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Study of Vorasidenib (AG-881) in Participants With Residual or Recurrent Grade 2 Glioma With an IDH1 or IDH2 Mutation (INDIGO)

Phase 3
Active, not recruiting
Conditions
Grade 2 Glioma
Residual Glioma
Recurrent Glioma
Interventions
Drug: Matching Placebo
Registration Number
NCT04164901
Lead Sponsor
Institut de Recherches Internationales Servier
Brief Summary

Study AG881-C-004 is a phase 3, multicenter, randomized, double-blind, placebo-controlled study comparing the efficacy of vorasidenib to placebo in participants with residual or recurrent Grade 2 glioma with an IDH1 or IDH2 mutation who have undergone surgery as their only treatment. Participants will be required to have central confirmation of IDH mutation status prior to randomization. Approximately 340 participants are planned to be randomized 1:1 to receive orally administered vorasidenib 40 mg QD or placebo.

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
331
Inclusion Criteria
  • Be at least 12 years of age and weigh at least 40 kg.
  • Have Grade 2 oligodendroglioma or astrocytoma per WHO 2016 criteria.
  • Have had at least 1 prior surgery for glioma (biopsy, sub-total resection, gross-total resection), with the most recent surgery having occurred at least 1 year (-1 month) and not more than 5 years (+3 months) before the date of randomization, and no other prior anticancer therapy, including chemotherapy and radiotherapy and not be in need of immediate chemotherapy or radiotherapy in the opinion of the Investigator.
  • Have confirmed IDH1 (IDH1 R132H/C/G/S/L mutation variants tested) or IDH2 (IDH2 R172K/M/W/S/G mutation variants tested) gene mutation status disease by central laboratory testing during the Prescreening period and available 1p19q status by local testing (eg, fluorescence in situ hybridization [FISH], comparative genomic hybridization [CGH] array, sequencing) using an accredited laboratory.
  • Have MRI-evaluable, measurable, non-enhancing disease, as confirmed by the BIRC.
  • Have a Karnofsky Performance Scale (KPS) score (for participants ≥16 years of age) or Lansky Play Performance Scale (LPPS) score (for participants <16 years of age) of ≥80%.

Key

Exclusion Criteria
  • Have had any prior anticancer therapy other than surgery (biopsy, sub-total resection, gross-total resection) for treatment of glioma including systemic chemotherapy, radiotherapy, vaccines, small-molecules, IDH inhibitors, investigational agents, laser ablation, etc.
  • Have features assessed as high-risk by the Investigator, including brainstem involvement either as primary location or by tumor extension, clinically relevant functional or neurocognitive deficits due to the tumor in the opinion of the Investigator (deficits resulting from surgery are allowed), or uncontrolled seizures (defined as persistent seizures interfering with activities of daily life AND failed 3 lines of antiepileptic drug regimens including at least 1 combination regimen).

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
VorasidenibVorasidenibVorasidenib 40 mg, continuous daily dosing.
Matching PlaceboMatching PlaceboMatching placebo 40 mg, continuous daily dosing.
Primary Outcome Measures
NameTimeMethod
Progression-Free Survival (PFS)Up to approximately 30 months

PFS is defined as the time from date of randomization to date of first documented radiographic PD (as assessed by the blinded independent review committee (BIRC) per modified Response Assessment for Neuro-oncology for Low-Grade Gliomas or date of death due to any cause, whichever occurs earlier.

Secondary Outcome Measures
NameTimeMethod
Time to Next Intervention (TTNI)Up to approximately 3 years

TTNI is defined as the time from randomization to the initiation of the first subsequent anticancer therapy (including vorasidenib, for subjects randomized to placebo who subsequently cross over) or death due to any cause.

Tumor Growth Rate (TGR)every 6 months, up to 2 years and 9 months

Calculated as the mean of the percentage change in tumor volume every 6 months

Objective Response (OR) as Assessed by the Blinded Independent Review Committee (BIRC)approximatively 30 months

OR is defined as a best overall response (BOR) of Complete Response, Partial Rresponse, or minor Response as assessed by the BIRC per the modified Response Assessment in Neuro-oncology for Low-grade Gliomas (RANO-LGG).

