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Clinical Transplant-Related Long-term Outcomes of Alternative Donor Allogeneic Transplantation (BMT CTN 1702)

Not Applicable
Completed
Conditions
Myelodysplastic Syndromes
Hodgkin Lymphoma
Acute Lymphoblastic Leukemia
Sickle Cell Disease
Acute Myeloid Leukemia
Non-hodgkin Lymphoma
Acquired Aplastic Anemia
Interventions
Other: Donor Search Prognosis Score
Registration Number
NCT03904134
Lead Sponsor
Center for International Blood and Marrow Transplant Research
Brief Summary

The purpose of this study is to determine if a search strategy of searching for an HLA-matched unrelated donor for allogeneic transplantation if possible then an alternative donor if an HLA-matched unrelated donor is not available versus proceeding directly to an alternative donor transplant will result in better survival for allogeneic transplant recipients within 2 years after study enrollment.

Detailed Description

This is a multicenter, interventional and observational study to understand factors affecting the likelihood of transplantation in patients without a human leukocyte antigen (HLA) matched family donor and to compare outcomes associated with pursuing an HLA-identical unrelated versus other alternative donor graft sources. Alternative donors are defined as any donor other than an HLA-matched or 1 antigen-mismatched related donor. Patients with acute myeloid leukemia (AML), acute lymphoblastic leukemia (ALL), myelodysplastic syndromes (MDS), Non-Hodgkin lymphoma (NHL), Hodgkin lymphoma (HL), acquired aplastic anemia (AA) or sickle cell disease (SCD) are eligible. The primary comparison for the interventional study will be between two arms based on biologic assignment, analyzed on an intention-to-treat basis: Arm 1: Patients who are Very Likely to find a matched unrelated donor (MUD), defined as having a \>90% chance of finding an 8/8 HLA-matched unrelated donor, for whom a fully matched unrelated donor will be pursued; and Arm 2: Patients who are Very Unlikely to find a MUD, defined as having a \<10% chance of finding an 8/8 HLA-matched unrelated donor, for whom a haploidentical, cord blood, or mismatched unrelated donor transplant will be pursued. Patients with a Less Likely chance of finding a MUD, i.e., those not falling into the other two groups (a 26% chance), will be enrolled onto the observational component of the study and analyzed for all relevant endpoints but will not be included in the primary comparison.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
1753
Inclusion Criteria

Patients fulfilling the inclusion criteria will be eligible for enrollment in this study. Of those who consent, only patients who lack a suitable HLA-identical or 1 allele or antigen mismatched related donors are evaluable. Patients with an HLA-identical sibling or 1 allele or antigen mismatched family member donor are evaluable as long as the center deems the family member donor as unsuitable for other reasons. Patients may co-enroll with other interventional or observational studies.

  1. Patients of all ages with AML, ALL, MDS, NHL, HL, AA, or SCD are eligible.
  2. Any planned conditioning regimen and GVHD prophylaxis approach is eligible.
  3. Patients must be considered suitable allogeneic transplant candidates at the time of enrollment based on medical history, physical examination, and available laboratory tests. Specific testing for organ function is not required for eligibility but, if available, these tests should be used by the treating physician to judge transplant suitability.
  4. Patient and physician must intend to proceed with allogeneic HCT within the next 6 months if a suitable donor is identified.
  5. Center plans to follow the algorithm for alternative donor identification: (a) for subjects who are Very Likely to find a MUD, attempt to identify a matched unrelated donor; (b) for a subjects who are Very Unlikely to find a MUD, proceed expeditiously to a haploidentical, cord blood or mismatched unrelated donor.
  6. Signed informed consent, and assent if applicable. Consent may be signed prior to completion of family typing but patients will only be considered evaluable upon confirmation that there is no suitable HLA-identical or 1 allele or antigen mismatched related donor available.
Exclusion Criteria
  1. Prior allogeneic HCT (prior autologous transplant is allowed)
  2. Previous formal unrelated donor search

