MedPath

RRx-001 in Lung Cancer, Ovarian Cancer and Neuroendocrine Tumors Prior to Re-administration of Platinum Based Doublet Regimens (QUADRUPLE THREAT)

Phase 2
Completed
Conditions
Carcinoma, Non-Small-Cell Lung
Neuroendocrine Tumors
Small Cell Carcinoma
Ovarian Epithelial Cancer
Interventions
Registration Number
NCT02489903
Lead Sponsor
EpicentRx, Inc.
Brief Summary

This study is designed to explore the potential of the epigenetic agent RRx-001 to sensitize patients who previously received and now have failed a platinum based doublet regimen. RRx-001 is administered with autologous blood once weekly followed by or in combination with reintroduction of platinum-based doublet therapy.

Detailed Description

This is an open label, four 'cohort' study for administration of RRx-001 with autologous blood once weekly followed by or in combination with reintroduction of platinum-based doublet therapy according to the treatment schedule listed below. Small cell carcinoma and ovarian cohort participants will be randomized to 1 of 2 treatment arms, respectively. Neuroendocrine and NSCLC patients will be enrolled to single arms.

Participants with SCC will receive one of the following; RRx-001 followed by platinum doublet chemotherapy or platinum based chemotherapy alone. HGNEC, RRx-001 followed by platinum doublet chemotherapy. NSCLC, RRx-001 followed by platinum doublet chemotherapy. Participants with Platinum Refractory/Resistant Ovarian and MMMT will receive one of the following, RRx-001 followed by platinum doublet chemotherapy or chemotherapy alone.

Approximately 213 participants will be enrolled.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
139
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Small Cell Lung Cancer (Arm 2)CisplatinCarboplatin or cisplatin plus etoposide or irinotecan or vinorelbine until progression or intolerable toxicity
Non Small Cell Lung CancerPaclitaxelRRx-001 weekly for 3 weeks followed by up to 6 cycles of cisplatin or carboplatin plus paclitaxel or nab-paclitaxel or pemetrexed and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Non Small Cell Lung CancerNab-PaclitaxelRRx-001 weekly for 3 weeks followed by up to 6 cycles of cisplatin or carboplatin plus paclitaxel or nab-paclitaxel or pemetrexed and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Small Cell Lung Cancer (Arm 2)CarboplatinCarboplatin or cisplatin plus etoposide or irinotecan or vinorelbine until progression or intolerable toxicity
Ovarian epithelial cancer (Arm 2)TaxaneCarboplatin, Etoposide, Doxil, Gemcitabine or Vinorelbine or Taxane until progression or intolerable toxicity
Ovarian epithelial cancer (Arm 2)DoxilCarboplatin, Etoposide, Doxil, Gemcitabine or Vinorelbine or Taxane until progression or intolerable toxicity
Small Cell Lung Cancer (Arm 1)RRx-001RRx-001 weekly for 3 weeks followed by up to 4 cycles of carboplatin or cisplatin plus etoposide and then RRx-001 and carboplatin or cisplatin (for patients with stable disease (SD) or better at discontinuation of platinum).
Small Cell Lung Cancer (Arm 1)CisplatinRRx-001 weekly for 3 weeks followed by up to 4 cycles of carboplatin or cisplatin plus etoposide and then RRx-001 and carboplatin or cisplatin (for patients with stable disease (SD) or better at discontinuation of platinum).
Small Cell Lung Cancer (Arm 1)EtoposideRRx-001 weekly for 3 weeks followed by up to 4 cycles of carboplatin or cisplatin plus etoposide and then RRx-001 and carboplatin or cisplatin (for patients with stable disease (SD) or better at discontinuation of platinum).
Small Cell Lung Cancer (Arm 2)EtoposideCarboplatin or cisplatin plus etoposide or irinotecan or vinorelbine until progression or intolerable toxicity
Small Cell Lung Cancer (Arm 1)CarboplatinRRx-001 weekly for 3 weeks followed by up to 4 cycles of carboplatin or cisplatin plus etoposide and then RRx-001 and carboplatin or cisplatin (for patients with stable disease (SD) or better at discontinuation of platinum).
Small Cell Lung Cancer (Arm 2)IrinotecanCarboplatin or cisplatin plus etoposide or irinotecan or vinorelbine until progression or intolerable toxicity
Small Cell Lung Cancer (Arm 2)VinorelbineCarboplatin or cisplatin plus etoposide or irinotecan or vinorelbine until progression or intolerable toxicity
Non Small Cell Lung CancerCisplatinRRx-001 weekly for 3 weeks followed by up to 6 cycles of cisplatin or carboplatin plus paclitaxel or nab-paclitaxel or pemetrexed and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Non Small Cell Lung CancerCarboplatinRRx-001 weekly for 3 weeks followed by up to 6 cycles of cisplatin or carboplatin plus paclitaxel or nab-paclitaxel or pemetrexed and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Non Small Cell Lung CancerPemetrexedRRx-001 weekly for 3 weeks followed by up to 6 cycles of cisplatin or carboplatin plus paclitaxel or nab-paclitaxel or pemetrexed and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Neuroendocrine tumorsCisplatinRRx-001 weekly until progression followed by up to 6 cycles of carboplatin or cisplatin plus etoposide and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Neuroendocrine tumorsEtoposideRRx-001 weekly until progression followed by up to 6 cycles of carboplatin or cisplatin plus etoposide and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Ovarian epithelial cancer (Arm 2)CarboplatinCarboplatin, Etoposide, Doxil, Gemcitabine or Vinorelbine or Taxane until progression or intolerable toxicity
Neuroendocrine tumorsCarboplatinRRx-001 weekly until progression followed by up to 6 cycles of carboplatin or cisplatin plus etoposide and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Ovarian epithelial cancer (Arm 2)EtoposideCarboplatin, Etoposide, Doxil, Gemcitabine or Vinorelbine or Taxane until progression or intolerable toxicity
Ovarian epithelial cancer (Arm 1)CarboplatinRRx-001 weekly for 2 weeks followed by 2 cycles of Carboplatin chemotherapy and then RRx-001/Carboplatin maintenance (for patients with stable disease or better at discontinuation of platinum).
Ovarian epithelial cancer (Arm 2)VinorelbineCarboplatin, Etoposide, Doxil, Gemcitabine or Vinorelbine or Taxane until progression or intolerable toxicity
Ovarian epithelial cancer (Arm 2)GemcitabineCarboplatin, Etoposide, Doxil, Gemcitabine or Vinorelbine or Taxane until progression or intolerable toxicity
Non Small Cell Lung CancerRRx-001RRx-001 weekly for 3 weeks followed by up to 6 cycles of cisplatin or carboplatin plus paclitaxel or nab-paclitaxel or pemetrexed and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Neuroendocrine tumorsRRx-001RRx-001 weekly until progression followed by up to 6 cycles of carboplatin or cisplatin plus etoposide and then RRx-001 maintenance (for patients with stable disease or better at discontinuation of platinum).
Ovarian epithelial cancer (Arm 1)RRx-001RRx-001 weekly for 2 weeks followed by 2 cycles of Carboplatin chemotherapy and then RRx-001/Carboplatin maintenance (for patients with stable disease or better at discontinuation of platinum).
Primary Outcome Measures
NameTimeMethod
Overall SurvivalFrom start of treatment through death for up to 64 months from Start of Treatment.

