MedPath

Long-Term Safety Study of Elagolix in Combination With Estradiol/Norethindrone Acetate for the Management of Heavy Menstrual Bleeding Associated With Uterine Fibroids in Premenopausal Women

Phase 3
Completed
Conditions
Uterine Fibroids
Heavy Menstrual Bleeding
Interventions
Other: Elagolix Placebo
Other: E2/NETA Placebo
Registration Number
NCT03271489
Lead Sponsor
AbbVie
Brief Summary

This is phase 3b study seeks to evaluate the safety of elagolix in combination with estradiol/norethindrone acetate for the management of heavy menstrual bleeding associated with uterine fibroids in premenopausal women. This study is double-blinded in the first year and an open-label for the next three years.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
478
Inclusion Criteria
  • Participant is a premenopausal female at the time of Screening.
  • Participant has a diagnosis of uterine fibroids documented by a Pelvic Ultrasound [Transabdominal ultrasound (TAU) and transvaginal ultrasound (TVU)].
  • Participant has Heavy Menstrual Bleeding (HMB) associated with uterine fibroids as evidenced by Menstrual Blood Loss (MBL) > 80 mL during each of two screening menses as measured by the alkaline hematin method.
  • Participant has negative urine and/or serum pregnancy test during Washout (if applicable) and/or Screening and just prior to first dose.
  • Participant has an adequate endometrial biopsy performed during Screening, the results of which show no clinical significant endometrial pathology.
Exclusion Criteria
  • Participant has screening pelvic ultrasound or Saline Infusion Sonohysterography (SIS) results that show a clinically significant gynecological disorder.
  • Participant has history of osteoporosis or other metabolic bone disease.
  • Participant has clinically significant abnormalities in clinical chemistry, hematology, or urinalysis.
  • Participant has a history of major depression or post-traumatic stress disorder (PTSD) episode within 2 years of screening, OR a history of other major psychiatric disorder at any time (e.g., schizophrenia, bipolar disorder).
  • Participant is using any systemic corticosteroids for over 14 days within 3 months prior to Screening or is likely to require treatment with systemic corticosteroids during the course of the study. Over the counter and prescription topical, inhaled, intranasal or intra-articular injectable (for occasional use) corticosteroids are allowed.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboElagolix PlaceboPlacebo
Elagolix plus estradiol (E2)/norethindrone acetate (NETA)ElagolixElagolix plus estradiol (E2)/norethindrone acetate (NETA)
PlaceboE2/NETA PlaceboPlacebo
Elagolix plus estradiol (E2)/norethindrone acetate (NETA)E2/NETAElagolix plus estradiol (E2)/norethindrone acetate (NETA)
Primary Outcome Measures
NameTimeMethod
Number of Participants with Adverse Events (AEs)Month 60

An AE is defined as any untoward medical occurrence in a patient or clinical investigation in which a participant is administered a pharmaceutical product which does not necessarily have a causal relationship with this treatment.

Secondary Outcome Measures
NameTimeMethod
Change in Bone Mineral Density (BMD)From Baseline through Month 60

Bone mineral density (BMD) is measured by dual X-ray absorptiometry (DXA).

Trial Locations

Locations (157)

Exordia Medical Research, Inc /ID# 160853

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Fall River, Massachusetts, United States

Health care Affiliates Medical Group /ID# 163324

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Santa Ana, California, United States

Duplicate_Northwell Health System - Manhasset /ID# 201058

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Manhasset, New York, United States

Discovery Clinical Trials -HCWC /ID# 161543

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Dallas, Texas, United States

Houston Ctr for Clin Research /ID# 160837

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Sugar Land, Texas, United States

Mount Vernon Clinical Res, LLC /ID# 161491

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Atlanta, Georgia, United States

Atlanta Women's Research Institute /ID# 160844

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Atlanta, Georgia, United States

Moore for Women Healthcare and Wellness Institute, LLC /ID# 167118

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Chicago, Illinois, United States

Duplicate_University of Chicago /ID# 162667

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Chicago, Illinois, United States

Central Ohio Clinical Research /ID# 201162

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Columbus, Ohio, United States

Invictus Clinical Research Group,LLC /ID# 160925

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Miami, Florida, United States

Healthcare Clinical Data, Inc /ID# 160888

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Miami, Florida, United States

