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A Study Evaluating the Efficacy and Safety of Inavolisib + Palbociclib + Fulvestrant vs Placebo + Palbociclib + Fulvestrant in Patients With PIK3CA-Mutant, Hormone Receptor-Positive, HER2-Negative, Locally Advanced or Metastatic Breast Cancer

Phase 2
Active, not recruiting
Conditions
Breast Cancer
Interventions
Registration Number
NCT04191499
Lead Sponsor
Hoffmann-La Roche
Brief Summary

This study will evaluate the efficacy, safety, and pharmacokinetics of inavolisib in combination with palbociclib and fulvestrant compared with placebo plus palbociclib and fulvestrant in participants with PIK3CA-mutant, hormone receptor (HR)-positive, HER2-negative locally advanced or metastatic breast cancer whose disease progressed during treatment or within 12 months of completing adjuvant endocrine therapy and who have not received prior systemic therapy for metastatic disease.

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
325
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Inavolisib + Palbociclib + FulvestrantInavolisibParticipants will receive inavolisib, palbociclib, and fulvestrant.
Inavolisib + Palbociclib + FulvestrantPalbociclibParticipants will receive inavolisib, palbociclib, and fulvestrant.
Inavolisib + Palbociclib + FulvestrantFulvestrantParticipants will receive inavolisib, palbociclib, and fulvestrant.
Placebo + Palbociclib + FulvestrantPlaceboParticipants will receive placebo, palbociclib, and fulvestrant.
Placebo + Palbociclib + FulvestrantPalbociclibParticipants will receive placebo, palbociclib, and fulvestrant.
Placebo + Palbociclib + FulvestrantFulvestrantParticipants will receive placebo, palbociclib, and fulvestrant.
Primary Outcome Measures
NameTimeMethod
Progression-Free Survival (PFS)Up to 3.7 years

PFS was defined as the time from randomization to the first occurrence of disease progression, as determined by the investigator according to Response Evaluation Criteria in Solid Tumors (RECIST), Version 1.1 or death from any cause (whichever occurs first). Progressive disease (PD) was defined as at least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum in the study, including baseline, in addition to the relative increase of 20%, the sum must also demonstrate an absolute increase of at least 5 millimeter (mm). The appearance of one or more new lesions was also considered progression. Data for participants without the occurrence of PD or death as of the clinical cutoff date (CCOD) were censored at the time of the last tumor assessment prior to the CCOD. Median PFS was calculated using the Kaplan-Meier methodology.

Secondary Outcome Measures
NameTimeMethod
Percentage of Participants With Objective Response Rate (ORR)Up to approximately 6 years

ORR is defined as the percentage of participants with a complete response (CR) and/or partial response (PR) on at least two consecutive occasions ≥ 4 weeks apart, as determined by the investigator according to RECIST v1.1. CR is defined as the disappearance of all target lesions or any pathological lymph nodes (whether target or non-target) having a reduction in short axis to \<10 mm. PR is defined as at least a 30% decrease in the sum of diameters of target lesions, taking as reference the smallest sum in the study (nadir), including baseline.

Percentage of Participants With Best Overall Response Rate (BOR)Up to approximately 6 years

BOR is defined as the percentage of participants with a CR or PR, as determined by the investigator according to RECIST v1.1. CR is defined as the disappearance of all target lesions or any pathological lymph nodes (whether target or non-target) having a reduction in short axis to \<10 mm. PR is defined as at least a 30% decrease in the sum of diameters of target lesions, taking as reference the smallest sum in the study (nadir), including baseline.

Duration of Response (DOR)Up to approximately 6 years

DOR is defined as the time from the first occurrence of a CR or PR to the first occurrence of disease progression as determined by the investigator according to RECIST v1.1, or death from any cause (whichever occurs first). CR is defined as the disappearance of all target lesions or any pathological lymph nodes (whether target or non-target) having a reduction in short axis to \<10 mm. PR is defined as at least a 30% decrease in the sum of diameters of target lesions, taking as reference the smallest sum in the study (nadir), including baseline. PD is defined as at least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum in the study, including baseline, in addition to the relative increase of 20%, the sum must also demonstrate an absolute increase of at least 5 mm. The appearance of one or more new lesions is also considered progression.

