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To asses the role of drug therapy in disease of muscle dysfunction of childre

Not Applicable
Conditions
Health Condition 1: M625- Muscle wasting and atrophy, not elsewhere classified
Registration Number
CTRI/2020/06/025541
Lead Sponsor
All India Institute of Medical Science Rishikesh
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Yet Recruiting
Sex
Not specified
Target Recruitment
0
Inclusion Criteria

1)Molecular / Biopsy based diagnosis of DMD

2)Patients 2 - 10 years of age at time of screening

3)Ambulatory patients

Exclusion Criteria

•History of glucocorticoids intake within the last 3 months

•Use of Metformin or Melatonin within the last 3 months

•Hypersensitivity to Metformin or melatonin

•Suspected malignancy

•Other chronic disease or clinical relevant limitation of renal, liver, heart function according to discretion of investigator

•Participants not willing to give informed consent

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
To compare the change in Functional outcome by using Motor Function Measure (MFM) score after 3 months of Metformin, Melatonin and steroid (combined therapy) vs. steroid monotherapy alone.Timepoint: Three months
Secondary Outcome Measures
NameTimeMethod
1.To assess mean change in time taken to perform Gowerâ??s Maneuver (time taken in seconds to stand up from supine position) <br/ ><br>2.Change in per minute walking distance <br/ ><br>3.To assess change in Muscle weakness based on Medical Research Council (MRC) Scale <br/ ><br>4.Change in 6 minute walking distance (6MWT) <br/ ><br>5.To assess change in weight gain <br/ ><br>6.To assess change in biochemical markers of DMD <br/ ><br>7.To record the associated complications with both the therapies.Timepoint: Three months
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