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Phase II Trial of Oral Vinorelbine in Children With Recurrent or Progressive Unresectable Low-Grade Glioma

Phase 2
Completed
Conditions
Low-Grade Glioma
Interventions
Registration Number
NCT02197637
Lead Sponsor
Centre Oscar Lambret
Brief Summary

The purpose of this study is to determine whether oral vinorelbine is effective in the treatment of children with progressive or recurrent unresectable low grade glioma.

Detailed Description

The aim of this study is to determine efficacy of oral vinorelbine in children with progressive or recurrent unresectable low grade glioma, in addition to safety, pharmacokinetic, pharmacogenetic, medical costs and quality of life.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
39
Inclusion Criteria

TUMOR CHARACTERISTICS:

  • Histologically confirmed recurrent or progressive primary Low-Grade Glioma (LGG) defined as follow (WHO classification 2007): optic pathway glioma (OPG), pilocytic astrocytoma (PA), fibrillary or diffuse astrocytoma (DA), oligodendroglioma (OG) or oligoastrocytoma (OA)
  • Patients with OPG do not require biopsy confirmation of disease, if clinical and radiological findings as well as ophthalmological examination are unequivocal
  • Low-Grade Glioma involving the brainstem can be included in case of histological confirmation
  • Tumor has to be considered as non totally resectable

PATIENT CHARACTERISTICS:

  • Age 6-18 years old
  • Lansky or Karnofsky status more than 50 %
  • Measurable disease on cerebral and/or spinal MRI, with at least 1 lesion diameter superior to 1 cm
  • Patients with metastatic disease are eligible, but at least 1 lesion must be measurable as previously defined
  • Patients must have received at least 1 prior chemotherapy regimen containing carboplatin
  • Life expectancy of at least 3 months
  • Evidence of adequate organ functions, including:
  • neutrophil count (ANC) ≥ 1500/mm3 ,
  • platelet count ≥100 000/mm3 ;
  • serum creatinine < 1.5 x normal for age when the serum creatinine is ≥ 1.5 × the ULN, the glomerular filtration rate (either estimated or formal) must be > 70 mL/min/1.73m2;
  • total bilirubin< 1.5 x normal for age,
  • ASAT and ALAT < 2.5 x normal for age
  • Effective contraception for patients (male and female) with reproductive potential, and for a minimum of 3 months after the end of treatment
  • Negative pregnancy test, if applicable
  • Patients able to swallow capsules
  • Patient affiliated with a health insurance system
  • Written informed consent of patient and/or parents/guardians prior to the study participation.

PRIOR OR CONCURRENT THERAPY

  • Prior treatments containing vinca alkaloids like vincristine and/or vinblastine are authorized
  • Patients must have fully recovered from the toxic effects of any prior therapy before entering the study. No organ toxicity superior to grade 2 according to NCI-CTCAE v4.0
  • An interval of at least 2 months from prior radiotherapy, 6 weeks from nitrosourea chemotherapy, and 4 weeks from other chemotherapy regimen, is required
Exclusion Criteria
  • Inclusion criteria failure
  • Prior treatment with intravenous or oral vinorelbine
  • Known hypersensibility to other vinca-alkaloïdes
  • Digestive pathology affecting absorption in a important way
  • Prior surgical resection of stomach or the small intestine
  • Severe hepatic failure independent from tumoral disease
  • Fructose intolerance
  • Leptomeningeal relapse without any available measurable disease on MRI (for example, leptomeningeal relapse with totally resected primary lesion)
  • Uncontrolled active infection within 2 weeks
  • Pregnancy or breast feeding woman
  • Uncontrolled intercurrent illness or active infection
  • Unsuitable for medical follow-up (geographic, social or mental reasons)
  • Patients requiring long-term oxygen therapy
  • Patients with ANC less than 1500/mm3
  • Patients vaccinated against yellow fever

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
ORAL VINORELBINEORAL VINORELBINEOrally vinorelbine 60 mg/m2 D1, 8 and 15 Cycle of 28 days For a maximum of 12 cycles The dose of vinorelbine should be increased to 80 mg/m2 from the 2nd cycle
Primary Outcome Measures
NameTimeMethod
Progression free survival9 months

no progressive disease according to RANO criteria

Secondary Outcome Measures
NameTimeMethod
Response rate12 months

Complete, partial and minor responses according to RANO criteria

Progression Free Survival PFS36 months

No progressive disease according to RANO criteria

Overall Survival OS36 months

Death incidence

Adverse events12 months

According to NCI-CTC AE scale v4.0

Growth Modulation Index GMI36 months

GMI defined as PFS2/ PSF1 ratio (PFS2 = PFS since the beginning of study treatment ; PFS1 = PFS observed in previous line of treatment)

Modifications of tumor aspects in diffusion and perfusion MRIAt each tumor assessment, after 3, 6, 9 and 12 cycles of treatment, at the end of study, then every 4 months during the first year post therapy, then every 6 months for 3 years, if no prior progressive disease

Cerebral and/or spinal MRI (morphological and functional) with 2 dimensional assessment of target lesions.

Constitutional polymorphisms of cyp3A5, ABCB1Before the start of treatment

Single nucleotide polymorphisms (SNPs) will be analyzed by real time PCR and correlated with efficacy and toxicity of vinorelbine

Pharmacokineticcycles 1 and 2, prior to the initial dose, 30 min, 1, 1.5, 2, 3, 6, 8, 10 and 26 hours post-dose

Plasmatic concentrations measured by LC-MS/MS (liquid chromatography tandem mass spectrometry) ; Area under the curve (AUC), maximal concentration (Cmax), time to Cmax (Tmax).

Medical costsduring all the study (up to 1 year)

Costs of medical care including : hospitalisations, emergency admissions, nursing care at home, medical consultations, diet support...

Health Utilities Index (HUI)Before the treatment, then at day 1 of 1st cycle, after the 3th, 6th, 9th and the 12th cycles of study treatment, and at the end of study (up to 1 year)

Health Utilities Index (HUI)

Trial Locations

Locations (16)

Hôpital de la TIMONE

🇫🇷

Marseille, France

CHU de Rouen

🇫🇷

Rouen, France

Institut Gustave Roussy

🇫🇷

Villejuif, France

CHU de Bordeaux

🇫🇷

Bordeaux, France

Centre Léon Bérard

🇫🇷

Lyon, France

CHU de Nancy

🇫🇷

Nancy, France

CHU de Limoges

🇫🇷

Limoges, France

Institut Curie

🇫🇷

Paris, France

Hôpital Hautepierre

🇫🇷

Strasbourg, France

CHU de Reims

🇫🇷

Reims, France

CHU d'Angers

🇫🇷

Angers, France

Centre Oscar Lambret

🇫🇷

Lille, France

CHRU Arnaud de Villeneuve

🇫🇷

Montpellier, France

CHU de Rennes - Hôpital Sud

🇫🇷

Rennes, France

Hôpital des Enfants

🇫🇷

Toulouse, France

CHU de Grenoble

🇫🇷

Grenoble, France

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