MedPath

Topotecan in Treating Patients With Myelodysplastic Syndrome

Phase 2
Completed
Conditions
Leukemia
Myelodysplastic Syndromes
Interventions
Registration Number
NCT00003675
Lead Sponsor
Alliance for Clinical Trials in Oncology
Brief Summary

RATIONALE: Drugs used in chemotherapy use different ways to stop cancer cells from dividing so they stop growing or die.

PURPOSE: Randomized phase II trial to study the effectiveness of topotecan in treating patients who have myelodysplastic syndrome.

Detailed Description

OBJECTIVES: I. Estimate complete or partial remission, hematologic improvement, and cytogenic response rate when oral topotecan is given twice a day for 5 days versus once a day for 10 days to patients with myelodysplastic syndromes. II. Evaluate the safety and toxicity of oral topotecan in these patients. III. Evaluate whether there are morphologic and/or cytogenetic subsets of the myelodysplastic syndromes that will respond optimally to this regimen. IV. Evaluate the change in the percentage of bone marrow blast cells in these patients during treatment. V. Evaluate the time to transformation to acute myeloid leukemia (AML) or death in this patient population.

OUTLINE: This is a randomized, multicenter study. Patients are stratified according to FAB subtype: 1. Refractory anemia with excess blasts 2. Refractory anemia with excess blasts in transformation 3. Chronic myelomonocytic leukemia 4. Refractory anemia, refractory anemia with ringed sideroblasts, and refractory cytopenia with multilineage dysplasia Patients are randomized to receive oral topotecan either twice daily for 5 days or once daily for 10 days. Courses are repeated every 21 days. Patients are evaluated for hematologic response after the initial 2 courses, and then every 4 courses. If a partial response or hematologic improvement is observed, treatment continues until disease progression to acute myeloid leukemia, relapse, death, or irreversible toxicity. Patients who achieve a complete response receive an additional 2 courses of therapy before discontinuation of protocol treatment. Patients are followed every 3 months for 2 years, then every year for an additional 3 years, and at time of progression.

PROJECTED ACCRUAL: A total of 90 patients (45 per arm) will be accrued for this study within 13 months.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
100
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Oral Topotecan 10 daystopotecan hydrochloridePatients receive intervention once daily for 10 days
Oral Topotecan 5 daystopotecan hydrochloridePatients receive intervention twice daily for 5 days
Primary Outcome Measures
NameTimeMethod
ResponseDuring treatment and up to progression post treatment

Response in the peripheral blood is assessed during tx, q 3 mon for 2 yrs post tx, then annually for another 3 years, and then at progression Bone marrow response is assessed prior to cycle 3, then q 4 cycles for the 1st yr. then q 8 cycles for patients who continue beyond

Toxicityduring treatment until progression

assessment during treatment, q 3 mon for 2 years post tx, then annually for another 3 yrs, then at progression

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (48)

Veterans Affairs Medical Center - Columbia (Truman Memorial)

🇺🇸

Columbia, Missouri, United States

University of Massachusetts Memorial Medical Center

🇺🇸

Worcester, Massachusetts, United States

CCOP - Southern Nevada Cancer Research Foundation

🇺🇸

Las Vegas, Nevada, United States

Veterans Affairs Medical Center - San Francisco

🇺🇸

San Francisco, California, United States

Veterans Affairs Medical Center - Minneapolis

🇺🇸

Minneapolis, Minnesota, United States

Duke Comprehensive Cancer Center

🇺🇸

Durham, North Carolina, United States

UCSF Cancer Center and Cancer Research Institute

🇺🇸

San Francisco, California, United States

University of Iowa Hospitals and Clinics

🇺🇸

Iowa City, Iowa, United States

University of Chicago Cancer Research Center

🇺🇸

Chicago, Illinois, United States

Ellis Fischel Cancer Center - Columbia

🇺🇸

Columbia, Missouri, United States

Veterans Affairs Medical Center - Chicago (Westside Hospital)

🇺🇸

Chicago, Illinois, United States

University of Illinois at Chicago Health Sciences Center

🇺🇸

Chicago, Illinois, United States

Marlene & Stewart Greenebaum Cancer Center, University of Maryland

🇺🇸

Baltimore, Maryland, United States

Vincent T. Lombardi Cancer Research Center, Georgetown University

🇺🇸

Washington, District of Columbia, United States

Veterans Affairs Medical Center - Buffalo

🇺🇸

Buffalo, New York, United States

Louis A. Weiss Memorial Hospital

🇺🇸

Chicago, Illinois, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Barnes-Jewish Hospital

🇺🇸

Saint Louis, Missouri, United States

New York Presbyterian Hospital - Cornell Campus

🇺🇸

New York, New York, United States

CCOP - North Shore University Hospital

🇺🇸

Manhasset, New York, United States

Roswell Park Cancer Institute

🇺🇸

Buffalo, New York, United States

Lineberger Comprehensive Cancer Center, UNC

🇺🇸

Chapel Hill, North Carolina, United States

State University of New York - Upstate Medical University

🇺🇸

Syracuse, New York, United States

Veterans Affairs Medical Center - Syracuse

🇺🇸

Syracuse, New York, United States

Mount Sinai Medical Center, NY

🇺🇸

New York, New York, United States

CCOP - Southeast Cancer Control Consortium

🇺🇸

Winston-Salem, North Carolina, United States

MBCCOP - Massey Cancer Center

🇺🇸

Richmond, Virginia, United States

CCOP - Syracuse Hematology-Oncology Associates of Central New York, P.C.

🇺🇸

Syracuse, New York, United States

Arthur G. James Cancer Hospital - Ohio State University

🇺🇸

Columbus, Ohio, United States

Comprehensive Cancer Center of Wake Forest University Baptist Medical Center

🇺🇸

Winston-Salem, North Carolina, United States

Veterans Affairs Medical Center - Durham

🇺🇸

Durham, North Carolina, United States

University of Tennessee, Memphis Cancer Center

🇺🇸

Memphis, Tennessee, United States

Veterans Affairs Medical Center - Birmingham

🇺🇸

Birmingham, Alabama, United States

Memorial Sloan-Kettering Cancer Center

🇺🇸

New York, New York, United States

University of California San Diego Cancer Center

🇺🇸

La Jolla, California, United States

CCOP - Christiana Care Health Services

🇺🇸

Wilmington, Delaware, United States

CCOP - Mount Sinai Medical Center

🇺🇸

Miami Beach, Florida, United States

Veterans Affairs Medical Center - Togus

🇺🇸

Togus, Maine, United States

University of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

Walter Reed Army Medical Center

🇺🇸

Washington, District of Columbia, United States

North Shore University Hospital

🇺🇸

Manhasset, New York, United States

Vermont Cancer Center

🇺🇸

Burlington, Vermont, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Veterans Affairs Medical Center - Memphis

🇺🇸

Memphis, Tennessee, United States

Norris Cotton Cancer Center

🇺🇸

Lebanon, New Hampshire, United States

Veterans Affairs Medical Center - White River Junction

🇺🇸

White River Junction, Vermont, United States

Veterans Affairs Medical Center - Richmond

🇺🇸

Richmond, Virginia, United States

Rhode Island Hospital

🇺🇸

Providence, Rhode Island, United States

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