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Donor Search Prognosis: MUD Very LikelyDonor Search Prognosis ScorePatients who are Very Likely to find a matched unrelated donor (MUD), defined as having a \>90% chance of finding an 8/8 HLA-matched unrelated donor, for whom a fully matched unrelated donor will be pursued.
Donor Search Prognosis: MUD Less LikelyDonor Search Prognosis ScorePatients with a Less Likely chance of finding a MUD, i.e., those not falling into the other two groups (a 26% chance), will be enrolled onto the observational component of the study and analyzed for all relevant endpoints but will not be included in the primary comparison.
Donor Search Prognosis: MUD Very UnlikelyDonor Search Prognosis ScorePatients who are Very Unlikely to find a MUD, defined as having a \<10% chance of finding an 8/8 HLA-matched unrelated donor, for whom a haploidentical, cord blood, or mismatched unrelated donor transplant will be pursued.
Primary Outcome Measures
NameTimeMethod
Overall Survival for MUD Very Likely and MUD Very Unlikely Arms2 years

Compare overall survival between Very Likely to find a matched unrelated donor search prognosis patients and Very Unlikely to find a matched unrelated donor search prognosis patients who are evaluable.

Secondary Outcome Measures
NameTimeMethod
Cumulative Incidence of Transplant by Donor Search Prognosis Score2 years

To estimate and compare the cumulative incidence of receiving a transplant according to donor search prognosis, regardless of donor search prognosis

Barriers to Transplant2 years

To describe barriers to achieving transplantation with different donor search strategies, regardless of donor search prognosis

Trial Locations

Locations (52)

Children's Hospital Los Angeles

🇺🇸

Los Angeles, California, United States

Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

University of Miami

🇺🇸

Miami, Florida, United States

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

M.D. Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Fred Hutchinson Cancer Research Center

🇺🇸

Seattle, Washington, United States

University of Minnesota

🇺🇸

Minneapolis, Minnesota, United States

Karmanos Cancer Institute

🇺🇸

Detroit, Michigan, United States

University of Oklahoma

🇺🇸

Oklahoma City, Oklahoma, United States

University of Utah

🇺🇸

Salt Lake City, Utah, United States

Mayo Clinic Rochester

🇺🇸

Rochester, Minnesota, United States

University of Nebraska Medical Center - Pediatrics

🇺🇸

Omaha, Nebraska, United States

Oregon Health and Science University

🇺🇸

Portland, Oregon, United States

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

H. Lee Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

University of Michigan

🇺🇸

Ann Arbor, Michigan, United States

Wake Forest Baptist Health

🇺🇸

Winston-Salem, North Carolina, United States

City of Hope

🇺🇸

Duarte, California, United States

University of California, San Diego Medical Center

🇺🇸

La Jolla, California, United States

Stanford Hospitals and Clinics

🇺🇸

Stanford, California, United States

Children's National Medical Center

🇺🇸

Washington, District of Columbia, United States

Memorial Healthcare System

🇺🇸

Pembroke Pines, Florida, United States

Children's Healthcare of Atlanta

🇺🇸

Atlanta, Georgia, United States

Emory University

🇺🇸

Atlanta, Georgia, United States

Indiana University

🇺🇸

Indianapolis, Indiana, United States

Northside Hospital

🇺🇸

Atlanta, Georgia, United States

Loyola University

🇺🇸

Maywood, Illinois, United States

University of Maryland

🇺🇸

Baltimore, Maryland, United States

University of Mississippi

🇺🇸

Jackson, Mississippi, United States

St. Louis Children's Hospital

🇺🇸

Saint Louis, Missouri, United States

University of Nebraska Medical Center - Adults

🇺🇸

Omaha, Nebraska, United States

Washington University in St. Louis

🇺🇸

Saint Louis, Missouri, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

Rosewell Park Cancer Institute

🇺🇸

Buffalo, New York, United States

Mount Sinai Medical Center

🇺🇸

New York, New York, United States

Levine Cancer Institute

🇺🇸

Charlotte, North Carolina, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

University Hospitals Cleveland Medical Center

🇺🇸

Cleveland, Ohio, United States

Nationwide Children's Hospital

🇺🇸

Columbus, Ohio, United States

The Ohio State University

🇺🇸

Columbus, Ohio, United States

Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

Children's Medical Center Dallas

🇺🇸

Dallas, Texas, United States

Cook Children's Medical Center

🇺🇸

Fort Worth, Texas, United States

University of Virginia

🇺🇸

Charlottesville, Virginia, United States

University of Wisconsin

🇺🇸

Madison, Wisconsin, United States

Children's Mercy Hospital

🇺🇸

Kansas City, Missouri, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

University of Florida

🇺🇸

Gainesville, Florida, United States

Virginia Commonwealth University

🇺🇸

Richmond, Virginia, United States

University of North Carolina

🇺🇸

Chapel Hill, North Carolina, United States

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