Palmetto Professional Research /ID# 161442

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Miami, Florida, United States

Vista Health Research, LLC /ID# 163044

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Miami, Florida, United States

Centex Studies, Inc /ID# 163858

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Houston, Texas, United States

Centex Studies, Inc. - Houston /ID# 160917

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Houston, Texas, United States

UAG Innovation Women Research, /ID# 167415

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Houston, Texas, United States

America's Adv. Wellness Center /ID# 167548

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Houston, Texas, United States

Private practice: Dr. Rex G. Mabey JR /ID# 160915

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Las Vegas, Nevada, United States

Wayne State University /ID# 160944

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Detroit, Michigan, United States

Carolina Women's Research and Wellness Center /ID# 160914

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Durham, North Carolina, United States

Duplicate_CTI Clinical Research Center /ID# 160942

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Cincinnati, Ohio, United States

Clinical Trials of Texas, Inc /ID# 161510

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San Antonio, Texas, United States

Precision Research Institute - San Diego /ID# 163069

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San Diego, California, United States

VIP Trials /ID# 161546

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San Antonio, Texas, United States

Womens & Family Care, LLC dba /ID# 160890

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Shawnee Mission, Kansas, United States

MD Strategies Research Centers /ID# 161544

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San Diego, California, United States

Alabama Clinical Therapeutics /ID# 160927

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Birmingham, Alabama, United States

Alabama Clinical Therapeutics /ID# 160835

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Birmingham, Alabama, United States

Emerson Clinical Research Inst /ID# 162181

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Washington, District of Columbia, United States

Mesa Obstetricians and Gynecologists /ID# 160955

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Mesa, Arizona, United States

Willis-Knighton Pediatric GI S /ID# 161534

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Shreveport, Louisiana, United States

Research Memphis Associates, LLC /ID# 160939

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Memphis, Tennessee, United States

Noble Clinical Research /ID# 166949

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Tucson, Arizona, United States

VitaLink Research-Spartanburg /ID# 164592

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Spartanburg, South Carolina, United States

Jersey Shore University Medical Center /ID# 160916

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Neptune, New Jersey, United States

Vista Clinical Research /ID# 160946

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Columbia, South Carolina, United States

Excel Clinical Research /ID# 165588

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Las Vegas, Nevada, United States

The Jackson Clinic, PA /ID# 162496

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Jackson, Tennessee, United States

Oregon Medical Research Center /ID# 161514

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Portland, Oregon, United States

GCP Clinical Research, LLC /ID# 164593

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Tampa, Florida, United States

University of South Florida- Neuroscience Institute /ID# 160960

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Tampa, Florida, United States

Jedidiah Clinical Research /ID# 167114

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Tampa, Florida, United States

Choice Research, LLC /ID# 161498

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Dothan, Alabama, United States

E Squared Research /ID# 163645

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Huntsville, Alabama, United States

Mobile, OBGYN P.C. /ID# 161530

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Mobile, Alabama, United States

Southern Women's Specialists PC /ID# 161531

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Fairhope, Alabama, United States

Women's Health Alliance of Mobile /ID# 161443

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Mobile, Alabama, United States

Vision's Clinical Research-Tucson /ID# 161508

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Tucson, Arizona, United States

Duplicate_Core Healthcare Group /ID# 160858

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Cerritos, California, United States

Eclipse Clinical Research /ID# 161516

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Tucson, Arizona, United States

Diagnamics Inc. /ID# 160950

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Encinitas, California, United States

SC Clinical Research /ID# 164395

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Garden Grove, California, United States

National Research Institute /ID# 160952

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Los Angeles, California, United States

HRC Fertility /ID# 161493

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Encino, California, United States

Grossmont Ctr Clin Research /ID# 165120

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La Mesa, California, United States

Olympia Clinical Trials /ID# 201562

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Los Angeles, California, United States

Duplicate_Duplicate_Marvel Clinical Research /ID# 167297

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Huntington Beach, California, United States

California Medical Research Associates /ID# 161481

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Northridge, California, United States

Futura Research, Org /ID# 160924

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Montebello, California, United States

Advanced RX Clinical Research /ID# 161599

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Westminster, California, United States

Alta California Medical Group /ID# 163564

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Simi Valley, California, United States

Bayview Research Group LLC /ID# 161484

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Valley Village, California, United States