Percentage of Participants With Clinical Benefit Rate (CBR)Up to approximately 6 years

CBR is defined as the percentage of participants with a CR, PR, and/or stable disease (SD) for at least 24 weeks, as determined by the investigator according to RECIST v1.1. CR= disappearance of all target lesions or any pathological lymph nodes (whether target or non-target) having a reduction in short axis to \<10 mm. PR=at least a 30% decrease in the sum of diameters of target lesions, taking as reference the smallest sum in the study (nadir), including baseline. PD=at least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum in the study (nadir), including baseline. In addition to the relative increase of 20%, the sum must also demonstrate an absolute increase of at least 5 mm. The appearance of one or more new lesions is also considered progression. SD=neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for PD, taking as reference the smallest sum in the study.

Overall Survival (OS)Up to approximately 6 years

OS is defined as the time from randomization to death from any cause.

Time to Deterioration (TTD) in PainFrom randomization to first documentation of a ≥ 2-point increase (Up to approximately 6 years)

TTD in pain is defined as the time from randomization to the first documentation of a ≥ 2-point increase from baseline on the "worst pain" item from the Brief Pain Inventory-Short Form (BPI-SF). BPI-SF is a self-administered questionnaire in which the participant was asked to rate severity on a 10-point scale where 0 represents 'No pain/No interference' and 10 represents 'Pain/Interference as bad as you can imagine'. A ≥2-point change is defined as clinically meaningful difference.

TTD in Physical Function (PF)Treatment: Day 1 of Cycles 1-3, then Day 1 of every other cycle until treatment discontinuation. Post-treatment: Every 8 weeks for 2 years, then every 12 weeks thereafter, to end of study (up to 6 years) (Cycle length = 28 days)]

TTD in physical function is defined as the time from randomization to the first documentation of a ≥ 10-point decrease from baseline held for two consecutive cycles or initial decrease followed by death or treatment discontinuation within three weeks of last assessment in the European Organisation for Research and Treatment of Cancer Quality of Life-Core 30 Questionnaire (EORTC QLQ-C30) PF scale (items 1-5). A ≥10-point change is defined as a clinically meaningful difference. EORTC QLQ-C30 is a cancer-specific health-related quality-of life (QoL) questionnaire with 30 questions. For the PF scale, participant responses to 5 questions about daily activities (strenuous activities, long walks, short walks, bed/chair rest \& needing help with eating, dressing, washing themselves, or using the toilet) is scored on a 4-point scale (1=Not at All to 4=Very Much). Scores are linearly transformed on a scale of 0 to 100, with a high score indicating worst functioning.

TTD in Role Function (RF)Treatment: Day 1 of Cycles 1-3, then Day 1 of every other cycle until treatment discontinuation. Post-treatment: Every 8 weeks for 2 years, then every 12 weeks thereafter, to end of study (up to 6 years) (Cycle length = 28 days)]

TTD in Role Function is defined as the time from randomization to the first documentation of a ≥ 10-point decrease from baseline held for two consecutive cycles, or initial decrease followed by death or treatment discontinuation within three weeks of last assessment in the EORTC QLQ-C30 RF scale (items 6 and 7). A ≥10-point change is defined as clinically meaningful difference. EORTC QLQ-C30 is a cancer specific health-related QoL questionnaire. For the role functioning scale, participant responses to the 2 questions "Q6: Were you limited in doing either your work or daily activities" and "Q7: Were you limited in pursuing your hobbies or other leisure time activities" were scored on a 4-point scale (1=Not at All to 4=Very Much). The scores were linearly transformed on a scale of 0 to 100, with a low score indicating better functioning.

TTD in Global Health Status (GHS)Treatment: Day 1 of Cycles 1-3, then Day 1 of every other cycle until treatment discontinuation. Post-treatment: Every 8 weeks for 2 years, then every 12 weeks thereafter, to end of study (up to 6 years) (Cycle length = 28 days)]

TTD in (GHS)/health-related quality of life (HRQoL) is defined as the time from randomization to the first documentation of a ≥ 10-point decrease from baseline held for two consecutive cycles, or initial decrease followed by death or treatment discontinuation within three weeks of last assessment in the EORTC QLQ-30 GHS/HRQoL scale. A ≥10-point change is defined as clinically meaningful difference. EORTC QLQ-C30 is a cancer specific health-related QoL questionnaire. Participant responses to the questions regarding Global Health Status (Q29: GHS; "How would you rate your overall health during the past week?") and Quality of Life (Q30: QoL; "How would you rate your overall quality of life during the past week?") are scored on a 7-point scale (1= Very poor to 7=Excellent). Using linear transformation, raw scores are standardized, so that scores range from 0 to 100. A higher score indicates a better outcome.

