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Paracetamol Versus Ibuprofen in Premature Infants With Hemodynamically Significant Patent Ductus Arteriosus

Phase 3
Conditions
Patent Ductus Arteriosus After Premature Birth
Interventions
Registration Number
NCT04037514
Lead Sponsor
Máximo Vento Torres
Brief Summary

Multicentric, double-blind clinical trial, which will evaluate the efficacy of iv paracetamol versus standard treatment with ibuprofen in the closure of patent ductus arteriosus in the preterm newborn. Secondarily, we intend to compare the safety of both treatments, increase our knowledge about the pharmacokinetics, pharmacodynamics and pharmacogenetics of paracetamol and ibuprofen in the neonatal period and make a pharmacoeconomic assessment of the use of both drugs.

Detailed Description

Those newborns ≤ 30 weeks of gestational age who are diagnosed in the first 2 weeks of hemodynamically significant ductus arteriosus and who do not meet any exclusion criteria will be eligible to participate in the study.

The PARACETAMOL group will receive intravenous doses of 15 mg/kg administered every 6h for 3 days (up to a maximum of 2 courses, i.e. 6 days). The IBUPROFEN group (control group) will receive the usual treatment, this is an initial dose of 10 mg/kg followed by 5 mg/kg intravenously at 24 and 48 hours after the first (all three doses are considered a treatment course), up a maximum of 2 courses).

A daily echocardiographic control will be performed to evaluate the closure of the ductus. If the ductus remains open and with significant clinical repercussion after completing a 3-day course of treatment, another batch of 3 doses of the same treatment will be administered. If medical treatment fails after two courses (6 days), the possibility of administering a batch of Ibuprofen at usual doses in both groups with the intention of offering standard treatment to all patients will be considered. Once the medical treatment with both drugs is completed if the ductus remains significant, the surgical closure will be carried out.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
300
Inclusion Criteria
  • Written Informed consent of parents/guardians
  • Gestacional Age ≤30 weeks
  • Postnatal age ≤ 2 weeks
  • Need for ventilatory support
  • Born in participating hospital/arrival to them within the period of application of the treatment
  • 1 st episode of hemodynamically significant Patent Ductus Arteriosus
Exclusion Criteria
  • Major congenital malformations or chromosomopathies
  • Refusal to participate and / or sign the informed consent.
  • Impossibility or erroneous randomization
  • Participation in another clinical trial with drugs
  • Diuresis less than 1 ml / kg / h for 8 h prior to treatment
  • Greater than 1.8 mg / dl Creatinine
  • Platelets below 50,000 / uL
  • Active bleeding (tracheal, gastrointestinal and renal)
  • Intraventricular hemorrhage recently (48h) (grades 3-4)
  • Severe hyperbilirubinemia
  • Liver failure or severe coagulopathy
  • Active necrotizing enterocolitis or intestinal perforation
  • Septic shock
  • Imminent death

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
ParacetamolParacetamolIntravenous paracetamol 15 mg/kg/6h for 3 or 6 days
IbuprofenIbuprofenIntravenous ibuprofen 10 mg/kg/24 h (day 1) and 5 mg/kg/24h (day 2 and 3) for 3 or 6 days
Primary Outcome Measures
NameTimeMethod
Rate of closure of the hsPDA after treatment with paracetamol (experimental drug) versus ibuprofen (control drug).24-48 hours after the completion of study intervention

It will include the closure rate after the first course of treatment, considered as ductus diameter \< 1 mm monitored by echocardiography performed by a pediatric cardiology specialist.

Secondary Outcome Measures
NameTimeMethod
Need for surgical ligationfrom randomization until discharge, an average of 2 months
Need for rescue treatment after two courses of treatmentfrom randomization until discharge, an average of 2 months
Need for a second course of treatmentfrom randomization until discharge, an average of 2 months
Closure rate after two treatment coursesfrom randomization until discharge, an average of 2 months
Reopening rate after closurefrom randomization until discharge, an average of 2 months
Closing rate after reopeningfrom randomization until discharge, an average of 2 months
Incidence of early complicationsfrom randomization until discharge, an average of 2 months

oliguria, renal failure, necrotizing enterocolitis, intraventricular hemorrhage, hyperbilirubinemia, gastrointestinal bleeding or perforation

Incidence of late complicationsfrom randomization until 2 years

bronchopulmonary dysplasia, periventricular leukomalacia, necrotizing enterocolitis, retinopathy of the newborn, neurodevelopmental assessment, sepsis, death

Pharmacodynamics model of paracetamol in the context of hsPDA: Maximum Plasma Concentration [Cmax]24-48 hours after the completion of study intervention

Relation of effectiveness/adverse reactions to serum levels

Pharmacodynamics model of paracetamol in the context of hsPDA: Minimum Plasma Concentration [Cmin]24-48 hours after the completion of study intervention

Relation of effectiveness/adverse reactions to serum levels

Pharmacodynamics model of paracetamol in the context of hsPDA: Area Under the Curve [AUC])24-48 hours after the completion of study intervention

Relation of effectiveness/adverse reactions to serum levels

Time required until closingfrom randomization until discharge, an average of 2 months
Pharmacodynamics model of paracetamol in the context of hsPDA: urine metabolites24-48 hours after the completion of study intervention

Quantification of metabolites in urine and its relationship with drug elimination/metabolism

Pharmacogenetics of paracetamol24-48 hours after the completion of study intervention

Genetic polymorphisms in TFAP2B, TGFBR2, EPAS1, MD-2 and GM2A genes related to efficacy/occurrence of adverse reactions

Genotoxicity mesured by %DNA damagefrom randomization until discharge, an average of 2 months
Price-effectiveness ratio. Cost-effectiveness analysis depending on the efficiency obtained in the treatment.from randomization until discharge, an average of 2 months

Trial Locations

Locations (4)

Hospital Reina Sofía

🇪🇸

Córdoba, Cordoba, Spain

Hospital Universitario de Cabueñes

🇪🇸

Gijón, Spain

Hospital Universitari i Politècnic La Fe

🇪🇸

Valencia, Spain

Hospital Materno-Infantil (Hospital Regional Carlos Haya) Málaga:

🇪🇸

Málaga, Spain

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