MedPath

A Study of Elacestrant Versus Standard Endocrine Therapy in Women and Men With ER+,HER2-, Early Breast Cancer With High Risk of Recurrence

Registration Number
NCT06492616
Lead Sponsor
Stemline Therapeutics, Inc.
Brief Summary

The primary goal of this study is to evaluate the effectiveness of elacestrant versus standard endocrine therapy in participants with node-positive, Estrogen Receptor-positive (ER+), Human Epidermal Growth Factor-2 negative (HER2-) early breast cancer with high risk of recurrence.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
4220
Inclusion Criteria
  • Histopathologically or cytologically confirmed ER-positive (≥ 10% by immunohistochemistry [IHC]), HER2-negative [IHC = 0 or 1, or (IHC = 2 and in situ hybridization [ISH]-negative)] on tumor biopsy or final surgical pathology specimen early stage resected invasive breast cancer without evidence of recurrence or distant metastases, per local laboratory, according to the American Society of Clinical Oncology (ASCO)/College of American Pathologists (CAP) guidelines
  • Participants considered at high risk of recurrence at initial staging
  • Participants who have received at least 24 months but not more than 60 months of endocrine therapy (AIs or tamoxifen) with or without a CDK 4 and CKD 6 inhibitor (CDK4/6i)
  • Participants who received prior CDK4/6i or a poly adenosine diphosphate-ribose polymerase (PARP) inhibitor must have already completed or discontinued these treatments.

Key

Exclusion Criteria
  • Participants with inflammatory breast cancer
  • History of any prior (ipsilateral and/or contralateral) invasive breast cancer
  • Participant with history of malignancy within 3 years of the date of randomization, except for adequately treated basal or squamous cell skin cancer, superficial bladder cancer or carcinoma in situ of the cervix
  • Participants who have had more than a 6-month continuous interruption of prior SoC adjuvant endocrine therapy or who discontinued adjuvant endocrine therapy more than 6 months prior to randomization

Note: Other protocol defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Standard of Care (SoC) Endocrine TherapyLetrozoleParticipants will receive the SoC endocrine therapy that was used prior to randomization: * AI (anastrozole 1 mg QD, letrozole 2.5 mg QD, or exemestane 25 mg QD); or * Tamoxifen 20 mg QD
ElacestrantElacestrantParticipants will receive 345 milligrams (mg) elacestrant once daily (QD) for 5 years
Standard of Care (SoC) Endocrine TherapyAnastrozoleParticipants will receive the SoC endocrine therapy that was used prior to randomization: * AI (anastrozole 1 mg QD, letrozole 2.5 mg QD, or exemestane 25 mg QD); or * Tamoxifen 20 mg QD
Standard of Care (SoC) Endocrine TherapyExemestaneParticipants will receive the SoC endocrine therapy that was used prior to randomization: * AI (anastrozole 1 mg QD, letrozole 2.5 mg QD, or exemestane 25 mg QD); or * Tamoxifen 20 mg QD
Standard of Care (SoC) Endocrine TherapyTamoxifenParticipants will receive the SoC endocrine therapy that was used prior to randomization: * AI (anastrozole 1 mg QD, letrozole 2.5 mg QD, or exemestane 25 mg QD); or * Tamoxifen 20 mg QD
Primary Outcome Measures
NameTimeMethod
Invasive Breast Cancer-Free Survival (IBCFS)Up to 5 years

Assessed by the time from date of randomization to the date of first occurrence of:

* Ipsilateral invasive breast tumor recurrence

* Local/regional invasive breast cancer recurrence

* Distant recurrence

* Contralateral invasive breast cancer, or

* Death attributable to any cause

Secondary Outcome Measures
NameTimeMethod
Number of Participants With Adverse Events (AEs)Up to 5 years plus 28 days
Maximum Plasma Concentration at Steady State (Cmaxss) of ElacestrantPredose up to 4 hours postdose
Overall Survival (OS)Up to 5 years
Change from Baseline in Global Health Status Quality of Life Scale score, as Assessed by the European Organization for the Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)Baseline, Month 6, Annually at Years 1, 2, 3, 4, 5
Distant Relapse-Free Survival (DRFS)Up to 5 years

Assessed by the time from date of randomization to the date of first occurrence of:

* Distant recurrence, or

* Death attributable to any cause

Invasive Disease-Free Survival (IDFS)Up to 5 years

Assessed by the time from date of randomization to the date of first occurrence of:

