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Curcumin in Treating Patients With Familial Adenomatous Polyposis

Phase 2
Completed
Conditions
Familial Adenomatous Polyposis
Interventions
Other: Laboratory Biomarker Analysis
Other: Placebo
Registration Number
NCT00641147
Lead Sponsor
National Cancer Institute (NCI)
Brief Summary

This randomized phase II trial studies curcumin in treating patients with familial adenomatous polyposis. Curcumin may prevent colorectal cancer in patients with a history of rectal polyps or colorectal neoplasia.

Detailed Description

Specific Aims:

I. To determine in a randomized, double-blinded, placebo-controlled study the tolerability and effectiveness of curcumin to regress intestinal adenomas by measuring duodenal and colorectal/ileal polyp number, and polyp size in familial adenomatous polyposis patients with intact colons, ileorectal anastomosis surgery, or ileo-anal pullthrough (reservoir) surgery.

II. To measure markers of cell proliferation including colorectal mucosal levels of ornithine decarboxylase (ODC), polyamines, mucosal deoxyribonucleic acid (DNA) methylation, proliferative index (Ki67 antiproliferative cell nuclear antibody), apoptosis index, vascular density, mucosal prostaglandin, leukotriene levels, and activation of the nuclear factor kappa B (NFKB), and v-akt murine thymoma viral oncogene homolog 1 (Akt) survival pathways.

OUTLINE: Patients are randomized to 1 of 2 treatment arms.

Arm I: Patients receive curcumin orally (PO) twice daily (BID) for 12 months.

Arm II: Patients receive placebo PO BID for 12 months.

After completion of study treatment, patients are followed up at 4 months.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
44
Inclusion Criteria
  • Patients with familial adenomatous polyposis who have undergone subtotal colectomy with ileorectal anastomosis, total colectomy with ileo-anal pull through (reservoir), and patients with intact colons with 5 or more adenomas in the rectum-sigmoid or reservoir
  • Patients with familial adenomatous polyposis (FAP) and duodenal adenomatous polyposis without current lower tract adenomatous polyposis i.e. status/post (s/p) ileostomy
Exclusion Criteria
  • Female patients of childbearing age not on effective birth control
  • Pregnant women
  • White blood cell count (WBC) < 3500/ml
  • Platelet count < 100,000/ml
  • Blood urea nitrogen (BUN) > 25mg%
  • Creatinine > 1.5mg%
  • Patients unable to stop non-steroidal anti-inflammatory drugs (NSAIDs), aspirin, curcumin, tumeric, calcium, vitamin D, green tea, or polyphenol E supplements for the duration of the trial
  • Malignancy other than nonmelanoma skin cancer
  • Active bacterial infection
  • Patients with symptoms of active gastroesophageal reflux disease (GERD) (symptomatic despite medication or current erosive esophagitis on endoscopy)
  • Patients with a history of peptic ulcer disease
  • Patients on warfarin or plavix

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm II (placebo)Laboratory Biomarker AnalysisPatients receive placebo PO BID for 12 months. Laboratory Biomarker Analysis
Arm I (curcumin)Laboratory Biomarker AnalysisPatients receive curcumin PO BID for 12 months. Laboratory Biomarker Analysis
Arm II (placebo)PlaceboPatients receive placebo PO BID for 12 months. Laboratory Biomarker Analysis
Arm I (curcumin)CurcuminPatients receive curcumin PO BID for 12 months. Laboratory Biomarker Analysis
Primary Outcome Measures
NameTimeMethod
Polyp NumberUp to 12 months

Average number of polyps in the placebo arm at the end of the study is compared to the average in the curcumin arm

Secondary Outcome Measures
NameTimeMethod
Number of Participants With a Decrease in Polyp Burden at 12 Months12 months

The polyp burden as evaluated by video tape review. Polyp burden at 12 months compared to time 0 for each participant and counting participants with decrease in polyp burden at 12 months.

Medication ComplianceUp to 12 months

Medication compliance of the participant= number of capsules taken divided by the number of capsules prescribed as determined by pill count and described as a percentage per participant. Then the compliance of each participant in the assigned group (curcumin or placebo) was averaged together to obtain the medication compliance rate of that group.

Change in Ornithine Decarboxylase (ODC) Activity LevelsBaseline and 8 months

Change in ODC mean activity levels (expressed as nmol of activity/mg of mucosal tissue/hr) at 8 months compared to baseline (time 0)

Change in Total Polyamines LevelsBaseline and 8 months

Polyamine mean level changes (expressed as pg/mg protein) at month 8-baseline

Change in Micro RNA 124-U6 (miR124-U6)Baseline and 8 months

Change in MicroRNA mean activity level at 8 months compared to baseline (time 0)

Mean Polyp Size in mmUp to 12 months

Mean size of the 5 largest polyps

Change in Spermine Oxidase (SMOX)Baseline and 8months

Change in SMOX mean activity level at 8 months compared to baseline (time 0)

Number of Participants With Grade >=2 Adverse EventsUp to 12 months

Events were graded as follows:

Grade 0= no adverse event or within normal limits; Grade 1= mild adverse event (causing no limitations of usual activity); Grade 2= moderate adverse event (causing some limitation of activity); Grade 3= severe adverse event (severe and undesirable; causing inability to carry out usual activities; Grade 4= life threatening or disabling adverse event; Grade 5= fatal adverse event.

Change in Spermidine/Spermine N-1 Acetyl Transferase (SSAT)Baseline and 8 months

Change in SSAT mean activity level at 8 months compared to baseline (time 0)

Change in Ki-67 Anti-proliferative Cell Nuclear Antibody Index LevelsBaseline up to 8 months

Change in cellular proliferation rate was measured by assessment of Ki-67 anti-proliferative cell nuclear antibody index levels at 8 months

Change in Apoptosis Index Levels8 months

Change in apoptosis index levels at 8 months by assessing cleaved Caspase-3 measurement

Trial Locations

Locations (2)

University of Puerto Rico

🇵🇷

San Juan, Puerto Rico

Johns Hopkins University/Sidney Kimmel Cancer Center

🇺🇸

Baltimore, Maryland, United States

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