Upland Clinical Research /ID# 164528

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Upland, California, United States

James A. Simon, MD, PC /ID# 160931

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Washington, District of Columbia, United States

Omega Research Maitland, LLC /ID# 160857

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DeBary, Florida, United States

Brandon Premier Health Care, PA/Gulf Coast Research Group, LLC /ID# 160910

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Brandon, Florida, United States

Women's Health Partners /ID# 203577

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Boca Raton, Florida, United States

David Lubetkin MD LLC /ID# 203578

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Boca Raton, Florida, United States

Midland Florida Clinical Research Center /ID# 161487

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DeLand, Florida, United States

KO Clinical Research, LLC /ID# 160928

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Fort Lauderdale, Florida, United States

Sweet Hope Research Specialty Inc /ID# 163522

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Hialeah, Florida, United States

Solutions Through Adv Rch /ID# 160935

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Jacksonville, Florida, United States

Altus Research, Inc /ID# 160912

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Lake Worth, Florida, United States

Wellington Anti-Aging Centre /ID# 203540

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Loxahatchee Groves, Florida, United States

South Florida Wellness & Clinic /ID# 161535

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Margate, Florida, United States

Ocean Blue Medical Research Center, Inc /ID# 161549

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Miami Springs, Florida, United States

Duplicate_Precision Research Organization /ID# 161522

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Miami Lakes, Florida, United States

Salom Tangir, LLC /ID# 162542

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Miramar, Florida, United States

Advanced Research Institute, Inc /ID# 163748

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New Port Richey, Florida, United States

A Premier Medical Research of FL /ID# 201882

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Orange City, Florida, United States

Oncova Clinical Research, Inc. /ID# 160937

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Saint Cloud, Florida, United States

Accel Research Sites - St Petersburg Clinical Research Unit /ID# 160913

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Saint Petersburg, Florida, United States

Treasure Coast Research /ID# 161824

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Stuart, Florida, United States

Precision Clinical Research /ID# 165377

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Sunrise, Florida, United States

Discovery Clinical Research /ID# 160891

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Sunrise, Florida, United States

Virtus Research Consultants, LLC /ID# 160855

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Wellington, Florida, United States

Comprehensive Clinical Trials LLC /ID# 161479

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West Palm Beach, Florida, United States

Journey Medical Research Insti /ID# 160958

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Alpharetta, Georgia, United States

Paramount Research Solutions /ID# 161557

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Alpharetta, Georgia, United States

Medisense Inc /ID# 161494

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Atlanta, Georgia, United States

Bingham Memorial Hospital /ID# 201130

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Blackfoot, Idaho, United States

AGILE Clinical Research Trials /ID# 160941

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Atlanta, Georgia, United States

Duplicate_Atlanta Gynecology Research Institute /ID# 160851

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Suwanee, Georgia, United States

Sonora Clinical Research /ID# 167610

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Meridian, Idaho, United States

Leavitt Womens Healthcare /ID# 163419

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Idaho Falls, Idaho, United States

Womens Healthcare Assoc, DBA /ID# 160933

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Idaho Falls, Idaho, United States

Asr, Llc /Id# 162179

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Nampa, Idaho, United States

Women's Health Advantage /ID# 161537

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Fort Wayne, Indiana, United States

Alliance for Multispecialty Research, LLC /ID# 160932

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Oak Brook, Illinois, United States

Women's Health Practice, LLC /ID# 161553

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Champaign, Illinois, United States

Clinical Trials Management, LLC - Covington /ID# 160838

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Covington, Louisiana, United States

Praetorian Pharmaceutical Research /ID# 161532

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Marrero, Louisiana, United States

Clinical Trials Management, LLC - Covington /ID# 160893

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Covington, Louisiana, United States

Duplicate_Great Lakes Research Group, Inc. /ID# 161511

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Bay City, Michigan, United States

Saginaw Valley Med Res Group /ID# 160840

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Saginaw, Michigan, United States

Valley OB-Gyn Clinic - Saginaw /ID# 203579

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Saginaw, Michigan, United States

Quad Clinical Research, LLC /ID# 200943

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Saint Louis, Missouri, United States

Office of Edmond E. Pack, MD /ID# 162604

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Las Vegas, Nevada, United States

SUNY Downstate Medical Center /ID# 160922

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Brooklyn, New York, United States