* Local/regional recurrence

* Contralateral recurrence

* Second primary non-breast invasive cancer

* Distant recurrence, or

* Death attributable to any cause

Change from Baseline in the Physical Functioning Sub-Scale Score as Assessed by EORTC QLQ-C30Baseline, Month 6, Annually at Years 1, 2, 3, 4, 5
Change From Baseline in the Breast Cancer Endocrine Therapy Symptoms Sub-Scale Score, as Assessed by the EORTC Quality of Life Breast Cancer Questionnaire module (EORTC QLQ-BR42)Baseline, Month 6, Annually at Years 1, 2, 3, 4, 5
Area Under the Plasma Concentration Versus Time Curve at Steady State (AUCss) of ElacestrantPredose up to 4 hours postdose
Change From Baseline in Side Effects, as Assessed by the Question 168 of the European Organization for the Research and Treatment of Cancer Question Library (EORTC Q168)Baseline, Month 6, Annually at Years 1, 2, 3, 4, 5

Trial Locations

Locations (172)

Hospital Beata Maria Ana

🇪🇸

Madrid, Spain

Southern Cancer Center, PC

🇺🇸

Daphne, Alabama, United States

Banner MD Anderson Cancer Center

🇺🇸

Gilbert, Arizona, United States

Arizona Clinical Research Center, Inc.

🇺🇸

Tucson, Arizona, United States

Highlands Oncology Group, PA

🇺🇸

Springdale, Arkansas, United States

UC San Diego Moores Cancer Center

🇺🇸

La Jolla, California, United States

Cancer and Blood Research Center, LLC

🇺🇸

Los Alamitos, California, United States

UCLA Department of Medicine - Hematology/Oncology

🇺🇸

Los Angeles, California, United States

Hoag Memorial Hospital Presbyterian

🇺🇸

Newport Beach, California, United States

Dignity Health dba Health Research Institute

🇺🇸

Sacramento, California, United States

Sutter Institute for Medical Research

🇺🇸

Sacramento, California, United States

Helen Diller Family Comprehensive Cancer Center

🇺🇸

San Francisco, California, United States

Sansum Clinic

🇺🇸

Solvang, California, United States

St.Joseph Hospital- Cancer Centers of Colorado

🇺🇸

Denver, Colorado, United States

Rocky Mountain Cancer Centers, LLP

🇺🇸

Lone Tree, Colorado, United States

AHMG Hematology and Oncology

🇺🇸

Parker, Colorado, United States

Cancer Care at CommonSpirit St. Anthony North Hospital

🇺🇸

Westminster, Colorado, United States

Yale New Haven Hospital- Yale Cancer Center

🇺🇸

New Haven, Connecticut, United States

Florida Cancer Specialists

🇺🇸

West Palm Beach, Florida, United States

AdventHealth Orlando Infusion Center

🇺🇸

Orlando, Florida, United States

Cancer Care Centers of Brevard (CCCB) - Palm Bay

🇺🇸

Palm Bay, Florida, United States

Memorial Healthcare System

🇺🇸

Pembroke Pines, Florida, United States

University Blood & Cancer Center, LLC

🇺🇸

Athens, Georgia, United States

Northside Hospital

🇺🇸

Atlanta, Georgia, United States

Kaiser Permanente Hawaii Moanalua Medical Center

🇺🇸

Honolulu, Hawaii, United States

Illinois Cancer Specialists

🇺🇸

Arlington Heights, Illinois, United States

Northwest Cancer Centers, PC

🇺🇸

Dyer, Indiana, United States

Mission Cancer and Blood

🇺🇸

Des Moines, Iowa, United States

Cancer Center of Kansas

🇺🇸

Wichita, Kansas, United States

Mercy Medical Center

🇺🇸

Baltimore, Maryland, United States

Ascension St. Agnes Hospital

🇺🇸

Baltimore, Maryland, United States

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

🇺🇸

Baltimore, Maryland, United States

Maryland Oncology Hematology, P.A.

