MedPath

A 3-year, Prospective, Non-interventional, Multicenter Registry in Sickle Cell Disease (SCD) Patients

Completed
Conditions
Sickle Cell Disease
Registration Number
NCT01220115
Lead Sponsor
Novartis
Brief Summary

A long term observational study in sickle cell disease will enhance the understanding of the disease patterns, current transfusion practices, treatments and outcomes in sickle cell disease.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
498
Inclusion Criteria
  • Male or female patients with HbSS, HbS/beta-thalassemia and HbSC
  • Age > 2 years old.
  • Written informed consent by the patient or legal guardians, and pediatric assent where indicated.
Exclusion Criteria
  • Patients with Sickle Cell trait (HbAS) are not eligible for the study
  • Patient or legal guardians unable or unwilling to give consent, or pediatric assent where indicated.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Document current treatment patterns, natural history and outcomes in patients with sickle cell diseaseup to 5 years
Secondary Outcome Measures
NameTimeMethod
Measure Sickle cell crisis and hospitalizationsup to 5 years

To evaluate whether patients on regular transfusion protocol have fewer crisis and hospitalizations

Data collectionup to 5 years

Collection of the following data:Current therapies used for the treatment of SCD Current transfusion practices, Difference in treatments between pediatric and adult patients, Use of chelation therapies, Frequency and types of crises including Frequency of hospitalizations, Incidence of end organ damage (caridac, renal, pulmonary,liver), Quality of life assessed by PedsQL TM Pediatric Quality of Life Inventory for patients 2- \<18 years old and SF-36® Health Survey for patients 18 years old and older

Trial Locations

Locations (42)

Hematology Oncology, P.C.

🇺🇸

Stamford, Connecticut, United States

Children's Hospital Oakland (CHO)

🇺🇸

Oakland, California, United States

Hematology Oncology Services of Arkansas

🇺🇸

Little Rock, Arkansas, United States

Children's Hospital of Orange County Sickle Cell Disease Center

🇺🇸

Orange, California, United States

Howard University

🇺🇸

Washington, District of Columbia, United States

Broward Oncology Associates, P.A.

🇺🇸

Fort Lauderdale, Florida, United States

All Children's Hospital

🇺🇸

Saint Petersburg, Florida, United States

University of Illinois at Chicago, Dept of Pediatrics

🇺🇸

Chicago, Illinois, United States

Abington Hematology Oncology Associates, Inc

🇺🇸

Oak Lawn, Illinois, United States

Tulane University School of Medicine

🇺🇸

New Orleans, Louisiana, United States

Johns Hopkins University Division of Hematology

🇺🇸

Baltimore, Maryland, United States

LSU Department of Pediatrics Children's Hospital

🇺🇸

New Orleans, Louisiana, United States

Children's Hospital Boston - Harvard

🇺🇸

Boston, Massachusetts, United States

Oncology-Hematology Associates, P.A.

🇺🇸

Clinton, Maryland, United States

Boston Comprehensive Sickle Cell Center

🇺🇸

Boston, Massachusetts, United States

West Michigan Cancer Center

🇺🇸

Kalamazoo, Michigan, United States

University of Missouri Child Health, Division of Pediatric Hematology/Oncology

🇺🇸

Columbia, Missouri, United States

Children's Mercy Hospital

🇺🇸

Kansas City, Missouri, United States

Research Medical Center

🇺🇸

Kansas City, Missouri, United States

Newark Beth Israel Medical Center

🇺🇸

Newark, New Jersey, United States

New York Methodist Hospital Dept of Med/Sickle Cell Program

🇺🇸

Brooklyn, New York, United States

Interfaith Medical Center-Comprehensive Sickle Cell Program

🇺🇸

Brooklyn, New York, United States

Presbyterian Hospital Pediatric Sickle Cell Program

🇺🇸

Charlotte, North Carolina, United States

Cohen Children's Medical Center of NY (CCMC)

🇺🇸

New Hyde Park, New York, United States

Center for Children's Cancer & Blood Disorders

🇺🇸

Syracuse, New York, United States

Ohio Region VI Sickle Cell Program

🇺🇸

Akron, Ohio, United States

The Children's Medical Center of Dayton

🇺🇸

Dayton, Ohio, United States

Medical University of SC-Pediatric Sickle Cell Center

🇺🇸

Charleston, South Carolina, United States

M. Francisco Gonzalez, M.D., P.A.

🇺🇸

Columbia, South Carolina, United States

Diggs-Kraus Sickle Cell Center

🇺🇸

Memphis, Tennessee, United States

Peninsula Cancer Institute

🇺🇸

Newport News, Virginia, United States

Baylor College of Medicine-Texas Children's Hospital

🇺🇸

Houston, Texas, United States

Rady Children's Hopsital / UC San Diego University Hospital Sickle Cell Disease Center

🇺🇸

San Diego, California, United States

Innovative Medical Research

🇺🇸

Miami, Florida, United States

Miami Children's Hospital

🇺🇸

Miami, Florida, United States

Cincinnati Children's Medical Center

🇺🇸

Cincinnati, Ohio, United States

Meharry Comprehensive Sickle Cell Center

🇺🇸

Nashville, Tennessee, United States

Sickle Cell Disease and Hemoglobinopathy Clinic Children's Hospital at Vanderbilt

🇺🇸

Nashville, Tennessee, United States

Central Tampa Hematology and Oncology Associates

🇺🇸

Tampa, Florida, United States

St. Joseph Children's Hospital

🇺🇸

Tampa, Florida, United States

Maimonides Medical Center

🇺🇸

Brooklyn, New York, United States

M.D. Anderson Cancer Center Orlando

🇺🇸

Orlando, Florida, United States

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