MedPath

Pitolisant in Refractory Restless Legs Syndrome

Phase 4
Recruiting
Conditions
Restless Legs Syndrome
Interventions
Registration Number
NCT05581576
Lead Sponsor
William Ondo, MD
Brief Summary

This is an open-label trial in Restless Legs Syndrome (RLS) patients inadequately treated with standard therapy, defined by an IRLS score greater than 15. Investigators hypothesize that the study drug, Pitolisant (Wakix), may improve RLS symptoms.

Detailed Description

This is an open-label trial in RLS patients who have been inadequately treated with standard therapies, defined by an IRLS \> 15. This trial consists of four study center visits (weeks 0, 4, 8, and 16) and four telephone visits (weeks 1, 3, 11, and a post safety phone call at week 17).

Subjects will titrate pitolisant for three weeks, starting with a dose of 8.9 mg at week 1, then increase to 17.8 mg at week 2, and a final increase to maximum dosage of 35.6 mg at week 3. If subjects are unable to tolerate the highest dose, they may reduce their dose to 17.8 mg. Titration of the drug will be monitored via telephone visits. During weeks 0-8, subjects will continue to take their current RLS medications. From week 8-16, subjects may either reduce or stop their other RLS medications as mutually agreed upon with investigator.

Several questionnaire assessments will be conducted throughout the study to monitor the subjects. Subjects will complete the International RLS Rating Scale (IRLS), Restless Legs Syndrome - 6 Scale (RLS-6), RLS Quality of Life Questionnaire (RLSQoL), Fatigue Severity Scale (FSS), Hamilton Depression Scale (HDS), Montreal Cognitive Assessment (MoCA), Epworth Sleepiness Scale (ESS), Clinical Global Impressions (CGI), and Clinical Global Impressions-Change (CGI-C).

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
18
Inclusion Criteria
  • RLS diagnosed by standard criteria with an IRLS > 15 while taking at least 1 RLS medication
  • Stable RLS medications for at least 2 weeks prior to study entry
Exclusion Criteria
  • MoCA < 24
  • Concurrent untreated sleep disorders, not felt to be stable
  • Subjects with any significant, unstable cardiovascular, liver, lung, renal, psychiatric, or neurological diseases (not including RLS)
  • Intravenous iron within 4 weeks of study entry
  • Breast feeding or pregnancy determined by urine pregnancy test in subjects where pregnancy is possible (pre-menopausal, sexually active women)
  • Subjects with previous allergic reaction or lack of tolerability to Pitolisant

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Pitolisant (Wakix)PitolisantPitolisant will be titrated weekly until maximum dosage of 35.6 mg. Titration is dependent on subjects response.
Primary Outcome Measures
NameTimeMethod
International RLS Rating Scale (IRLS)At week 8

This is a subjective scale to measure the severity of RLS within the past week.

Secondary Outcome Measures
NameTimeMethod
The Restless Legs Syndrome - 6 Scale (RLS-6)Baseline, 4 weeks, 8 weeks, and 16 weeks

This scale measures the severity of daytime versus nighttime RLS symptoms.

Fatigue Severity Scale (FSS)Baseline, 4 weeks, 8 weeks, and 16 weeks

This scale evaluates the impact of fatigue patients are experiencing.

Hamilton Depression Scale (HDS)Baseline, 4 weeks, 8 weeks, and 16 weeks

This scale assess symptoms of depression.

Restless Legs Syndrome Quality of Life Questionnaire (RLSQoL)Baseline, 4 weeks, 8 weeks, and 16 weeks

This scale assess the quality of life in RLS patients.

Montreal Cognitive Assessment (MoCA)Baseline, 4 weeks, 8 weeks, and 16 weeks

This assessment detects mild cognitive impairment.

Epworth Sleepiness Scale (ESS)Baseline, 4 weeks, 8 weeks, and 16 weeks

This is a subjective scale that measures a patient's sleepiness.

Clinical Global Impressions - Change1 week, 2 weeks, 4 weeks, 8 weeks, 11 weeks, 16 weeks, and 17 weeks

This scale assess how much a patients illness has improved or worsened when compared to a baseline state from the beginning of the intervention.

Trial Locations

Locations (1)

Houston Methodist Hospital

🇺🇸

Houston, Texas, United States

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