Number of Participants With Adverse Events (AEs)Up to approximately 6 years

An AE is an untoward medical occurrence in participant administered a pharmaceutical product \& regardless of causal relationship with this treatment. An AE can therefore be any unfavorable \& unintended sign (including an abnormal laboratory finding), symptom/disease temporally associated with use of investigational product, whether or not considered related to investigational product.

Plasma Concentration of InavolisibPredose on Cycle 1 Days 1, 8 and 15 and Cycle 2 Day 15; 3 hours post-dose on Cycle 1 Days 1 and 15 (Cycle length = 28 days)
Plasma Concentration of PalbociclibPredose on Cycle 1 Days 1, 8 and 15 and Cycle 2 Day 15; 3 hours post-dose on Cycle 1 Days 1 and 15 (Cycle length = 28 days)
Plasma Concentration of FulvestrantPredose on Cycle 1 Days 1, 8 and 15 and Cycle 2 Day 15; 3 hours post-dose on Cycle 1 Days 1 and 15 (Cycle length = 28 days)

Trial Locations

Locations (138)

Hopital du Saint Sacrement

🇨🇦

Quebec City, Quebec, Canada

Beijing Cancer Hospital

🇨🇳

Beijing, China

The First Hospital of Jilin University

🇨🇳

Changchun City, China

West China Hospital, Sichuan University

🇨🇳

Chengdu, China

The First Affiliated Hospital, Chongqing Medical University

🇨🇳

Chongqing, China

Fujian Medical University Union Hospital

🇨🇳

Fujian, China

Sun Yet-sen University Cancer Center

🇨🇳

Guangzhou, China

Zhejiang Cancer Hospital

🇨🇳

Hangzhou, China

Harbin Medical University Cancer Hospital

🇨🇳

Harbin, China

Jasz-Nagykun-Szolnok Megyei Hetenyi Geza Korhaz-Rendelointezet

🇭🇺

Szolnok, Hungary

Azienda Ospedaliera Universitaria Federico II

🇮🇹

Napoli, Campania, Italy

A.O. Universitaria Di Parma

🇮🇹

Parma, Emilia-Romagna, Italy

Az. Osp. Spedali Civili

🇮🇹

Brescia, Lombardia, Italy

Narodowy Inst.Onkologii im.Sklodowskiej-Curie Panstw.Inst.Bad

🇵🇱

Warszawa, Poland

Centro Clinico Champalimaud

🇵🇹

Lisboa, Portugal

IPO do Porto

🇵🇹

Porto, Portugal

Regional Clinical Oncology Hospital

🇷🇺

Yaroslavl, Russian Federation

National Cancer Centre

🇸🇬

Singapore, Singapore

Hospital Universitari Germans Trias i Pujol

🇪🇸

Badalona, Barcelona, Spain

Clinica Universitaria de Navarra

🇪🇸

Pamplona, Navarra, Spain

ME Kryviy Rih Oncology Dispensary of Dnipropetrovs?k Regional Council

🇺🇦

Kryvyi Rih, Ukraine

Kyiv City Clinical Oncological Center

🇺🇦

Kyiv, Ukraine

Royal Marsden Hospital - Fulham

🇬🇧

London, United Kingdom

Mount Vernon Hospital

🇬🇧

Northwood, United Kingdom

Churchill Hospital

🇬🇧

Oxford, United Kingdom

Derriford Hospital

🇬🇧

Plymouth, United Kingdom

Royal Marsden Hosp NHS Fnd

🇬🇧

Sutton, United Kingdom

First Affiliated Hospital of Medical College of Xi'an Jiaotong University

🇨🇳

Xi'an, China

Henan Cancer Hospital

🇨🇳

Zhengzhou, China

Vejle Sygehus

🇩🇰

Vejle, Denmark

Centre Jean Perrin Centre Regional de Lutte Contre Le Cancer D auvergne

🇫🇷

Clermont-ferrand, France

Centre Georges Francois Leclerc

🇫🇷

Dijon, France

Centre Oscar Lambret

🇫🇷

Lille, France

Hopital Dupuytren

🇫🇷

Limoges, France

Hopital Prive Jean Mermoz

🇫🇷

Lyon, France

Institut régional du Cancer Montpellier

🇫🇷

Montpellier, France

Institut Universitaire du Cancer de Toulouse-Oncopole

🇫🇷

Toulouse, France

Israel-Georgian Medical Research Clinic Healthycore

🇬🇪

Tbilisi, Georgia

Tbilisi Oncology Dispensary

🇬🇪

Tbilisi, Georgia

Ambulantes Tumorzentrum Spandau

🇩🇪

Berlin, Germany

Klinikum Essen-Mitte Ev. Huyssens-Stiftung / Knappschafts GmbH

🇩🇪

Essen, Germany

Nationales Centrum für Tumorerkrankungen (NCT)

