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A Multicenter Trial Assessing the Impact of Lipoprotein(a) Lowering With Pelacarsen (TQJ230) on the Progression of Calcific Aortic Valve Stenosis

Phase 2
Recruiting
Conditions
Aortic Stenosis
Interventions
Drug: Matching placebo
Registration Number
NCT05646381
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

The purpose of this study is to evaluate the efficacy, safety and tolerability of pelacarsen (TQJ230) administered subcutaneously once monthly compared to placebo in slowing the progression of calcific aortic valve stenosis.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
502
Inclusion Criteria
  • Male and female ≥50 to <80 years of age
  • Lp(a) ≥175 nmol/L at the screening visit, measured at the Central laboratory
  • Mild or moderate calcific aortic valve stenosis
  • At the randomization visit, participant must be optimally treated for existing CV risk factors
Exclusion Criteria
  • Severe calcific aortic valve stenosis
  • Uncontrolled hypertension
  • History of malignancy of any organ system
  • History of hemorrhagic stroke or other major bleeding
  • Platelet count ≤ LLN
  • Active liver disease or hepatic dysfunction
  • Significant kidney disease
  • Pregnant or nursing women

Other protocol-defined inclusion/exclusion criteria may apply

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Pelacarsen (TQJ230) 80mgPelacarsen (TQJ230) 80mgPelacarsen (TQJ230) 80 mg prefilled syringe injected monthly, administered subcutaneously
Matching placeboMatching placeboPlacebo to match pelacarsen (TQJ230) prefilled syringe injected monthly, administered subcutaneously
Primary Outcome Measures
NameTimeMethod
Change in peak aortic jet velocity36 months

To demonstrate the superiority of pelacarsen (TQJ230) vs. placebo in slowing the progression of calcific aortic valve stenosis by evaluating the change from baseline to month 36 in peak aortic jet velocity by echocardiography

Change in aortic valve calcium score36 months

To demonstrate the superiority of pelacarsen (TQJ230) vs. placebo in slowing the progression of calcific aortic valve stenosis by evaluating the change from baseline to month 36 in aortic valve calcium score by computed tomography

Secondary Outcome Measures
NameTimeMethod
Change in Lp(a) levels12 months

To assess the effect of pelacarsen (TQJ230) vs. placebo on the reduction of Lp(a) levels from baseline to month 12

Change in fibrocalcific thickening of the aortic valve36 months

To assess the effect of pelacarsen (TQJ230) vs. placebo in slowing the progression of CAVS by evaluating the change from baseline to month 36 in fibrocalcific thickening of the aortic valve by contrast CT

Time from randomization to first occurrence of composite clinical endpoint eventUp to 36 months

To assess the effect of pelacarsen (TQJ230) vs. placebo in reducing the risk of composite clinical endpoint defined as reaching either:

1. Unplanned CAVS related hospital admission

2. Aortic valve intervention

3. Death related to calcific aortic valve stenosis

Trial Locations

Locations (29)

Heart Center Research Llc

🇺🇸

Huntsville, Alabama, United States

Cardiovascular Res Found

🇺🇸

Beverly Hills, California, United States

National Heart Institute

🇺🇸

Beverly Hills, California, United States

Valley Clinical Trials

🇺🇸

Northridge, California, United States

University Of California San Diego

🇺🇸

San Diego, California, United States

UC San Francisco Medical Center

🇺🇸

San Francisco, California, United States

Stanford University Medical Center

🇺🇸

Stanford, California, United States

Excel Medical Clinical Trials LLC

🇺🇸

Boca Raton, Florida, United States

Inpatient Research Clinical LLC

🇺🇸

Miami Lakes, Florida, United States

Advanced Research for Health Improvement LLC

🇺🇸

Naples, Florida, United States

Midwest Heart and Vascular Spec

🇺🇸

Overland Park, Kansas, United States

Tufts Medical Center

🇺🇸

Boston, Massachusetts, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Brigham and Womens Hosp Harvard Med School

🇺🇸

Boston, Massachusetts, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

William Beaumont Hospital

🇺🇸

Royal Oak, Michigan, United States

Minneapolis Heart Institute

🇺🇸

Minneapolis, Minnesota, United States

University Of Minnesota

🇺🇸

Minneapolis, Minnesota, United States

Overlook Medical Center

🇺🇸

Summit, New Jersey, United States

New York Presbyterian Hospital

🇺🇸

New York, New York, United States

Icahn School of Med at Mt Sinai

🇺🇸

New York, New York, United States

Strong Memorial Hospital

🇺🇸

Rochester, New York, United States

Wake Forest University Baptist Medical Center

🇺🇸

Winston-Salem, North Carolina, United States

Carl and Edyth Lindner Ctr for Resch and Ed at The Christ Hosp

🇺🇸

Cincinnati, Ohio, United States

Ohio State University

🇺🇸

Columbus, Ohio, United States

Perelman School of Medicine

🇺🇸

Philadelphia, Pennsylvania, United States

Virginia Heart

🇺🇸

Falls Church, Virginia, United States

Carient Heart and Vascular

🇺🇸

Manassas, Virginia, United States

Novartis Investigative Site

🇬🇧

Tyne And Wear, United Kingdom

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