Complete Response (CR) and Partial Response (PR) by BIRCApproximatively 30 months

CR and PR is defined as a BOR of CR or PR as assessed by BIRC per the modified RANO-LGG

Time to Response (TTR) by BIRCApproximatively 30 months

TTR is defined as the time from the date of randomization to the date of first documented CR, PR, or mR by BIRC per the modified RANO-LGG

Time to CR+PR by BIRCApproximatively 30 months

Time to CR+PR is defined as defined as the time from the date of randomization to the date of first documented CR or PR for subjects with CR or PR per the modified RANO-LGG (by BIRC)

Duration of Response (DoR)Approximatively 30 months

DoR is defined as the time from the date of first documented CR, PR, or mR to the date of death due to any cause or date of first documented radiographic Prgressive Disease, whichever occurred earlier

Duration of CR+PRApproximatively 30 months

Duration of CR+PR is defined as the time from the date of first documented CR or PR to the date of death due to any cause or first documented radiographic PD, whichever occurred earlier

Overall Survival (OS)Approximatively 30 months

OS wad defined as the time from the date of randomization to the date of death due to any cause or data cutoff.

Progression-Free Survival (PFS) by the InvestigatorApproximatively 30 months

PFS as assessed by the Investigator per the modified RANO-LGG

Health-Related Quality of Life (FACT-Br)Approximatively 30 months

Health-Related Quality of Life (HRQoL) Functional Assessment of Cancer Therapy-Brain (FACT-Br) is a 50-item measure comprising the following subscales: Physical Well-Being, Functional Well-Being, Emotional Well-Being, and Social Well-Being subscales from the FACT-General (FACT-G), with the addition of a 23-item brain tumor-specific subscale. These subscales are summed to provide a total score. The total score is given at the end of treatment and total scores range from 0 to 200. Higher scores indicate a better HRQoL

Trial Locations

Locations (84)

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

City of Hope

🇺🇸

Duarte, California, United States

University of California San Diego

🇺🇸

La Jolla, California, United States

UCLA Oncology Center

🇺🇸

Los Angeles, California, United States

University of California Irvine - Hospital

🇺🇸

Orange, California, United States

University of California San Francisco

🇺🇸

San Francisco, California, United States

Stanford Cancer Center

🇺🇸

Stanford, California, United States

University of Colorado Hospital - Anschutz Cancer Pavilion

🇺🇸

Aurora, Colorado, United States

Yale University, Yale Cancer Center

🇺🇸

New Haven, Connecticut, United States

Mayo Clinic Jacksonville

🇺🇸

Jacksonville, Florida, United States

Sylvester Comprehensive Cancer Center - University of Miami Hospital and Clinics

🇺🇸

Miami, Florida, United States

Northwestern University

🇺🇸

Chicago, Illinois, United States

University of Chicago

🇺🇸

Chicago, Illinois, United States

Indiana University Medical Center

🇺🇸

Indianapolis, Indiana, United States

University of Kansas Medical Center

🇺🇸

Kansas City, Kansas, United States

University of Kentucky

🇺🇸

Lexington, Kentucky, United States

Maine Medical Partners Neurology

🇺🇸

Scarborough, Maine, United States

John Hopkins Cancer Center

🇺🇸

Baltimore, Maryland, United States

Tufts Medical Center

🇺🇸

Boston, Massachusetts, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

University of Michigan Comprehensive Cancer Center

🇺🇸

Ann Arbor, Michigan, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

Metro Minnesota Community Oncology

🇺🇸

Minneapolis, Minnesota, United States

Mayo Comprehensive Cancer

🇺🇸

Rochester, Minnesota, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

Ohio State University Comprehensive Cancer Center

🇺🇸

Columbus, Ohio, United States

Oregon Health and Science University

🇺🇸

Portland, Oregon, United States

University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

University of Pittsburgh Hillman Cancer Center

🇺🇸

Pittsburgh, Pennsylvania, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Tennessee Oncology

