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L-citrulline to Improve Adverse Outcomes in Admitted Children (EChiLiBRiST, Clinical Trial 2, Inpatients)

Not Applicable
Not yet recruiting
Conditions
Child, Only
Infectious Disease
Infections
Interventions
Dietary Supplement: L-citrulline
Dietary Supplement: Placebo
Registration Number
NCT06426147
Lead Sponsor
Barcelona Institute for Global Health
Brief Summary

In low and middle-income countries, children admitted to hospital are not similarly ill, and do not all have a comparable prognosis. In fact, understanding at first encounter their risk of developing adverse outcomes (including mortality) could allow a more focused management and the tailoring of specific interventions to decrease in hospital mortality, and post discharge adverse longer-term outcomes. This clinical trial, part of the EChiLiBRiST larger project ("Development and validation of a quantitative point-of-care test for the measurement of severity biomarkers to improve risk stratification of fever syndromes and enhance child survival") has the two-fold objective of:

1. Assessing whether a POINT-OF-CARE rapid triaging test (PoC RTT) based on the quantitative measurement at the bedside of the "prognostic" biomarker sTREM-1 (soluble-triggering receptor expressed on myeloid cells 1) can reliably identify those admitted children with a higher risk of adverse outcomes; and

2. Assessing whether the therapeutic intervention (the L-arginine precursor, L-Citrulline, key in the nitric oxide biosynthesis), administered orally for 28 days to those children aged 1-\<60 months identified as "moderate-to-high risk" by the prognostic biomarker can improve outcomes as compared to those receiving an indistinguishable placebo.

This second objective will be assessed in a prospective multi-country, multi-site, individually randomised, two-arm, placebo-controlled, double blind clinical trial involving \~888 children 1-\<60m of age admitted to hospital and determined to be at high risk of adverse outcomes by their baseline sTREM-1 levels. The trial will compare the efficacy of a twice-daily dose of L-citrulline syrup vs placebo (200-300mg/kg/day depending on weight-band; for 28 days) in reducing adverse outcomes in children with severe disease. The trial will be running independently but in parallel in two high-mortality settings in Mozambique and in Ethiopia.

Detailed Description

Children admitted to hospital and meeting the study eligibility criteria who are 0-\<60 months of age will be eligible for study inclusion, and for initial biomarker screening using the study-designed rapid triaging PoC test, based on the measurement of sTREM-1. Study participants aged 1m-\<5 years of age with sTREM-1 values classified as moderate (i.e., "yellow") or high-risk (i.e., "red") in the traffic light risk-stratification system will be randomly allocated (1:1) to receive L-Cit intervention or placebo. All study participants will be followed for 6 months, with study visits at the study hospitals or at home or via phone communication after discharge at day 3, day 5, day 7, day 28, and month 6. The study primary outcome will be "adverse disease outcome", defined as a composite of mortality, incident neurological sequelae, major adverse kidney event at discharge, need for organ support, clinical shock, coma, severe respiratory distress or need for readmission within 28 days after recruitment.

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
2200
Inclusion Criteria
  • Enrolled in the initial prognostic screening component.
  • Sick children with fever (axillary temperature>37.5ºC) or a history of fever (within the preceding 72h) or with suspected severe disease.
  • 1m-<60 months of age.
  • With an indication for admission, or having already been admitted to hospital due to their illness.
  • With an sTREM-1 PoC result classifying their disease as of "moderate-high risk" ("yellow" or "red") upon study recruitment and within D3.
  • Residents in the study area or willing to be contacted and traced during the study duration.
  • Willing to sign an informed consent document.
  • Willing to undergo and adhere to study procedures as explained in the IC document.
Exclusion Criteria
  • Admission to hospital for social reasons (and not on account of their disease).
  • Children for which informed consent document has not been signed.
  • Known allergy or contraindication to any of the study supplements including lactose intolerance or observing a lactose-free diet.
  • Concurrent participation in any other clinical trial.
  • Patient under NPO or "nothing by mouth" prescription .
  • Contraindication for the insertion of a nasogastric tube (NGT) of for the enteral administration of drugs through the NGT in children who cannot tolerate by mouth.
  • Critically sick patient whose prognosis is considered by the clinical researcher as fatal outcome in the following hours after screening.
  • Any other condition determined by the investigators that makes it unlikely that the participant would complete the follow up until day 28 of study.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
L-citrullineL-citrulline1 or 2 sachets every 12 hours (200-300mg/kg/day depending on weight-band) for 28 days
PlaceboPlacebo1 or 2 sachets every 12 hours (depending on weight-band) for 28 days
Primary Outcome Measures
NameTimeMethod
Adverse disease outcomeUp to day 28

Proportion of participants with "adverse disease outcome" defined as a composite of (i.e., the occurrence between D0 and D28 after recruitment of at least one -or more- of the following adverse outcomes):

* Mortality

* Incident neurological sequelae

* Major adverse kidney event at discharge (MAKE-DC, defined as a severe AKI event between 2-7 days or a discharge eGFR\<60mL/min per 1.73m2)

* Need for organ support

* Clinical shock

* Coma

* Severe respiratory distress

* Need for readmission within the first 28 days post-recruitment (after having been discharged)

Secondary Outcome Measures
NameTimeMethod
MortalityUp to month 6

Proportion of participants with mortality up to M6

Major adverse kidney eventUp to day 28

Proportion of participants with major adverse kidney event at discharge (MAKE-DC, defined as a severe AKI event between 2-7 days or a discharge eGFR\<60mL/min per 1.73m2)

Clinical shockUp to day 28

Proportion of participants with clinical shock

Severe respiratory distressUp to day 28

Proportion of participants with severe respiratory distress

Lenght of hospitalisationUp to day 28

Length of hospitalisation up to D28 and/or up to hospital discharge

ComaUp to day 28

Proportion of participants with coma

Median duration of antibiotic treatmentUp to day 28

Median duration of antibiotic treatment up to day 28

Radiological pneumoniaUp to day 28

Proportion of participants with radiological pneumonia among children with RTI up to D28 and/or up to hospital discharge

Incident neurological sequelaeUp to day 28

Proportion of participants with incident neurological sequelae between day 0 and day 28 after recruitment and/or up to hospital discharge.

Need for organ supportUp to day 28

Proportion of participants with need for organ support

Need for readmissionUp to day 28

Proportion of participants with need for readmission within the first 28 days post-recruitment (after having been discharged)

Hypoxemia (Sp02 <90%)Up to day 28

Proportion of participants with hypoxemia (Sat 02\<90% irrespective of supplementary oxygen in absence of cyanotic heart disease) up to D28 and/or up to hospital discharge

Secondary consultation or hospitalisationsUp to month 6

Proportion of participants with secondary consultations or hospitalisations up to M6

Proportion of participants with suspected unexpected serious adverse reactionsUp to month 6

Proportion of participants with suspected unexpected serious adverse reactions up to M6.

Proportion of participants with adverse eventsUp to day 30

Proportion of participants with adverse events up to D30.

Oxygen requirementUp to day 28

Proportion of participants with oxygen requirement up to D28 and/or up to hospital discharge

Proportion of participants with serious adverse eventsUp to month 6

Proportion of participants with serious adverse events up to month 6

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