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Growing into adulthood with Duchenne Muscular Dystrophy – comparing patient experiences and systems to optimize care

Recruiting
Registration Number
DRKS00029270
Lead Sponsor
European Joint Programme for Rare Diseases
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
Male
Target Recruitment
650
Inclusion Criteria

Patients with the diagnosis DMD (age 15-25 years old), their relatives and the health care professionals involved in the transition process, living in Canada, Germany, and Italy.

Exclusion Criteria

Patients with other diagnosis, siblings; and other professionals (e.g. teacher)

Study & Design

Study Type
observational
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
In the qualitative comparison, differences and similarities on the level of patients/relatives and care organizations with regard to the implementation of transition guidelines will be examined.
Secondary Outcome Measures
NameTimeMethod
In the quantitative part, different quantifiable transition-aspects from the patient-view point will be assessed through standardized questionnaires. Differences between the three different countries as well as between three different age groups will be examined.
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