MedPath

Praluent® (Alirocumab) Pregnancy Exposure Registry: An OTIS Pregnancy Surveillance Study

Terminated
Conditions
Hypercholesterolemia
Interventions
Registration Number
NCT03379558
Lead Sponsor
Regeneron Pharmaceuticals
Brief Summary

Primary Objective:

To estimate the overall combined rate of major structural birth defects in infants of mothers with atherosclerotic cardiovascular disease (ASCVD) and/or familial hypercholesterolemia (FH) exposed to Praluent® (alirocumab) during pregnancy when used to treat hypercholesterolemia and to compare that rate to unexposed disease-matched and unexposed non-diseased comparison pregnancies.

Secondary Objectives:

* Secondary objectives are to estimate the rates of the outcomes in pregnancies/infants of mothers with atherosclerotic cardiovascular disease and/or familial hypercholesterolemia exposed to alirocumab during pregnancy when used to treat hypercholesterolemia and to compare that rate to unexposed disease-matched and non-diseased comparison pregnancies, and secondarily to compare the rates of these outcomes in the unexposed disease-matched pregnancies to the rates in the unexposed non-diseased comparison pregnancies.

* Safety and tolerability of alirocumab.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
Female
Target Recruitment
37
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Cohort 1 : alirocumab exposedALIROCUMAB SAR236553 (REGN727)Pregnant women diagnosed with primary hypercholesterolemia and atherosclerotic cardiovascular disease, or primary hypercholesterolemia associated with familial hypercholesterolemia and exposed to alirocumab during the current pregnancy.
Primary Outcome Measures
NameTimeMethod
Rate of major structural birth defectsUp to 1 year of age of the infant

Overall combined rate of major structural birth defects in infants born to females with atherosclerotic cardiovascular disease (ASCVD) and/or familial hypercholesterolemia (FH) exposed to Praluent (alirocumab)

Secondary Outcome Measures
NameTimeMethod
Infant outcome: serious infections or hospitalizations, adverse reactions to childhood vaccinationsUp to 5 years of age of the child

Proportion of infants who experienced serious infections or hospitalizations, and adverse reactions to childhood vaccinations

Infant outcome: adequacy of immune responseUp to 5 years of age of the child

Proportion of infants who has adequate immune response as measured by IgG-Tetanus antibody

Adverse eventsUp to 5 years follow-up period

Proportion of patients who experienced adverse events (AEs), AEs of special interest, and serious AEs

Infant outcome: adverse neurodevelopmentUp to 5 years of age of the child

Proportion of infants who experienced adverse neurodevelopment

Breastfeeding/Lactation outcomeUp to 2 years of age of the child

Proportion of patients breastfeeding exclusively for more than 2 weeks

Pregnancy outcome: Spontaneous abortionDate of conception to 20 weeks gestation

Rate of spontaneous abortion

Pregnancy outcome: Elective abortionDate of conception to 20 weeks gestation

Rate of elective abortion

Pregnancy outcome: Still birthAt birth

Rate of still birth

Pregnancy outcome: Preterm deliveryLive birth prior to 37 weeks gestation

Rate of preterm delivery

Infant outcome: Pattern of minor structural birth defectsUp to 1 year of age of the infant

Specific pattern of 3 or more minor structural defects in live born infants receiving the exam

Infant outcome: Small for gestational ageAt birth

Proportion of infants who are small for gestational age on weight, length, or head circumference

Infant outcome: Postnatal growth deficiencyUp to 1 year of age of the infant

Proportion of infants less than or equal to the 10th percentile for sex and age on weight, length, or head circumference at 1 year postnatal evaluation

Trial Locations

Locations (1)

Investigational site UNITED STATES

🇺🇸

San Diego, California, United States

© Copyright 2025. All Rights Reserved by MedPath