临床试验/NCT02399748

NCT02399748招募中不适用

A Long-term Study for the Outcome of Pompe Disease

National Taiwan University Hospital1 个研究点分布在 1 个国家目标入组 50 人开始时间: 2007年4月最近更新: 2017年7月18日

适应症

试验速览

阶段: 不适用
状态: 招募中
发起方: National Taiwan University Hospital
入组人数: 50
试验地点: 1
主要终点: all cause morbidities

研究概览研究设计入排标准结局指标研究者研究点记录与标识符相似试验

研究概览

简要总结

Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.

研究设计

研究类型: Observational
观察模型: Case Only
时间视角: Prospective

入排标准

性别: All
接受健康志愿者: 否

入选标准

•Confirm diagnosis with Pompe disease, is or is preparing receiving enzyme replacement therapy

排除标准

未提供

结局指标

主要结局

all cause morbidities

时间窗: 10 years

次要结局

未报告次要终点

研究者

发起方

National Taiwan University Hospital

申办方类型

Other

责任方

Sponsor

研究点 (1)

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A Long-term Study for the Outcome of Pompe Disease | 临床试验