Muscle Response to Enzyme Replacement Therapy in Pompe Disease
- Conditions
- Pompe Disease
- Registration Number
- NCT00713453
- Lead Sponsor
- National Taiwan University Hospital
- Brief Summary
This study is to study the response of muscle cells from Pompe disease after enzyme replacement therapy
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- UNKNOWN
- Sex
- All
- Target Recruitment
- 16
Inclusion Criteria
- patients with Pompe disease, prepare or on enzyme replacement therapy
- signed informed consent
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Exclusion Criteria
Read More
Study & Design
- Study Type
- OBSERVATIONAL
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method all morphology changes improvement 6 months
- Secondary Outcome Measures
Name Time Method
Trial Locations
- Locations (1)
National Taiwan University Hospital
🇨🇳Taipei, Taiwan