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Trial of Mifepristone for Fibroids

Phase 3
Completed
Conditions
Leiomyoma
Interventions
Drug: Inert Capsule
Registration Number
NCT00133705
Lead Sponsor
University of Rochester
Brief Summary

The purpose of this trial is to determine if low-dose mifepristone benefits women with symptomatic fibroids.

Detailed Description

This trial is designed to assess the efficacy and tolerability of mifepristone 5 mg given daily for 6 months to pre-menopausal women with symptomatic fibroids. The primary study outcome will be disease-specific quality of life. Secondary outcome measures include global quality of life, pain, bleeding, potential adverse effects, tumor size, and endometrial effects. The researchers will also examine a the effect of mifepristone on uterine blood flow. Randomization of study subjects will be stratified in order to ensure that equal numbers of women with moderate and severe symptoms will be enrolled in the placebo and control groups.

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
70
Inclusion Criteria
  • Gender: Female
  • Age: 18 - premenopausal
  • Have at least moderate symptoms of menorrhagia or pelvic pain/pressure
  • Have a total uterine volume greater than or equal to 160 cc by ultrasound measurement and at least one fibroid that is => 2.5cm in size
  • Have a score of equal to or greater than 39 on the Uterine Fibroid Symptom and Quality of Life scale
  • Declined standard treatment options for symptomatic fibroids
  • Agree to use a double-barrier method (condoms, diaphragms) or other effective non-hormonal methods of contraception (abstinence, sterilization) throughout participation in the study to prevent pregnancy and to report any exposure to pregnancy to the research staff immediately
  • Willing and able to give informed consent
  • Willing and able to comply with study requirements
Exclusion Criteria
  • Current or planned pregnancy during the study period

  • Menopausal, as indicated by follicle stimulating hormone (FSH) level of the reference laboratory

  • Currently breast-feeding

  • Untreated abnormal pap smear

  • Presence of conditions other than fibroids contributing to pain and/or bleeding

  • Hemoglobin < 9.0 mg/dl

  • Presence of adnexal masses or tenderness indicating further evaluation or surgery

  • Grade III or IV hydronephrosis by ultrasound

  • Severe, active mental health disorder

  • Active substance abuse or dependence

  • Presence of any contraindication to mifepristone including:

    • Adrenal insufficiency by history
    • Sickle cell disease
    • Active liver disease (liver function tests greater than 1.5 times upper range of normal)
    • Severe, respiratory disease (P02 saturation< 92%)
    • Renal disease (serum creatinine > 1.5 mg/dl)
    • Blood clotting defect. (abnormal PT and PTT)
    • Thromboembolic disease (history of deep vein thrombosis or pulmonary embolus)
  • Current or recent (within the past 3 months) use of the following medications:

    • Oral or systemic corticosteroids
    • Hormones: estrogens, progestins, oral contraceptives
    • Danazol, anticoagulants
  • Herbal or botanical supplements with possible hormonal effects.

  • Use within the past six months of the gonadotropin releasing hormones (GnRH) analogs or Depo-Provera.

  • Current or planned use during the study of any of the following medications/or products:

    • ketoconazole,
    • itraconazole,
    • erythromycin,
    • grapefruit juice,
    • rifampin,
    • St John's Wort,
    • phenytoin,
    • phenobarbital, or
    • carbamazepine

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Inert capsuleInert CapsulePlacebo (for Mifepristone) capsule of nearly identical color, size, and weight taken once daily by mouth
MifepristoneMifepristoneMifepristone 5 MG capsule taken once daily by mouth
Primary Outcome Measures
NameTimeMethod
Uterine Volume6 months

Uterine volume is measured in mLs

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

University of Rochester School of Medicine & Dentistry

🇺🇸

Rochester, New York, United States

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