🇩🇪

Heidelberg, Germany

Universitätsklinikum Mannheim

🇩🇪

Mannheim, Germany

Klinikum Mutterhaus der Borromaeerinnen gGmbH

🇩🇪

Trier, Germany

Universitätsfrauenklinik Ulm

🇩🇪

Ulm, Germany

Anticancer Hospital Ag. Savas

🇬🇷

Athens, Greece

Univ General Hosp Heraklion

🇬🇷

Heraklion, Greece

Euromedical General Clinic of Thessaloniki

🇬🇷

Thessaloniki, Greece

European Interbalkan Medical Center

🇬🇷

Thessaloniki, Greece

Queen Mary Hospital

🇭🇰

Hong Kong, Hong Kong

Tianjin Cancer Hospital

🇨🇳

Tianjin, China

Hubei Cancer Hospital

🇨🇳

Wuhan, China

Beverly Hills Cancer Center

🇺🇸

Beverly Hills, California, United States

Massachusetts General Hospital.

🇺🇸

Boston, Massachusetts, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

Sarah Cannon Research Institute / Tennessee Oncology

🇺🇸

Nashville, Tennessee, United States

Texas Oncology - Central South

🇺🇸

Austin, Texas, United States

Texas Tech University Health Sciences Center

🇺🇸

El Paso, Texas, United States

Texas Oncology - Northeast Texas

🇺🇸

Tyler, Texas, United States

Northwest Medical Specialties

🇺🇸

Tacoma, Washington, United States

Fundación CENIT para la Investigación en Neurociencias

🇦🇷

Buenos Aires, Argentina

Centro Oncologico Korben

🇦🇷

Ciudad Autonoma Buenos Aires, Argentina

Hosp Provincial D. Centenarios

🇦🇷

Rosario, Argentina

Macquarie University Hospital

🇦🇺

Macquarie Park, New South Wales, Australia

Southern Medical Day Care Centre

🇦🇺

Wollongong, New South Wales, Australia

Mater Adult Hospital

🇦🇺

South Brisbane, Queensland, Australia

Princess Alexandra Hospital

🇦🇺

Woolloongabba, Queensland, Australia

Western Health

🇦🇺

Fitzroy, Victoria, Australia

Peninsula and South Eastern Haematology and Oncology Group

🇦🇺

Frankston, Victoria, Australia

UZ Leuven Gasthuisberg

🇧🇪

Leuven, Belgium

Santa Casa de Misericordia de Porto Alegre

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

Clinica de Pesquisa e Centro de Estudos em Oncologia Ginecologica e Mamaria Ltda

🇧🇷

Sao Paulo, São Paulo, Brazil

Arthur J.E. Child Comprehensive Cancer Center-Calgary

🇨🇦

Calgary, Alberta, Canada

London Regional Cancer Program, London Health Sciences Centre, Baines Centre

🇨🇦

London, Ontario, Canada

Ottawa Hospital

🇨🇦

Ottawa, Ontario, Canada

Princess Margaret Cancer Center

🇨🇦

Toronto, Ontario, Canada

Jiangsu Province Hospital (the First Affiliated Hospital With Nanjing Medical University)

🇨🇳

Nanjing City, China

Fudan University Shanghai Cancer Center

🇨🇳

Shanghai City, China

Hebei Medical University Fourth Hospital

🇨🇳

Shijiazhuang, China

Prince of Wales Hospital

🇭🇰

Shatin, Hong Kong

Orszagos Onkologiai Intezet

🇭🇺

Budapest, Hungary

Uzsoki Utcai Korhaz

🇭🇺

Budapest, Hungary

Fondazione IRCCS Istituto Nazionale dei Tumori

🇮🇹

Milano, Lombardia, Italy

Ospedale Santa Maria Annunziata

🇮🇹

Bagno a Ripoli, Toscana, Italy

IOV - Istituto Oncologico Veneto - IRCCS

🇮🇹

Padova, Veneto, Italy

Pusan National University Hospital

🇰🇷

Busan, Korea, Republic of

Kyungpook National University Medical Center

🇰🇷

Daegu, Korea, Republic of

National Cancer Center

🇰🇷

Gyeonggi-do, Korea, Republic of

Seoul National University Bundang Hospital

🇰🇷

Gyeonggi-do, Korea, Republic of

Korea University Anam Hospital

🇰🇷

Seoul, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Severance Hospital, Yonsei University Health System