🇺🇸

Columbia, Maryland, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Boston Medical Center

🇺🇸

Boston, Massachusetts, United States

Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

The Cancer & Hematology Centers

🇺🇸

Grand Rapids, Michigan, United States

Allina Health Cancer Institute - Abbott Northwestern Hospital

🇺🇸

Minneapolis, Minnesota, United States

Siteman Cancer Center

🇺🇸

Saint Louis, Missouri, United States

NHO Revive Research Institute LLC

🇺🇸

Lincoln, Nebraska, United States

Oncology Hematology West, PC dba Nebraska Cancer Specialists - Legacy

🇺🇸

Omaha, Nebraska, United States

Summit Medical Group

🇺🇸

Florham Park, New Jersey, United States

John Theurer Ctr-Hackensack UMC

🇺🇸

Hackensack, New Jersey, United States

Rutgers Cancer Institute

🇺🇸

New Brunswick, New Jersey, United States

Exigent Research LLC/New Mexico Oncology Hematology Consultants Ltd.

🇺🇸

Albuquerque, New Mexico, United States

Cayuga Medical Center

🇺🇸

Ithaca, New York, United States

Laura and Isaac Perlmutter Cancer Center/NYU Langone Health

🇺🇸

New York, New York, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

Cape Fear Valley Medical Center

🇺🇸

Fayetteville, North Carolina, United States

Miami Valley Hospital South

🇺🇸

Centerville, Ohio, United States

Oncology_Hematology Care Clinical Trials, LLC

🇺🇸

Fairfield, Ohio, United States

Oregon Oncology Specialists

🇺🇸

Salem, Oregon, United States

Northwest Cancer Specialists, P.C.

🇺🇸

Tigard, Oregon, United States

Consultants In Medical Oncology and Hematology, P.C.

🇺🇸

Broomall, Pennsylvania, United States

Penn State Milton S. Hershey Medical Center

🇺🇸

Hershey, Pennsylvania, United States

Alliance Cancer Specialists, PC

🇺🇸

Media, Pennsylvania, United States

Hollings Cancer Center

🇺🇸

Charleston, South Carolina, United States

SCRI Oncology Partners

🇺🇸

Nashville, Tennessee, United States

Tennessee Oncology, PLLC

🇺🇸

Nashville, Tennessee, United States

Hendrick Cancer Center

🇺🇸

Abilene, Texas, United States

Texas Oncology - DFW

🇺🇸

Dallas, Texas, United States

The University of Texas MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Texas Oncology - San Antonio

🇺🇸

New Braunfels, Texas, United States

Mays Cancer Center

🇺🇸

San Antonio, Texas, United States

Texas Oncology- Central South

🇺🇸

Weslaco, Texas, United States

Virginia Oncology Associates

🇺🇸

Newport News, Virginia, United States

Virginia Cancer Institute

🇺🇸

Richmond, Virginia, United States

Oncology & Hematology Associates of Southwest Virginia, Inc

🇺🇸

Wytheville, Virginia, United States

Virginia Mason Medical Center

🇺🇸

Seattle, Washington, United States

Cancer Care Northwest

🇺🇸

Spokane Valley, Washington, United States

Northwest Medical Specialties PLLC

🇺🇸

Tacoma, Washington, United States

University of Wisconsin Carbone Cancer Center- University Hospital

🇺🇸

Madison, Wisconsin, United States

UW Cancer Center at ProHealth Care

🇺🇸

Waukesha, Wisconsin, United States

St Vincent's Hospital Sydney

🇦🇺

Darlinghurst, New South Wales, Australia

Lake Macquarie Private Hospital - Oncology

🇦🇺

Gateshead, New South Wales, Australia

Mater Hospital Sydney

🇦🇺

North Sydney, New South Wales, Australia

Westmead Hospital

🇦🇺

Westmead, New South Wales, Australia

Icon Cancer Centre Townsville

🇦🇺

Hyde Park, Queensland, Australia

Icon Cancer Centre Southport

🇦🇺

Southport, Queensland, Australia

Icon Cancer Centre Wesley

🇦🇺

Auchenflower, Quuensland, Australia

Icon Cancer Centre Kurralta Park

🇦🇺

Kurralta Park, South Australia, Australia

Goulburn Valley Health

🇦🇺

Shepparton, Victoria, Australia

Breast Cancer Research Centre

🇦🇺

Nedlands, Western Australia, Australia

Icon Cancer Centre Hobart

🇦🇺

Hobart, Australia

Mid North Coast Cancer Institute

🇦🇺

Port Macquarie, Australia

Hanusch Krankenhaus

🇦🇹

Wien, Austria

Jewish General Hospital

🇨🇦

Montreal, Quebec, Canada

Regional Hospital Saint-Jerome

🇨🇦

Saint-Jerome, Quebec, Canada

FN Kralovske Vinohrady - Radioterapeuticka a onkologicka klinika

🇨🇿

Praha 10, Czechia

Centre Hospitalier Regional et Universitaire (CHRU) de Besancon - L'Hopital Jean Minjoz

