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Co-administration of Acetaminophen with Ibuprofen to Improve Duct-Related Outcomes in Extremely Premature Infants

Phase 2
Recruiting
Conditions
Patent Ductus Arteriosus After Premature Birth
Interventions
Registration Number
NCT05340582
Lead Sponsor
Mount Sinai Hospital, Canada
Brief Summary

Patent ductus arteriosus (PDA), the most common cardiovascular complication of prematurity, is associated with higher mortality and morbidities in extremely low gestational age neonates (ELGANs, \< 27+0 weeks). Ibuprofen and acetaminophen, which act by reducing prostaglandin synthesis, are the most commonly used first and second line agents for PDA treatment across Canada. However, initial treatment failure with monotherapy is a major problem, occurring in \>60% ELGANs. Treatment failure is associated with worsening rates of mortality and bronchopulmonary dysplasia (BPD), while early treatment success can achieve rates comparable to neonates without PDA. Treatment failure resulting in prolonged disease exposure is thought to be a major contributor. Recently, combination therapy with acetaminophen and ibuprofen has emerged as a new treatment regime. Acetaminophen exerts anti-prostaglandin effect through a different receptor site than ibuprofen, providing a biological rationale for their synergistic action.

The objective of this study is to evaluate the clinical impact, efficacy and safety of combination regime (Ibuprofen + IV Acetaminophen) for the first treatment course for PDA in ELGANs vs. Ibuprofen alone (current standard treatment).

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
310
Inclusion Criteria
  • Preterm infants born <27+0 weeks gestational age
  • Permission given by the attending clinician to approach and then consent obtained from parents
  • Diagnosis of PDA ≥ 1.5 mm on echocardiography with unrestrictive predominantly left to right shunt
  • Designated to receive first treatment course with intravenous or enteral ibuprofen, as decided by the attending team.
Exclusion Criteria
  • Chromosomal anomaly
  • Pre-treatment renal dysfunction defined as urine output < 1ml/kg/hour for the previous 24 hours or serum creatinine > 100 micromol/L
  • Pre-treatment hepatic dysfunction defined as serum aminotransferase (ALT) > 100 units/L94
  • Platelet count <50,000 per microliter
  • Permission denied by the attending clinician to approach parents
  • Parental consent not available
  • Previous exposure to PDA medical treatment with any drug (prophylactic indomethacin use for prevention of intraventricular hemorrhage will not be considered as PDA treatment).

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Combination TherapyAcetaminophen InjectionIntravenous or enteral ibuprofen, as decided by clinical team, in the standard clinical dose used in participating NICUs (typically, for neonates \< 7 days old - 10 mg/kg/dose on day 1, 5 mg/kg/dose q24h on days 2 and 3; for neonates \> 7 days old - 20 mg/kg/dose on day 1, 10 mg/kg/dose q24h on days 2 and 3) And study drug (intravenous acetaminophen 15 mg/kg/dose IV q6h for 3 days).
Combination TherapyIbuprofen 20 mg/mL oral suspension or Ibuprofen lysine 10 mg/mL injection solution (Neoprofen)Intravenous or enteral ibuprofen, as decided by clinical team, in the standard clinical dose used in participating NICUs (typically, for neonates \< 7 days old - 10 mg/kg/dose on day 1, 5 mg/kg/dose q24h on days 2 and 3; for neonates \> 7 days old - 20 mg/kg/dose on day 1, 10 mg/kg/dose q24h on days 2 and 3) And study drug (intravenous acetaminophen 15 mg/kg/dose IV q6h for 3 days).
Standard Clinical Practice - MonotherapySodium chloride 0.9% injectionIntravenous or enteral ibuprofen, as decided by clinical team, in the standard clinical dose used in participating NICUs (typically, for neonates \< 7 days old - 10 mg/kg/dose on day 1, 5 mg/kg/dose q24h on days 2 and 3; for neonates \> 7 days old - 20 mg/kg/dose on day 1, 10 mg/kg/dose q24h on days 2 and 3) And Placebo \[(0.9% saline IV q6h for 3 days).
Standard Clinical Practice - MonotherapyIbuprofen 20 mg/mL oral suspension or Ibuprofen lysine 10 mg/mL injection solution (Neoprofen)Intravenous or enteral ibuprofen, as decided by clinical team, in the standard clinical dose used in participating NICUs (typically, for neonates \< 7 days old - 10 mg/kg/dose on day 1, 5 mg/kg/dose q24h on days 2 and 3; for neonates \> 7 days old - 20 mg/kg/dose on day 1, 10 mg/kg/dose q24h on days 2 and 3) And Placebo \[(0.9% saline IV q6h for 3 days).
Primary Outcome Measures
NameTimeMethod
Composite of pre-discharge mortality or any grade BPD36 weeks PMA