From the time from enrollment until the time of death from any cause or last follow-up. Patients will be followed clinically as outlined in the treatment schedule and will be followed off study for death.

Secondary Outcome Measures
NameTimeMethod
Overall Response Rate (ORR)Assessed up to 49 months

Overall Response Rate (ORR) will be defined as the proportion of patients with a CR or a PR per RECIST v1.1 based upon the best response as assessed; confirmation of response was not required, assessed up to 49 months.

Disease Control Rate (DCR)Assessed up to 49 months

The percentage of patients who have achieved complete response, partial response and stable disease (as per RECIST v1.1), assessed up to 49 months.

Progression Free Survival (PFS)Assessed up to 49 months

Progression-free survival (PFS) will be defined as the elapsed time from the from date of randomization until the date of first documented progression or date of death from any cause, whichever came first, assessed up to 49 months.

Trial Locations

Locations (10)

Stanford University

🇺🇸

Palo Alto, California, United States

Baptist Health

🇺🇸

Lexington, Kentucky, United States

Memorial Hospital of South Bend

🇺🇸

South Bend, Indiana, United States

Washington University

🇺🇸

Saint Louis, Missouri, United States

Henry Ford Allegiance Health

🇺🇸

Jackson, Michigan, United States

Virginia Cancer Specialists

🇺🇸

Fairfax, Virginia, United States

Walter Reed National Military Medical Center

🇺🇸

Bethesda, Maryland, United States

University of Cincinnati Cancer Institute

🇺🇸

Cincinnati, Ohio, United States

West Virginia University

🇺🇸

Morgantown, West Virginia, United States

VA Connecticut Cancer Center

🇺🇸

West Haven, Connecticut, United States

© Copyright 2025. All Rights Reserved by MedPath