsOBIZURParticipants enrolled and treated with Obizur after the prospective study start date
OBIZUR - Retrospective ParticipantsOBIZURRetrospective chart review of participants treated with OBIZUR from product approval date until prior to the prospective study start date
Primary Outcome Measures
NameTimeMethod
Incidence of therapy-related SAEs and level of severityThroughout the study period of approximately 4 years
Secondary Outcome Measures
NameTimeMethod
Occurrence of any thrombogenic eventThroughout the study period of approximately 4 years
Titer of newly recognized anti-porcine Factor VIII (anti-pFVIII) neutralizing antibodies (inhibitors) or increase in titer of anti-pFVIII inhibitors from baseline and changes over time.Throughout the study period of approximately 4 years
Occurrence of hypersensitivity reactionsThroughout the study period of approximately 4 years
Time to bleeding resolution, participant study termination, or switch to another treatmentThroughout the study period, up to approximately 4 years
Number of Obizur units/kg required for control of bleedingThroughout the study period, up to approximately 4 years
Impact of the inhibitor on hemostatic efficacy and any associated clinical manifestations.Throughout the study period of approximately 4 years
Hemostatic effectiveness assessment for resolution of bleedingThroughout the study period, up to approximately 4 years

Determined as either bleeding stopped or did not stop

Number of Obizur infusions required for control of bleedingThroughout the study period, up to approximately 4 years

Trial Locations

Locations (16)

University of Florida

🇺🇸

Gainesville, Florida, United States

University of Colorado Health

🇺🇸

Aurora, Colorado, United States

Emory University School of Medicine

🇺🇸

Atlanta, Georgia, United States

Bleeding and Clotting Disorders Institute

🇺🇸

Peoria, Illinois, United States

Indiana Hemophilia and Thrombosis Center

🇺🇸

Indianapolis, Indiana, United States

Henry Ford Health System

🇺🇸

Detroit, Michigan, United States

Washington University

🇺🇸

Saint Louis, Missouri, United States

Michigan State University

🇺🇸

East Lansing, Michigan, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

University of Iowa Hospitals & Clinics

🇺🇸

Iowa City, Iowa, United States

Tulane University Hospital & Clinics

🇺🇸

New Orleans, Louisiana, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

Comprehensive Cancer Center of Wake Forest Unversity

🇺🇸

Winston-Salem, North Carolina, United States

University of Pennsylvania Health System

🇺🇸

Philadelphia, Pennsylvania, United States

University of Utah Health Sciences Center

🇺🇸

Salt Lake City, Utah, United States

Blood Center of Southeast Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

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