🇰🇷

Seoul, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Gangnam Severance Hospital

🇰🇷

Seoul, Korea, Republic of

Ewha Womans University Mokdong Hospital

🇰🇷

Seoul, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

National Cancer Institute IKN

🇲🇾

Putrajaya, Federal Territory OF Putrajaya, Malaysia

Hospital Sultan Ismail

🇲🇾

Johor Bahru, Malaysia

Sarawak General Hospital

🇲🇾

Sarawak, Malaysia

Palmerston North Hospital

🇳🇿

Palmerston North, New Zealand

Narodowy Instytut Onkologii Odzia? w Gliwicach

🇵🇱

Gliwice, Poland

Przychodnia Lekarska KOMED, Roman Karaszewski

🇵🇱

Konin, Poland

Moscow Clinical Scientific Center

🇷🇺

Moscow, Moskovskaja Oblast, Russian Federation

Blokhin Cancer Research Center

🇷🇺

Moscow, Moskovskaja Oblast, Russian Federation

LLC Medscan

🇷🇺

Moskva, Moskovskaja Oblast, Russian Federation

Clinical Hospital Lapino (LLC Haven)

🇷🇺

Yudino, Moskovskaja Oblast, Russian Federation

Medical Clinic "AB Medical group"

🇷🇺

Saint Petersburg, Sankt Petersburg, Russian Federation

Volgograd Regional Clinical Oncology Dispensary

🇷🇺

Volgograd, Russian Federation

Hospital Universitario de Canarias

🇪🇸

La Laguna, Tenerife, Spain

Hospital del Mar

🇪🇸

Barcelona, Spain

Vall d?Hebron Institute of Oncology (VHIO), Barcelona

🇪🇸

Barcelona, Spain

Insituto Catalán de Oncologia (ICO)

🇪🇸

Barcelona, Spain

Complejo Hospitalario de Jaen-Hospital Universitario Medico Quirurgico

🇪🇸

Jaen, Spain

Hospital General Universitario Gregorio Marañon

🇪🇸

Madrid, Spain

Clinica Universidad de Navarra-Madrid

🇪🇸

Madrid, Spain

Hospital Clinico San Carlos

🇪🇸

Madrid, Spain

Hospital Universitario 12 de Octubre

🇪🇸

Madrid, Spain

Hospital Universitario Puerta de Hierro

🇪🇸

Madrid, Spain

Hospital Universitario Virgen Macarena

🇪🇸

Sevilla, Spain

Instituto Valenciano Oncologia

🇪🇸

Valencia, Spain

Hospital Clinico Universitario de Valencia

🇪🇸

Valencia, Spain

Kaohsiung Medical Uni Chung-Ho Hospital

🇨🇳

Kaohsiung, Taiwan

Veterans General Hospital

🇨🇳

Taipei, Taiwan

National Taiwan Uni Hospital

🇨🇳

Taipei, Taiwan

Koo Foundation Sun Yat-Sen Cancer Center

🇨🇳

Taipei, Taiwan

Tri-Service General Hospital, Division of General Surgery

🇨🇳

Taipei, Taiwan

Ramathibodi Hospital

🇹🇭

Bangkok, Thailand

Maharaj Nakorn Chiang Mai Hospital

🇹🇭

Chiang Mai, Thailand

Chulabhorn Hospital

🇹🇭

Lak Si, Thailand

Songklanagarind Hospital

🇹🇭

Songkhla, Thailand

Adana Baskent University Hospital

🇹🇷

Adana, Turkey

Gulhane Training and Research Hospital

🇹🇷

Ankara, Turkey

Ege University Medical Faculty

🇹🇷

Bornova, ?zm?r, Turkey

Istanbul University Cerrahpasa Faculty of Medicine

🇹🇷

Istanbul, Turkey

SI Institute of general&urgent surgery n/a Zaytseva V.T NAMSU

🇺🇦

Kharkiv, Kharkiv Governorate, Ukraine

Municipal Institution SubCarpathian Clinical Oncological Centre

🇺🇦

Ivano-Frankivsk, KIEV Governorate, Ukraine

Uzhhorod Central City Clinical Hospital

🇺🇦

Uzhhorod, KIEV Governorate, Ukraine

City Clinical Hospital #4

🇺🇦

Dnipropetrovsk, Ukraine

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