Need for oxygen or positive pressure respiratory support at 36 weeks postmenstrual age (PMA)

Secondary Outcome Measures
NameTimeMethod
Need for systemic steroidsFrom date of randomization until death, discharge home or discharge to a community hospital (whichever comes first) assessed up to a maximum of 250 days after randomization

Use for BPD treatment

Duration (days) of invasive or non-invasive respiratory supportFrom date of randomization until death, discharge home or discharge to a community hospital (whichever comes first) assessed up to a maximum of 250 days after randomization

Days of invasive or non invasive support during NICU say

PDA treatment success6-10 days post treatment initiation

Defined as PDA closure or becoming insignificant \[diameter \<1.5 mm\]

Severity of BPD at 36 weeks PDM using Jensen's criteriaAt 36 weeks PDM

Grade 1, nasal cannula ≤2 L/min; grade 2, nasal cannula \>2 L/min or noninvasive positive airway pressure; grade 3, invasive mechanical ventilation

Procedure for PDA closureFrom date of randomization until death, discharge home or discharge to a community hospital (whichever comes first) assessed up to a maximum of 250 days after randomization

Surgical closure for PDA

Further exposure to pharmacological PDA treatmentsFrom date of randomization until death, discharge home or discharge to a community hospital (whichever comes first) assessed up to a maximum of 250 days after randomization

As per units' standard practice (not part of study procedures)

NEC ≥ stage 2AFrom date of randomization until death, discharge home or discharge to a community hospital (whichever comes first) assessed up to a maximum of 250 days after randomization

NEC ≥ stage 2A during NICU stay

SepsisFrom date of randomization until death, discharge home or discharge to a community hospital (whichever comes first) assessed up to a maximum of 250 days after randomization

Diagnosis of sepsis during NICU stay

Renal or hepatic dysfunctionOccurring within 7 days of treatment initiation

Renal dysfunction defined as urine output \< 1ml/kg/hour for the previous 24 hours or serum creatinine \> 100 micromol/L; hepatic dysfunction defined as serum aminotransferase (ALT) \> 100 units/L

MortalityFrom date of randomization until date of death (assessed up to a maximum of 250 days after randomization)

Death during initial tertiary NICU stay

Need for diuretic useFrom date of randomization until death, discharge home or discharge to a community hospital (whichever comes first) assessed up to a maximum of 250 days after randomization

Diuretic use for BPD treatment

Trial Locations

Locations (9)

John Hunter Hospital

🇦🇺

Newcastle, New South Wales, Australia

Royal North Shore Hospital

🇦🇺

St Leonards, New South Wales, Australia

Royal Alexandra Hospital

🇨🇦

Edmonton, Ontario, Canada

McMaster Children's Hospital

🇨🇦

Hamilton, Ontario, Canada

Sunnybrook Health Sciences Centre

🇨🇦

Toronto, Ontario, Canada

Mount Sinai Hospital

🇨🇦

Toronto, Ontario, Canada

Centre Hospitalier de l'Université Laval

🇨🇦

Quebec, Canada

Prince of Wales Hospital

🇭🇰

Shatin, NT, Hong Kong

The Rotunda Hospital

🇮🇪

Dublin, Ireland

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