MedPath

High-Dose Combination Chemotherapy Plus Peripheral Stem Cell Transplantation Compared With Standard Combination Chemotherapy in Treating Women With High-Risk Breast Cancer

Phase 3
Completed
Conditions
Breast Cancer
Interventions
Drug: CMF regimen
Biological: filgrastim
Procedure: peripheral blood stem cell transplantation
Radiation: low-LET electron therapy
Radiation: low-LET photon therapy
Registration Number
NCT00002784
Lead Sponsor
ETOP IBCSG Partners Foundation
Brief Summary

RATIONALE: Drugs used in chemotherapy use different ways to stop tumor cells from dividing so they stop growing or die. Combining chemotherapy with peripheral stem cell transplantation may allow the doctor to give higher doses of chemotherapy drugs and kill more tumor cells. It is not yet known if high-dose combination chemotherapy plus peripheral stem cell transplantation is more effective than standard combination chemotherapy for breast cancer.

PURPOSE: Randomized phase III trial to compare high-dose combination chemotherapy plus peripheral stem cell transplantation with standard combination chemotherapy in treating women with stage II or stage III breast cancer.

Detailed Description

OBJECTIVES: I. Compare the survival, disease-free survival, and systemic disease-free survival of women with high-risk, operable stage II/III breast cancer treated with three courses of dose-intensive epirubicin/cyclophosphamide (EC) supported by granulocyte colony-stimulating factor (G-CSF) and G-CSF-mobilized peripheral blood stem cells vs. standard EC followed by cyclophosphamide/methotrexate/fluorouracil. II. Compare the toxicity, duration of quality-adjusted time without symptoms and toxicity, and quality of life associated with these two treatments. III. Evaluate the cost effectiveness of these two treatments.

OUTLINE: This is a randomized study. Patients are stratified by estrogen receptor status and menopausal status. Within 6 weeks of surgery, patients in the first group receive epirubicin (preferred) or doxorubicin plus cyclophosphamide every 3 weeks for 4 courses followed by conventional cyclophosphamide, methotrexate, and fluorouracil (CMF) every 4 weeks for 3 courses. Patients in the second group undergo stem cell mobilization and harvest with granulocyte colony-stimulating factor (G-CSF) followed within 10 weeks of surgery by high-dose chemotherapy with epirubicin and cyclophosphamide followed by peripheral blood stem cell rescue and G-CSF. All patients receive adjuvant tamoxifen, and patients who underwent lumpectomy prior to entry are required to receive adjuvant radiotherapy (radiotherapy is optional for patients who underwent mastectomy prior to entry). Patients are followed every 3 months for 2 years, then q 6 months for 3 years, then yearly.

PROJECTED ACCRUAL: 210 patients will be accrued over 4 years to provide 195 evaluable patients.

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
344
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Standard chemotherapyCMF regimenEC/AC x 4 followed by CMF x 3 and tamoxifen to 5 years after randomization.
Standard chemotherapycyclophosphamideEC/AC x 4 followed by CMF x 3 and tamoxifen to 5 years after randomization.
Standard chemotherapydoxorubicin hydrochlorideEC/AC x 4 followed by CMF x 3 and tamoxifen to 5 years after randomization.
Standard chemotherapyepirubicin hydrochlorideEC/AC x 4 followed by CMF x 3 and tamoxifen to 5 years after randomization.
Standard chemotherapyfluorouracilEC/AC x 4 followed by CMF x 3 and tamoxifen to 5 years after randomization.
Standard chemotherapymethotrexateEC/AC x 4 followed by CMF x 3 and tamoxifen to 5 years after randomization.
Standard chemotherapytamoxifen citrateEC/AC x 4 followed by CMF x 3 and tamoxifen to 5 years after randomization.
Standard chemotherapylow-LET electron therapyEC/AC x 4 followed by CMF x 3 and tamoxifen to 5 years after randomization.
Standard chemotherapylow-LET photon therapyEC/AC x 4 followed by CMF x 3 and tamoxifen to 5 years after randomization.
Dose-intensive ECfilgrastimHigh-dose EC x 3 supported by peripheral blood progenitor cells and tamoxifen to 5 years after randomization.
Dose-intensive ECmesnaHigh-dose EC x 3 supported by peripheral blood progenitor cells and tamoxifen to 5 years after randomization.
Dose-intensive ECtamoxifen citrateHigh-dose EC x 3 supported by peripheral blood progenitor cells and tamoxifen to 5 years after randomization.
Dose-intensive ECperipheral blood stem cell transplantationHigh-dose EC x 3 supported by peripheral blood progenitor cells and tamoxifen to 5 years after randomization.
Dose-intensive EClow-LET electron therapyHigh-dose EC x 3 supported by peripheral blood progenitor cells and tamoxifen to 5 years after randomization.
Dose-intensive EClow-LET photon therapyHigh-dose EC x 3 supported by peripheral blood progenitor cells and tamoxifen to 5 years after randomization.
Dose-intensive ECcyclophosphamideHigh-dose EC x 3 supported by peripheral blood progenitor cells and tamoxifen to 5 years after randomization.
Primary Outcome Measures
NameTimeMethod
Disease-free survival.16 years after randomization.

Time from randomization to recurrence (including recurrence isolated to the breast), metastasis, appearance of a second primary tumor, or death from any cause, whichever occurs first.

Secondary Outcome Measures
NameTimeMethod
Overall survival.16 years after randomization.

Time from randomization to death from any cause.

Toxicity.5 years after randomization.

Morbidity information was recorded using standard toxicity criteria.

Quality of life.16 years after randomization.

Quality of life was assessed using standard International Breast Cancer Study Group instruments.

Trial Locations

Locations (11)

Queen Elizabeth Hospital

🇦🇺

Adelaide, South Australia, Australia

Royal Prince Alfred Hospital, Sydney

🇦🇺

Sydney, New South Wales, Australia

Royal Adelaide Hospital

🇦🇺

Adelaide, South Australia, Australia

Newcastle Mater Misericordiae Hospital

🇦🇺

Newcastle, New South Wales, Australia

Royal Melbourne Hospital

🇦🇺

Parkville, Victoria, Australia

Swiss Institute for Applied Cancer Research

🇨🇭

Bern, Switzerland

Inselspital, Bern

🇨🇭

Bern, Switzerland

Centre Hospitalier Universitaire Vaudois

🇨🇭

Lausanne, Switzerland

Universitaetsspital

🇨🇭

Zurich, Switzerland

Istituto Oncologico della Svizzera Italiana

🇨🇭

Lugano, Switzerland

Kantonsspital - Saint Gallen

🇨🇭

Saint Gallen, Switzerland

© Copyright 2025. All Rights Reserved by MedPath