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Investigation of the genetic basis of unexplained monogenic diseases

Recruiting
Conditions
Monogenic, rare diseases
Registration Number
DRKS00034194
Lead Sponsor
Institut für Humangenetik und Genommedizin der Uniklinik RWTH Aachen
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
All
Target Recruitment
3000
Inclusion Criteria

Suspicion of monogenic disease, consent available

Exclusion Criteria

Lack of consent

Study & Design

Study Type
observational
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
The aim of this study is to identify causative mutations in coding and non-coding regions of the genome in affected individuals with a congenital, either defined or unclear disease pattern, the cause of which has remained unclear even after comprehensive interdisciplinary clinical and conventional molecular genetic diagnostics. <br>Furthermore, we would like to achieve a better characterization of patient groups or disease groups through molecular genetic analyses, for which the clinical spectrum can then be evaluated and, if necessary, clinical diagnostic criteria can be developed
Secondary Outcome Measures
NameTimeMethod
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