🇫🇷

Besancon, Alpes-Maritimes, France

Institut de Cancerologie de l'Ouest - Oncology

🇫🇷

St. Herblain, Loire-Atlantique, France

Institut Gustave Roussy

🇫🇷

Villejuif, Val-de-Marne, France

Centre Hospitalier Universitaire De Poitiers - Pôle Régional de Cancérologie

🇫🇷

Poitiers, France

Institut de Cancérologie de Lorraine

🇫🇷

Vandœuvre-Lès-Nancy Cedex 03, France

Universitätsmedizin Mannheim (UMM)

🇩🇪

Mannheim, Baden-Württemberg, Germany

'Klinikum Esslingen GmbH

🇩🇪

Esslingen am Neckar, Esslingen a.N., Germany

'Schwerpunktpraxis Fuer Gynaekologie und Onkologie

🇩🇪

Brandenburg, Fuerstenwalde /Spree, Germany

Klinikum Worms gGmbH

🇩🇪

Worms, Rheinland-Pfalz, Germany

Bacs-Kiskun Varmegyei Oktatakorhaz

🇭🇺

Kecskemét, Bács-Kiskun, Hungary

Debreceni Egyetem Klinikai Kozpont

🇭🇺

Debrecen, Hajdú-Bihar, Hungary

Nograd Varmegyei Szent Lazar Korhaz

🇭🇺

Salgótarján, Szabolcs-Szatmár-Bereg, Hungary

Budapesti Uzsoki Utcai Korhaz

🇭🇺

Budapest, Hungary

IRST Dino Amadori IRCCS

🇮🇹

Meldola, Forli-Cesena, Italy

IRCCS San Gerardo dei Tintori

🇮🇹

Monza, Monza E Brianza, Italy

Centro di Riferimento Oncologico, IRCCS

🇮🇹

Aviano, Pordenone, Italy

Ospedale Casa Sollievo della Sofferen IRCCS, Opera di San Pio da Pietrelcina

🇮🇹

San Giovanni Rotondo, Puglia, Italy

Istituto Europeo di Oncologia IRCCS

🇮🇹

Milano, Italy

Azienda USL Toscana Centro

🇮🇹

Prato, Italy

Irccs Crob

🇮🇹

Rionero In Vulture, Italy

U.O. Ginecologia Oncologica - Fondazione Policlinico A. Gemelli

🇮🇹

Roma, Italy

IRCCS Istituto Nazionale Tumori Regina Elena,UOSD Sperimentazioni di fase IV

🇮🇹

Roma, Italy

Ospedale Sacro cuore Don Calabria- Negrar di Valpolicella

🇮🇹

Verona, Italy

Chungbuk National University Hospital

🇰🇷

Cheongju-si, Chungcheongbugdo [Ch'ungch'ongbuk-do], Korea, Republic of

Hospital CUF Descobertas

🇵🇹

Lisboa, Portugal

CHA Bundang Medical Center, CHA University

🇰🇷

Seongnam-si, Gyeonggido, Korea, Republic of

Gachon University Gil Medical Center

🇰🇷

Incheon, Incheon Gwang'yeogsi [Inch'n-Kwangyokshi], Korea, Republic of

Severance Hospital, Yonsei University Health System

🇰🇷

Seoul, Seoul Teugbyeolsi [Seoul-T'ukpyolshi], Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Seoul Teugbyeolsi [Seoul-T'ukpyolshi], Korea, Republic of