Hamburg Regional Gynecology Gr /ID# 161427

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Orchard Park, New York, United States

Columbia Univ Medical Center /ID# 161519

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New York, New York, United States

DJL Clinical Research, PLLC /ID# 161548

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Charlotte, North Carolina, United States

Wake Radiology UNC REX Healthcare - Raleigh Office /ID# 161490

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Raleigh, North Carolina, United States

Clinical Inquest Center Ltd /ID# 160892

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Beavercreek, Ohio, United States

Univ Hosp Cleveland /ID# 160953

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Cleveland, Ohio, United States

Duplicate_Optimed Research /ID# 165600

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Columbus, Ohio, United States

Hilltop Obstetrics & Gynecology /ID# 203576

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Middletown, Ohio, United States

University of Toledo /ID# 160923

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Toledo, Ohio, United States

OB/GYN Associates of Erie /ID# 161541

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Erie, Pennsylvania, United States

Penn State University and Milton S. Hershey Medical Center /ID# 160896

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Hershey, Pennsylvania, United States

University of Pennsylvania /ID# 160936

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Philadelphia, Pennsylvania, United States

DUP_Thomas Jefferson University /ID# 200304

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Philadelphia, Pennsylvania, United States

WR-ClinSearch /ID# 160887

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Chattanooga, Tennessee, United States

Duplicate_The University of Texas Southwestern Medical Center /ID# 161496

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Dallas, Texas, United States

The Woman's Hospital of Texas /ID# 160959

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Houston, Texas, United States

Baylor Scott & White /ID# 161515

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Fort Worth, Texas, United States

Willowbend Health and Wellness - Frisco /ID# 160954

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Frisco, Texas, United States

The Ob/Gyn Center /ID# 165928

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Houston, Texas, United States

Precision Research Institute, LLC /ID# 161554

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Houston, Texas, United States

ClinRx Research, LLC /ID# 201170

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Plano, Texas, United States

FMC Science /ID# 160886

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Lampasas, Texas, United States

Advances in Health, Inc. /ID# 160930

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Pearland, Texas, United States

The Univ Texas HSC at Tyler /ID# 161533

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Tyler, Texas, United States

Center of Reproductive Medicine /ID# 162498

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Webster, Texas, United States

Univ of Virgnia Medical center /ID# 166283

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Charlottesville, Virginia, United States

Clinical Research Partners /ID# 160948

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North Chesterfield, Virginia, United States

Eastern Virginia Med School /ID# 160856

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Norfolk, Virginia, United States

Clinical Research Partners /ID# 160929

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North Chesterfield, Virginia, United States

Specialists for Women /ID# 201129

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Suffolk, Virginia, United States

School of Medicine University of Puerto Rico-Medical Science Campus /ID# 160862

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San Juan, Puerto Rico

Henry A. Rodriguez Ginorio, MD /ID# 160861

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San Juan, Puerto Rico

Tidewater Clinical Research /ID# 160949

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Virginia Beach, Virginia, United States

Physician Care Clin. Res., LLC /ID# 161547

🇺🇸

Sarasota, Florida, United States

Duplicate_Chattanooga Medical Research /ID# 160885

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Chattanooga, Tennessee, United States

Unified Women's Clinical Resea /ID# 163014

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Raleigh, North Carolina, United States

Clinical Associates of Orlando /ID# 160889

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Orlando, Florida, United States

Northern California Research /ID# 161561

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Sacramento, California, United States

Bluegrass Clinical Research /ID# 163485

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Louisville, Kentucky, United States

Ochsner Baptist Medical Centre /ID# 161507

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New Orleans, Louisiana, United States

OBGYN North /ID# 203580

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Austin, Texas, United States

Clinical Trials Virginia, Inc. /ID# 160943

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Richmond, Virginia, United States

Women Under Study, LLC /ID# 163990

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New Orleans, Louisiana, United States

Unified Women's Clinical Resea /ID# 160957

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Winston-Salem, North Carolina, United States

Austin Area Obstetrics, Gynecology, and Fertility /Id# 203542

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Austin, Texas, United States

Lovelace Scientific Resources /ID# 163644

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Albuquerque, New Mexico, United States

Bosque Women's Care /ID# 162606

🇺🇸

Albuquerque, New Mexico, United States

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