Prognostic Factors , Morbidity and Mortality in Patients With Neuromuscular Disorders Admitted in ICU
- Conditions
- Muscular DystrophiesIntensive Care (ICU) Myopathy
- Registration Number
- NCT02685215
- Lead Sponsor
- Centre d'Investigation Clinique et Technologique 805
- Brief Summary
Muscular dystrophies are neuromuscular disorders with disability. Restrictive pulmonary failure and cardiomyopathy affect prognosis.The investigators aim to establish predictive factors for mortality and morbidity in Intensive care unit (ICU ) and to describe the long term follow up after ICU discharge.
- Detailed Description
Muscular dystrophies are neuromuscular disorders with disability. Restrictive pulmonary failure and cardiomyopathy affect prognosis. Little is known about morbidity and mortality of patients with muscular dystrophies admitted in intensive care unit (ICU).The investigators aim to describe the spectrum of patients with muscular dystrophies admitted in ICU , to establish predictive factors for ICU mortality and morbidity and to describe the long term follow up after ICU discharge.
Recruitment & Eligibility
- Status
- UNKNOWN
- Sex
- All
- Target Recruitment
- 800
- admitted in ICU
- Duchenne muscular dystrophy
- Becker muscular dystrophy
- LGMD
- Steinert disease
- Pompe disease
- FSHD
- metabolic disease
- mitochondrial disease
- congenital myopathy
- others neuro-muscular diseases
- brain injury
- minor patient
Study & Design
- Study Type
- OBSERVATIONAL
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method ICU mortality 1 month
- Secondary Outcome Measures
Name Time Method tracheostomy in ICU 1 month decline of vital capacity after ICU stay 2 years long term survival after ICU stay 5 years predictive factors for re admission in ICU 1 year
Trial Locations
- Locations (1)
Hopital Raymond Poincare
🇫🇷Garches, France