🇺🇸

Nashville, Tennessee, United States

Baylor University Medical Center

🇺🇸

Dallas, Texas, United States

University of Texas Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

The University of Utah, Huntsman Cancer Hospital

🇺🇸

Salt Lake City, Utah, United States

Seattle Cancer Care Alliance

🇺🇸

Seattle, Washington, United States

BC Cancer Agency

🇨🇦

Vancouver, British Columbia, Canada

London Health Sciences Centre

🇨🇦

London, Ontario, Canada

Sunnybrook Health Sciences Centre

🇨🇦

Toronto, Ontario, Canada

Princess Margaret Hospital

🇨🇦

Toronto, Ontario, Canada

McGill University Health Center

🇨🇦

Montreal, Quebec, Canada

Centre Hospitalier Universitaire de Lille

🇫🇷

Lille, France

Hôpital Pierre Wertheimer

🇫🇷

Lyon, France

Hopitaux de La Timone

🇫🇷

Marseille, France

Hospitalier Pitié Salpétrière

🇫🇷

Paris, France

Universitätsklinikum Essen

🇩🇪

Essen, Germany

Universitätsklinikum Hamburg Eppendorf

🇩🇪

Hamburg, Germany

Universitätsklinikum Heidelberg

🇩🇪

Heidelberg, Germany

Klinikum Mannheim Universitätsklinikum

🇩🇪

Mannheim, Germany

Hadassah Medical Center

🇮🇱

Jerusalem, Israel

Rabin Medical Center

🇮🇱

Petah Tikva, Israel

Chaim Sheba Medical Center

🇮🇱

Ramat-Gan, Israel

Tel Aviv Sourasky Medical Center

🇮🇱

Tel Aviv, Israel

Azienda Ospedaliera Città della Salute e della Scienza di Torino

🇮🇹

Torino, Piemonte, Italy

Ospedale Bellaria

🇮🇹

Bologna, Italy

Istituto Oncologico Veneto - I.R.C.C.S.

🇮🇹

Padua, Italy

Istituto Nazionale Tumori Regina Elena

🇮🇹

Roma, Italy

Istituto Clinico Humanitas

🇮🇹

Rozzano, Italy

Nagoya University Hospital

🇯🇵

Nagoya, Aichi, Japan

Fujita Health University Hospital

🇯🇵

Toyoake, Aichi, Japan

Hiroshima University Hospital

🇯🇵

Minami-Ku, Hiroshima, Japan

The University of Tokyo Hospital

🇯🇵

Bunkyō-Ku, Tokyo, Japan

National Cancer Center Hospital

🇯🇵

Chuo Ku, Tokyo, Japan

Kumamoto University Hospital

🇯🇵

Kumamoto, Japan

University Hospital, Kyoto Prefectural University of Medicine

🇯🇵

Kyoto, Japan

Kyoto University Hospital

🇯🇵

Kyoto, Japan

Okayama University Hospital

🇯🇵

Okayama, Japan

Haaglanden MC, Antoniushove

🇳🇱

Leidschendam, Zuid-Holland, Netherlands

Erasmus Medical Center

🇳🇱

Rotterdam, Netherlands

Universitair Medisch Centrum Utrecht

🇳🇱

Utrecht, Netherlands

Hospital Universitario Vall d'Hebrón

🇪🇸

Barcelona, Spain

Hospital Universitario Ramon y Cajal

🇪🇸

Madrid, Spain

Hospital Universitario 12 de Octubre

🇪🇸

Madrid, Spain

Hôpitaux Universitaire de Genève

🇨🇭

Geneva, Switzerland

Centre Hospitalier Universitaire Vaudois

🇨🇭

Lausanne, Switzerland

Universitätsspital Zürich

🇨🇭

Zürich, Switzerland

Freeman Hospital

🇬🇧

Newcastle Upon Tyne, England, United Kingdom

The Royal Marsden NHS Foundation Trust

🇬🇧

Sutton, Surrey, United Kingdom

Western General Hospital Edinburgh - PPDS

🇬🇧

Edinburgh, United Kingdom

The Christie NHS Foundation Trust

🇬🇧

Manchester, United Kingdom

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