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Erythropoietin in Infants With Hypoxic Ischemic Encephalopathy (HIE)

Phase 1
Completed
Conditions
Hypoxic Ischemic Encephalopathy
Interventions
Procedure: EEG and Brain MRI
Biological: Nitric oxide measurement in the blood
Registration Number
NCT00945789
Lead Sponsor
Tanta University
Brief Summary

In this prospective trial the investigators plan to study the efficacy of erythropoietin as a therapeutic agent in neonates who suffer from brain injury following perinatal asphyxia.

Detailed Description

During HIE free radicals are generated within mitochondria and also as byproducts in the synthesis of prostaglandins.These free radicals ignite a secondary phase of subsequent damage to the brain by attacking membranal fatty acids. Nitric oxide (NO) is involved in the cascade of metabolic events that contributes to HIE. It mediates, in part, the cytotoxic activity of macrophages, induces relaxation of blood vessels, and also acts as a neurotransmitter in the central and peripheral nervous system. Therefore, the therapeutic value of NO synthase inhibitors, among many other agents used to ameliorate the course of HIE, is currently under investigation in experimental animals.

Erythropoietin (EPO) is a cytokine originally identified for its role in erythropoiesis and more recently shown to be produced in the central nervous system.Relative insufficiency of endogenous EPO during periods of ischemic stress may trigger neuronal apoptosis, whereas the provision of exogenous EPO has been shown to inhibit this process. The potential immediate protective effects of EPO include decreased NO production, activation of antioxidant enzymes, reduction of glutamate toxicity, inhibition of lipid peroxidation, and reduction of inflammation. Long-term protective effects of EPO include the generation of neuronal anti-apoptotic mechanisms, stimulation of angiogenesis, and modulation of neurogenesis.

Preliminary data supports a protective role of exogenous EPO to neuronal cells. The presence of EPO rescues in vitro cultured neurons from NO-induced death. It specifically protects cultured neurons from N-methyl-D-aspartate (NMDA) receptor-mediated glutamate toxicity. Intercerebroventricular injection of EPO offered significant protection of neuronal tissue in animals with focal cerebral ischemia. EPO is able to cross the blood brain barrier, and its concentration in the cerebrospinal fluid in normal rats significantly increases within 30 minutes following intravenous administration. EPO also offered neuronal protection when it was administered systemically to animals suffering from global and focal cerebral ischemia. In adult patients with stroke, the administration of EPO ameliorates the course of the disease. Therefore, EPO has recently received much attention and is speculated to have a role in the protection of HIE infants. However, despite the biological plausibility and the encouraging preliminary data from animals and adult humans, surprisingly EPO has never been tried in newborns with HIE even though it has already been used in neonates for other indications and is known to be safe.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
45
Inclusion Criteria
  • Inborn infants at term gestation (38-42 weeks)
  • Apgar score ≤ 3 at 5 minutes and/or delayed first breath beyond five minutes after birth
  • Profound metabolic or mixed acidosis with serum bicarbonate <12 mMol/L in initial arterial blood gas
  • Evidence of encephalopathy such as stupor, coma, seizures, or hypotonia in the immediate neonatal period
Exclusion Criteria
  • Twin gestation
  • Maternal diabetes
  • Congenital malformations of the central nervous system
  • Chromosomal abnormalities
  • Chorioamnionitis and congenital infections
  • Intrauterine growth restriction

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
EPO HIE GroupHuman recombinant erythropoietinInfants with hypoxic ischemic encephalopathy receive human recombinant erythropoietin
EPO HIE GroupEEG and Brain MRIInfants with hypoxic ischemic encephalopathy receive human recombinant erythropoietin
EPO HIE GroupNitric oxide measurement in the bloodInfants with hypoxic ischemic encephalopathy receive human recombinant erythropoietin
Control HIEEEG and Brain MRIInfants with hypoxic ischemic encephalopathy who do not receive treatment drug (EPO)
Control HIENitric oxide measurement in the bloodInfants with hypoxic ischemic encephalopathy who do not receive treatment drug (EPO)
Healthy ControlsNitric oxide measurement in the bloodHealthy newborn without hypoxic ischemic encephalopathy
Primary Outcome Measures
NameTimeMethod
Neurodevelopmental outcomes6 months
EEG changes2-3 weeks
MRI of the brain3 weeks
Secondary Outcome Measures
NameTimeMethod
Nitric oxide concentrations in the plasma2 weeks

Trial Locations

Locations (1)

Tanta University Faculty of Medicine

🇪🇬

Tanta, Egypt

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