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Effect of Recombinant Human EPO on the Postoperative Neurologic Outcome in Pediatric Moyamoya Patients

Not Applicable
Active, not recruiting
Conditions
Pediatrics
Cerebrovascular Disorders
Moyamoya Disease
Interventions
Drug: Normal saline
Registration Number
NCT03882060
Lead Sponsor
Seoul National University Hospital
Brief Summary

This study evaluates the effect of recombinant human erythropoietin (rHuEPO) on the neovascularization of pediatric moyamoya disease patients. rHuEPO will be administrated during perioperative period of the first revascularization surgery. Primary outcome (Incidence of Good postoperative MCA territory revascularization by cerebral angiography) will be evaluated after 3-6 month of revascularization surgery.

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
60
Inclusion Criteria
  • Pediatric Moyamoya patients scheduled for the first revascularization surgery
Exclusion Criteria
  • Hypersensitivity or contraindication to rHuEPO
  • History of Unstable hypertension, Hypertensive encephalopathy, Thrombosis
  • Primary intracerebral hemorrhage (ICH), Subarachnoid hemorrhage (SAH), Arterio-venous malformation (AVM), Cerebral aneurysm, or cerebral neoplasm
  • History of seizure
  • Hemoglobin >16 mg/dl
  • Prolonged PT (PT > 15.5 seconds, PT INR > 1.2) or Prolonged aPTT (> 40 seconds)
  • Thrombocytopenia (platelet count < 100,000/microL), Thrombocytosis (platelet count > 400,000/microL), Neutropenia (absolute neutrophil count (ANC) < 1500/microL)
  • Abnormal kidney function (Creatinine> 2.0 mg/dl, History of dialysis)
  • Abnormal hepatic function (aspartate transaminase> 80 unit/L, alanine aminotransferase> 80 unit/L)

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
ControlNormal salineNormal saline 50mL x 3 times Preoperative day (12-24 hour before surgery) During surgery Postoperative day (12-24 hour after surgery)
rHuEPOerythropoietinrecombinant human erythropoietin 500 U/kg IVS x 3 times Preoperative day (12-24 hour before surgery) During surgery Postoperative day (12-24 hour after surgery)
Primary Outcome Measures
NameTimeMethod
postoperative <12 month Angiogenesis<12 month after revascularization operation

Incidence of Good postoperative MCA territory revascularization by cerebral angiography or MRI (3 grade: good, fair, poor)

Secondary Outcome Measures
NameTimeMethod
Preoperative information: Homozygous RNF213If the preoperative w/u is not completed before recruitment, up to 1 week

Homozygous RNF213

Long-term neurologic outcome: Cognitive function assessed by Korean Wechsler Intelligence Scale for Children-Ⅳ (K-WISC-Ⅳ)Outpatient clinical visit, Usually Postoperative 12~18 month, up to 2 years

Cognitive function assessed by Korean Wechsler Intelligence Scale for Children-Ⅳ (K-WISC-Ⅳ, has 4 domaines: Verbal Comprehension Index, Perceptual Reasoning Index, Working Memory Index, Processing Speed Index \> final score is calculated from T-score)

Short-term postoperative outcome: Total hospital stay (days)within the 1st postoperative hospital stay, up to 1 year

Total hospital stay (discharge criteria: Stable V/S + no progressive Sx)

Preoperative Cerebral angiography: Suzuki grade, Bilateral involvementBefore up to 1 year

Cerebral angiography: Suzuki grade(1-6), Bilateral involvement (yes/no)

Preoperative Hemoglobin, Hematocrit, serum EPO levelIf the preoperative w/u is not completed before recruitment, up to 1 week

Preoperative Hemoglobin, Hematocrit, serum EPO level

Short-term postoperative outcome: Incidence and number of the postoperative transient ischemic attack (TIA) within 1 weekup to 1 week

Incidence and number of the postoperative transient ischemic attack (TIA) within 1 week (yes or no)

Short-term postoperative outcome: Adverse neurologic eventwithin the 1st postoperative hospital stay, up to 1 year

seizure, increased intracranial pressure, cerebral infarct, hematoma, reoperation (yes or no)

Effect of rHuEPO on perioperative erythropoiesis: Total intraoperative and perioperative transfusion requirements (mL/kg)within the 1st postoperative hospital stay, up to 1 year

Total intraoperative and perioperative transfusion requirements (mL/kg)

Long-term neurologic outcome: Clinical outcomes (4 grade): Excellent, Good, Fair, PoorOutpatient clinical visit, Usually Postoperative 12~18 month, up to 2 years

Clinical outcomes (4 grade): Excellent, Good, Fair, Poor

Long-term neurologic outcome: Brain MRI/A or Brain perfusion MRIOutpatient clinical visit, Usually Postoperative 12~18 month, up to 2 years

Brain MRI/A or Brain perfusion MRI (2 grade): Favorable, Unfavorable

Short-term postoperative outcome: ICU stay (days)within the 1st postoperative hospital stay, up to 1 year

ICU stay (discharge criteria: Stable V/S + Consciousness)

Effect of rHuEPO on perioperative erythropoiesis: Perioperative Hemoglobin, Hematocrit, serum EPO levelwithin the 1st postoperative hospital stay, up to 1 year

Perioperative Hemoglobin, Hematocrit, serum EPO level

Effect of rHuEPO on perioperative erythropoiesis: GFR, BUN, Creatininewithin the 1st postoperative hospital stay, up to 1 year

GFR, BUN, Creatinine level

Short-term postoperative outcome: Other postoperative complicationswithin the 1st postoperative hospital stay, up to 1 year

e.g. Circulatory failure/arrest, Respiratory failure/arrest, Infection (yes or no)

Postoperative <12 month neurologic outcome: Clinical outcomes (4 grade): Excellent, Good, Fair, PoorOutpatient clinical visit, Usually Postoperative 3~6 month, up to 1 year

Clinical outcomes (4 grade): Excellent, Good, Fair, Poor

Postoperative <12 month neurologic outcome: Brain Perfusion MRI (2 grade): Favorable, UnfavorableOutpatient clinical visit, Usually Postoperative 3~6 month, up to 1 year

Brain Perfusion MRI (2 grade): Favorable, Unfavorable

Preoperative Brain MRI/A or Brain Perfusion MRIIf the preoperative w/u is not completed before recruitment, up to 1 week

Brain MRI/A or Brain Perfusion MRI (2 grade): Favorable, Unfavorable

Trial Locations

Locations (1)

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

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