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Shifting Brain Excitation-Inhibition Balance in Autism Spectrum Disorder

Not Applicable
Completed
Conditions
Autism Spectrum Disorder
Interventions
Registration Number
NCT03537950
Lead Sponsor
King's College London
Brief Summary

This study investigates brain response to single acute dose of cannabidiol, cannabidivarin, and placebo in healthy men with and without autism spectrum disorder

Detailed Description

Previous research suggests that cannabidiol (CBD) and cannabidivarin (CBDV) could have the potential to shift brain excitation and inhibition (E-I) in the healthy brain and in neurodevelopmental psychiatric conditions, where this balance is disrupted, such as autism spectrum disorder (ASD). However, no study to date has investigated this. Therefore, in this study, we invited 20 healthy men with and without ASD. Each participant received each drug once (600mg CBD/CBDV, or matched placebo) and magnetic resonance imaging was used to obtain measures of brain biochemistry, activity, and connectivity. We further obtained questionnaires, task data, saliva, urine and blood samples, and conducted visual tasks using eye tracking, electroencephalography, and retinal imaging.

Recruitment & Eligibility

Status
COMPLETED
Sex
Male
Target Recruitment
38
Inclusion Criteria
  • men
  • pass diagnostic threshold for ASD on the ADI-R (if informant is available)
  • currently symptomatic on ADOS
  • age 18-50 years
  • can give informed consent
  • IQ>70 (on a standard instrument such as WASI)
  • medication-free in the month preceding participation (but regular medication with drug, which does not affect glutamate or GABA directly may be permitted)
  • willing to provide urine samples to screen for use of illicit substances prior to each scan
Exclusion Criteria
  • IQ<70
  • history of psychosis, co-morbid major mental illness, significant physical illness (heart disease, high blood pressure, seizures)
  • habitual substance misuse (including alcohol)
  • known allergy to cannabis
  • ASD caused by a known genetic syndrome e.g. Fragile X or 22q11 deletion syndrome,
  • past/present treatment for epilepsy
  • Women will be excluded from this pilot study to reduce heterogeneity in a small sample; avoid the issues around exposing women of reproductive age to a drug; and because pregnancy is a routine exclusion criteria for research MRI. Lastly, ASD is more common in men.

Study & Design

Study Type
INTERVENTIONAL
Study Design
CROSSOVER
Arm && Interventions
GroupInterventionDescription
PLC, CBDV, CBDPLCDose order: PL, CBDV, CBD
CBD, PLC, CBDVPLCDose order: CBD, PLC, CBDV
CBDV, PLC, CBDCBDDose order: CBDV, PLC, CBD
CBDV, PLC, CBDCBDVDose order: CBDV, PLC, CBD
PLC, CBD, CBDVCBDDose order: PLC, CBD, CBDV
PLC, CBD, CBDVCBDVDose order: PLC, CBD, CBDV
PLC, CBD, CBDVPLCDose order: PLC, CBD, CBDV
CBD, PLC, CBDVCBDDose order: CBD, PLC, CBDV
CBD, PLC, CBDVCBDVDose order: CBD, PLC, CBDV
CBD, CBDV, PLCPLCDose order: CBD, CBDV, PLC
CBD, CBDV, PLCCBDDose order: CBD, CBDV, PLC
CBD, CBDV, PLCCBDVDose order: CBD, CBDV, PLC
CBDV, PLC, CBDPLCDose order: CBDV, PLC, CBD
CBDV, CBD, PLCPLCDose order: CBDV, CBD, PLC
PLC, CBDV, CBDCBDDose order: PL, CBDV, CBD
CBDV, CBD, PLCCBDDose order: CBDV, CBD, PLC
CBDV, CBD, PLCCBDVDose order: CBDV, CBD, PLC
PLC, CBDV, CBDCBDVDose order: PL, CBDV, CBD
Primary Outcome Measures
NameTimeMethod
Brain biochemistry response to pharmacological stimulationIn the months 1-2 following the last day of scanning.

The measure of brain biochemistry response to PLC, CBD, and CBDV includes the following:

Assessment of the ratio of brain excitation and inhibition (measured as the balance of excitatory and inhibitory neurotransmitters) using using proton magnetic resonance spectroscopy \[1H\]MRS.

Secondary Outcome Measures
NameTimeMethod
Measurement of low frequency brain activity using resting state fMRIIn the months 3-4 following the last day of scanning

In the third and fourth month following the day of the last scan, we will measure whole brain low frequency brain activity using resting state functional magnetic resonance imaging. Measure of activity: fractional amplitude of low frequency fluctuations.

Measurement of brain functional connectivity using resting state fMRIIn the months 5-6 following the last day of scanning

In the fifth and sixth month following the day of the last scan, we will measure whole brain resting state functional connectivity using resting state functional magnetic resonance imaging. Measure of connectivity: correlation between pairs of regions.

Trial Locations

Locations (1)

King's College London

🇬🇧

London, United Kingdom

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