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Effects of exercise therapy in patients with Pompe's disease

Recruiting
Conditions
Pompe's disease
Registration Number
NL-OMON22791
Lead Sponsor
This study is funded by a grant from Prinses Beatrix Spierfonds.
Brief Summary

/A

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
Not specified
Target Recruitment
46
Inclusion Criteria

Participants of the training study in 2011
- Controls: didn't participate in the training study in 2011, but were eligible to participate: mildly affected in 2011
- Confirmed disease (DNA mutation analysis and enzyme activity in leukocytes)
- Receiving at least 8 years of enzyme replacement therapy

Exclusion Criteria

- Controls depending on walking aids in 2011
- Controls (partially) depending on ventilation in 2011

Study & Design

Study Type
Observational non invasive
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Endurance
Secondary Outcome Measures
NameTimeMethod
Muscle strength, muscle function, core stability and quality of life
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