NCT00713453Unknown不适用
Muscle Response to Enzyme Replacement Therapy in Pompe Disease
适应症
试验速览
- 阶段
- 不适用
- 入组人数
- 16
- 试验地点
- 1
- 主要终点
- all morphology changes improvement
研究概览
简要总结
This study is to study the response of muscle cells from Pompe disease after enzyme replacement therapy
研究设计
- 研究类型
- Observational
- 观察模型
- Case Only
入排标准
- 性别
- All
- 接受健康志愿者
- 是
入选标准
- •patients with Pompe disease, prepare or on enzyme replacement therapy
- •signed informed consent
排除标准
- 未提供
结局指标
主要结局
all morphology changes improvement
时间窗: 6 months
次要结局
未报告次要终点
研究者
National Taiwan University Hospital
Yin-Hsiu Chien, M.D., PhD.
National Taiwan University Hospital
研究点 (1)
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