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Drug-Drug Interaction Study of VX-809 and VX-770 in Healthy Subjects

Phase 1
Completed
Conditions
Cystic Fibrosis
Interventions
Drug: VX-809 & VX-770
Drug: Placebo
Registration Number
NCT00966602
Lead Sponsor
Vertex Pharmaceuticals Incorporated
Brief Summary

The purpose of this study is to assess the pharmacokinetics and safety of co-administration of VX-770 and VX-809 in healthy adults.

Detailed Description

Cystic fibrosis (CF) is an inherited disease resulting from defects to a gene known as the cystic fibrosis transmembrane conductance regulator (CFTR). CF affects approximately 70,000 children and adults worldwide (30,000 in the United States) and is the most common fatal genetic disease in persons of European descent. Despite progress in the treatment of CF with antibiotics and mucolytics, the predicted median age of survival for a person with CF is in the mid-30s. Though the disease affects multiple organs, most morbidity and mortality is caused by progressive loss of lung function.

This is a Phase 1, randomized, double-blind, placebo-controlled, multiple-dose study of orally administered VX-809 and VX-770 in healthy subjects. The study will evaluate safety and tolerability of co-administration of VX-809 and VX-770 in healthy volunteers.

Enrollment is planned for 24 subjects at 1 clinical site. Subjects will be randomized to receive study drug or placebo during three 14-day treatment periods separated by 14-day washout periods. In Treatment Period 1, subjects randomized to study drug will receive VX-809 every 24 hours. In Treatment Period 2, subjects randomized to study drug will receive VX-770 every 12 hours. In Treatment Period 3, subjects randomized to study drug will receive VX-809 every 24 hours and VX-770 every 12 hours. Subjects randomized to placebo will receive placebo during all treatment periods.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
24
Inclusion Criteria
  • Male or female subject between 18 and 55 years of age, inclusive
  • Body mass index (BMI) between 18.5 and 30.0 kg/m2, inclusive
  • Subjects of child-bearing potential and who are sexually active must meet contraception requirements
  • Female subject must have a negative serum pregnancy test at screening, Day -1, and throughout the study
Exclusion Criteria
  • History of any illness that, in the opinion of the investigator might confound the results of the study or pose an additional risk in administering study drug to the subject. This may include but is not limited to a significant history of cardiovascular, central nervous system, hepatobiliary or renal disease, or a history of mental illness
  • Participated in a clinical study involving administration of either an investigational or a marketed drug within 60 days or 7 terminal half-lives (whichever is longer) before the Screening visit
  • Subject who has received VX-770 or VX-809 in a previous clinical study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Treatment Period 2VX-770-
Treatment Period 2Placebo-
Treatment Period 1VX-809-
Treatment Period 1Placebo-
Treatment Period 3VX-809 & VX-770-
Treatment Period 3Placebo-
Primary Outcome Measures
NameTimeMethod
Pharmacokinetic (PK) parameters of VX-770 and its metabolites in plasma in the presence and absence of VX-80970 days
PK parameters of VX-809 in plasma in the presence and absence of VX-77070 days
Secondary Outcome Measures
NameTimeMethod
Safety as measured by adverse events, physical examination, and clinically significant changes in laboratory values (hematology, chemistry, coagulation, and urinalysis), electrocardiograms (ECGs), and vital signs.70 days
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