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2nd Autologous Stem Cell Transplant in Patients With Persistent/Recurrent (AL) Amyloidosis

Phase 2
Terminated
Conditions
Plasma Cell Neoplasm
Multiple Myeloma
Interventions
Biological: filgrastim
Procedure: autologous stem cell transplantation
Procedure: stem cell infusion
Registration Number
NCT00075608
Lead Sponsor
Boston Medical Center
Brief Summary

RATIONALE: Drugs used in chemotherapy work in different ways to stop the growth of plasma cells, either by killing the cells or by stopping them from dividing. Having a stem cell transplant to replace the blood-forming cells destroyed by chemotherapy, allows higher doses of chemotherapy to be given so that more plasma cells are killed. By reducing the number of plasma cells, the disease may progress more slowly.

PURPOSE: This phase II trial is studying how well autologous stem cell transplant works in treating patients with persistent or recurrent primary systemic (AL) amyloidosis.

Detailed Description

OBJECTIVES:

* Determine the feasibility and tolerability of second autologous stem cell transplantation in patients with persistent or recurrent AL amyloidosis.

* Determine the response rate and durability of response in patients treated with this regimen.

* Determine immune reconstitution in patients treated with this regimen.

OUTLINE:

* Mobilization: Patients receive filgrastim (G-CSF) subcutaneously (SC) once daily beginning before the initiation of stem cell collection and continuing until the day before the completion of stem cell collection.

* Preparative regimen: Patients receive high-dose melphalan IV over 20 minutes on days -3 and -2.

* Autologous stem cell transplantation: Autologous stem cells are reinfused on day 0.

Patients are followed at 6 months, 1 year, and then annually thereafter.

PROJECTED ACCRUAL: A total of 19 patients will be accrued for this study within 5-6 years.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
12
Inclusion Criteria

Not provided

Exclusion Criteria
  • No myelodysplastic syndromes
  • No abnormal bone marrow cytogenetics

Other

  • Not pregnant or nursing
  • Fertile patients must use effective contraception
  • Acceptable toxicity from first transplantation, confirmed by the transplant team
  • HIV negative
  • No other concurrent malignancy except treated skin cancer

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
2nd Stem Cell TransplantfilgrastimMobilization with filgrastim autologous stem cell transplantation with melphalan conditioning stem cell infusion
2nd Stem Cell Transplantautologous stem cell transplantationMobilization with filgrastim autologous stem cell transplantation with melphalan conditioning stem cell infusion
2nd Stem Cell Transplantstem cell infusionMobilization with filgrastim autologous stem cell transplantation with melphalan conditioning stem cell infusion
2nd Stem Cell TransplantmelphalanMobilization with filgrastim autologous stem cell transplantation with melphalan conditioning stem cell infusion
Primary Outcome Measures
NameTimeMethod
Feasibility and Tolerability3 months after treatment and annually

Feasibility and tolerability will be evaluated based on participants completing second transplant with tolerable adverse events

Response and Durability of Response3 months after treatment and annually

Response and durability of response will be based on hematologic Complete Response or Partial Response and date of relapse or death

Evaluate Immune Reconstitution3 months after treatment and annually

Evaluate immune reconstitution based on time to engraftment

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

Boston University Cancer Research Center

🇺🇸

Boston, Massachusetts, United States

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