跳至主要内容
临床试验/NL-OMON21882
NL-OMON21882已完成不适用

Effect of Genestein as food supplement in patients with Sanfilippo syndrome (a double-blind randomised controlled trail).

AMC Amsterdam0 个研究点目标入组 30 人开始时间: 待定最近更新:
适应症

试验速览

阶段
不适用
状态
已完成
发起方
入组人数
30

研究概览

简要总结

/A

研究设计

研究类型
Interventional

入排标准

入选标准

  • 1. The patient should have a biochemically confirmed deficiency of heparan-N-sulfatase (MPSIIIA), A-N-acetylglucosaminidase (MPS IIIB) or Acetyl CoA:ƒÑ-glucosaminide N-acetyltransferase (MPS IIIC);
  • 2. Patients should be able to walk soms steps independent and make some form of contact.

排除标准

  • 1. The parent or legal representative is unwilling to participate;
  • 2. Patient is already using Genestein;

研究者

发起方
AMC Amsterdam

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