Gangnam Severance Hospital - Oncology

🇰🇷

Seoul, Seoul Teugbyeolsi [Seoul-T'ukpyolshi], Korea, Republic of

Korea University Guro Hospital

🇰🇷

Seoul, Seoul Teugbyeolsi [Seoul-T'ukpyolshi], Korea, Republic of

Korea University Anam Hospital

🇰🇷

Seoul, Seoul Teugbyeolsi [Seoul-T'ukpyolshi], Korea, Republic of

Ewha Womans University Mokdong Hospital

🇰🇷

Seoul, Seoul Teugbyeolsi [Seoul-T'ukpyolshi], Korea, Republic of

Inje University Haeundae Paik Hospital

🇰🇷

Busan, Korea, Republic of

National Cancer Center

🇰🇷

Gyeonggi-do, Korea, Republic of

Ajou University Hospital

🇰🇷

Gyeonggi-do, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

The Catholic University of Korea, Seoul St. Mary's Hospital

🇰🇷

Seoul, Korea, Republic of

Ulsan University Hospital

🇰🇷

Ulsan, Korea, Republic of

Hospital Pulau Pinang - Rheumatology

🇲🇾

George Town, Pulau Pinang, Malaysia

Pantai Hospital Kuala Lumpur

🇲🇾

Kuala Lumpur, Wilayah Persekutuan Kuala Lumpur, Malaysia

Oncolab - Medical Oncology

🇷🇴

Craiova, Dolj, Romania

UKM Medical Centre

🇲🇾

Kuala Lumpur, Wilayah Persekutuan Kuala Lumpur, Malaysia

Beacon Hospital

🇲🇾

Kuala Lumpur, Wilayah Persekutuan Kuala Lumpur, Malaysia

Universiti Malaya Medical Centre

🇲🇾

Kuala Lumpur, Wilayah Persekutuan, Malaysia

Institut Kanser Negara

🇲🇾

Putrajaya, Wilayah Persekutuan, Malaysia

Hospital Sultan Ismail

🇲🇾

Johor Bahru, Malaysia

Hospital Kuala Lumpur

🇲🇾

Kuala Lumpur, Malaysia

Mahkota Medical Center

🇲🇾

Melaka, Malaysia

Elisabeth-TweeSteden Ziekenhuis

🇳🇱

Tilburg, Noord-Brabant, Netherlands

Catharina Ziekenhuis

🇳🇱

Eindhoven, Netherlands

IP Clinic Sp. z o.o.

🇵🇱

Łódź, Lodz, Poland

Hospital Beatriz Ângelo. Hospital de Loures - Oncologia Medica

🇵🇹

Loures, Lisboa, Portugal

Centrul de Oncologie Sf. Nectarie

🇷🇴

Craiova, Dolj, Romania

Spitalul Clinic Filantropia

🇷🇴

Bucuresti, Romania

Spitalul Clinic CF Nr 2 Bucuresti

🇷🇴

Bucuresti, Romania

Memorial Healthcare International

🇷🇴

Bucuresti, Romania

Radiotherapy Center Cluj

🇷🇴

Floreşti, Romania

Raffles Hospital

🇸🇬

Singapore, Singapore

Hospital Alvaro Cunqueiro

🇪🇸

Vigo, A Coruña, Spain

Hospital Universitario de Canarias

🇪🇸

San Cristobal de la Laguna, Canarias, Spain

Hospital Universitario Virgen del Rocío

🇪🇸

Sevilla, Andalucia, Spain

H. Virgen de Valme

🇪🇸

Sevilla, Andalucia, Spain

Complexo Hospitalario Universitario A Coruña

🇪🇸

A Coruña, Spain

Hospital Clínico Universitario Virgen De La Arrixaca

🇪🇸

El Palmar, Murcia, Spain

Hospital Universitari Vall D Hebron

🇪🇸

Barcelona, Spain

Hospital Universitario Reina Sofia

🇪🇸

Córdoba, Spain

Hospital de La Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

H.U. Insular Gran Canaria

🇪🇸

Las Palmas De Gran Canaria, Spain

H.U Arnau De Vilanova Lleida

🇪🇸

Lleida, Spain

Hospital Universitario La Paz

🇪🇸

Madrid, Spain

Hospital Universitario Ramón y Cajal

🇪🇸

Madrid, Spain

Hospital Clínico San Carlos

🇪🇸

Madrid, Spain

Hospital Universitario 12 de Octubre

🇪🇸

Madrid, Spain

Hospital Universitario Virgen De La Victoria

🇪🇸

Málaga, Spain

Hospital Universitario de Santiago

🇪🇸

Santiago De Compostela, Spain

Hospital Clinico Universitario De Valencia

🇪🇸

Valencia, Spain

Hospital Quironsalud Valencia

🇪🇸

Valencia, Spain

Tumor Zentrum Aarau

🇨🇭

Aarau, Aargau (de), Switzerland

Brust-Zentrum AG Zurich

🇨🇭

Zürich, Zürich (de), Switzerland

Spitaeler Schaffhausen Kantonspital

🇨🇭

Schaffhausen, Switzerland

Changhua Christian Medical Foundation Changhua Christian Hospital

🇨🇳

Changhua City, Taiwan

Maidstone Hospital Kent Oncology Centre

🇬🇧

Maidstone, United Kingdom

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