跳至主要内容
临床试验/NL-OMON22791
NL-OMON22791招募中不适用

Effects of exercise therapy in mildly affected patients with Pompe's disease, long-term follow-up study

This study is funded by a grant from Prinses Beatrix Spierfonds.0 个研究点目标入组 46 人开始时间: 待定最近更新:
适应症

试验速览

阶段
不适用
状态
招募中
发起方
入组人数
46

研究概览

简要总结

/A

研究设计

研究类型
Observational

入排标准

入选标准

  • Participants of the training study in 2011
  • - Controls: didn't participate in the training study in 2011, but were eligible to participate: mildly affected in 2011
  • - Confirmed disease (DNA mutation analysis and enzyme activity in leukocytes)
  • - Receiving at least 8 years of enzyme replacement therapy

排除标准

  • - Controls depending on walking aids in 2011
  • - Controls (partially) depending on ventilation in 2011

研究者

发起方
This study is funded by a grant from Prinses Beatrix Spierfonds.

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