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Inhaled Nitric Oxide (INO) for the Prevention of Bronchopulmonary Dysplasia (BPD) in Preterm Infants

Phase 3
Completed
Conditions
Bronchopulmonary Dysplasia
Interventions
Drug: Placebo
Drug: Inhaled Nitric Oxide
Registration Number
NCT00931632
Lead Sponsor
Mallinckrodt
Brief Summary

This phase 3, multi-center, double blind, placebo-controlled, randomized clinical trial will attempt to demonstrate if preterm infants who require mechanical ventilation and/or positive pressure support at any point during days 5 to 14 after birth may benefit from treatment with iNO.

Detailed Description

Multi-center, double blind, placebo-controlled, randomized clinical trial. Infants who meet all enrollment criteria at any point during days 5 to 14 after birth will be randomized to inhaled NO starting at 20 ppm, or matching placebo, by means of a blinded INOvent® delivery device. All infants will receive 24 days of therapy, following a dose reduction schedule. Infants who are extubated before 24 days will continue therapy via nasal continuous positive airway pressure (CPAP) or nasal cannula to complete 24 days' of therapy. The primary outcome measure will be survival without BPD at 36 weeks gestational age using a physiologic assessment of BPD.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
451
Inclusion Criteria
  • Preterm infants who are:

    1. 500 to 1250 grams at birth
    2. < 30 weeks gestational age
    3. 5 to 14 days of age (inclusive) at the time of entry
    4. Requiring mechanical ventilation or for those infants ≤ 800 grams, positive pressure support (including CPAP) for respiratory insufficiency on days 5 to 14 days of age (inclusive)
Exclusion Criteria
  1. Preterm infants with life-threatening anomalies (cranial, cardiac, thoracic, chromosomal) or congenital diaphragmatic hernia with lung hypoplasia, or any subject who will not receive complete intensive care
  2. Preterm infants with bilateral Grade 4 intraventricular hemorrhage (IVH)
  3. Subjects who are dependent on right to left shunting to maintain the systemic circulation
  4. Preterm infants who received prior iNO therapy
  5. Use of another investigational agent

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
PlaceboPlaceboNitrogen Placebo
Inhaled Nitric OxideInhaled Nitric OxideInhaled Nitric Oxide
Primary Outcome Measures
NameTimeMethod
Survival Without BPD at 36 WeeksBaseline, 36 weeks PMA
Secondary Outcome Measures
NameTimeMethod
Number and Percentage of Participants With Use of Postnatal Corticosteroids for Bronchopulmonary DysplasiaThrough hospital discharge, an average of 105 days for placebo and 108 days for INO
Number and Percentage of Participants With Use of Postnatal Corticosteroids for Any Medical ReasonThrough hospital discharge, an average of 105 days for placebo and 108 days for INO
Systemic Use of Postnatal Corticosteroids for Any Medical ReasonThrough hospital discharge, an average of 105 days for placebo and 108 days for INO
Days of Airway Pressure Support - Intent-to-treat PopulationThrough hospital discharge, an average of 105 days for placebo and 108 days for INO

Airway pressure support includes conventional mechanical ventilation, conventional, high frequency oscillatory ventilation, jet, continuous positive airway pressure, and other.

Length of Birth HospitalizationThrough hospital discharge, an average of 105 days for placebo and 108 days for INO
Number of Days of Oxygen UseThrough hospital discharge, an average of 105 days for placebo and 108 days for INO
Severity of Bronchopulmonary Dysplasia36 weeks

Severity of bronchopulmonary dysplasia defined by the fraction of inspired O2 concentration (FiO2) requirement.

Trial Locations

Locations (33)

Saint Francis Children's Hospital

🇺🇸

Tulsa, Oklahoma, United States

Sharp Mary Birch Hospital for Women and Newborns

🇺🇸

San Diego, California, United States

Winnie Palmer Hospital for Women and Babies

🇺🇸

Orlando, Florida, United States

Loma Linda University School of Medicine

🇺🇸

Loma Linda, California, United States

Medical College of Georgia

🇺🇸

Augusta, Georgia, United States

Jersey Shore University Medical Center

🇺🇸

Neptune City, New Jersey, United States

Maria Fareri Children's Hospital at Westchester Medical Center

🇺🇸

Valhalla, New York, United States

Riley Hospital for Children

🇺🇸

Indianapolis, Indiana, United States

Advocate Lutheran General Children's Hospital

🇺🇸

Park Ridge, Illinois, United States

University of Louisville School of Medicine

🇺🇸

Louisville, Kentucky, United States

Hennepin County Medical Center

🇺🇸

Minneapolis, Minnesota, United States

Connecticut Children's Medical Center

🇺🇸

Hartford, Connecticut, United States

Mercy Children's Hospital

🇺🇸

Toledo, Ohio, United States

Wheaton Franciscan Healthcare

🇺🇸

Milwaukee, Wisconsin, United States

Cook Children's Medical Center

🇺🇸

Fort Worth, Texas, United States

Saint Barnabas Medical Center

🇺🇸

Livingston, New Jersey, United States

Stanford University School of Medicine

🇺🇸

Palo Alto, California, United States

Children's Hospital of Orange County

🇺🇸

Orange, California, United States

Rady Children's Hospital of San Diego

🇺🇸

San Diego, California, United States

Winthrop University Hospital

🇺🇸

Mineola, New York, United States

Robert Wood Johnson University Hospital

🇺🇸

New Brunswick, New Jersey, United States

WakeMed Faculty Physicians, Neonatology

🇺🇸

Raleigh, North Carolina, United States

St. Joseph's Hospital and Medical Center

🇺🇸

Phoenix, Arizona, United States

Children's Corporate Center, Division of Neonatology

🇺🇸

Wauwatosa, Wisconsin, United States

Greenville Memorial Hospital

🇺🇸

Greenville, South Carolina, United States

University of So Florida College of Medicine

🇺🇸

Tampa, Florida, United States

Sanford Children's Hospital

🇺🇸

Sioux Falls, South Dakota, United States

Primary Children's Medical Center

🇺🇸

Salt Lake City, Utah, United States

Centre Hospitalier Universitaire de Quebec

🇨🇦

Quebec, Canada

Phoenix Children's Hospital

🇺🇸

Phoenix, Arizona, United States

Virginia Commonwealth University

🇺🇸

Richmond, Virginia, United States

University of Calgary

🇨🇦

Calgary, Alberta, Canada

Montefiore Medical Center

🇺🇸

The Bronx, New York, United States

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