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Muscle Response to Enzyme Replacement Therapy in Pompe Disease

Conditions
Pompe Disease
Registration Number
NCT00713453
Lead Sponsor
National Taiwan University Hospital
Brief Summary

This study is to study the response of muscle cells from Pompe disease after enzyme replacement therapy

Detailed Description

Not available

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
16
Inclusion Criteria
  • patients with Pompe disease, prepare or on enzyme replacement therapy
  • signed informed consent
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Exclusion Criteria
Read More

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
all morphology changes improvement6 months
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

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