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A Trial of TTA-121 on Autism Spectrum Disorder

Phase 2
Conditions
Autism Spectrum Disorder
Interventions
Registration Number
NCT03466671
Lead Sponsor
Hamamatsu University
Brief Summary

To test efficacy and safety of a novel nasal spray of oxytocin on social deifies in autism spectrum disorder, and To compare effect sizes of different doses

Detailed Description

Not available

Recruitment & Eligibility

Status
UNKNOWN
Sex
Male
Target Recruitment
144
Inclusion Criteria
  1. Diagnosis of autism spectrum disorder based on Diagnostic and Statistical Manual of Mental Disorders-V with score exceeding the cut-off value of 10 for qualitative abnormalities in social reciprocity on Autism Diagnostic Interview Revised (ADIR)
  2. Full scale Intelligent quotient above 80 as measured using the Wechsler Adult Intelligent Scale-III
  3. Written informed consent for participating the trial
Exclusion Criteria
  1. Diagnosis of bipolar disorder or schizophrenia spectrum disorder
  2. Primary diagnosis of depressive disorders, obsessive-compulsive and related disorders, anxiety disorders, trauma- and stressor-related disorders, dissociative disorders, somatic symptom and related disorders, or neurodevelopmental disorders other than autism spectr um disorder
  3. Instability in symptoms of comorbid mental disorders such as depressive disorders or anxiety disorders
  4. History of changes in medication or doses of psychotropics within one month before registration
  5. Current treatment with more than one psychotropics
  6. History of hyper-sensitivity to oxytocin
  7. History of seizures or traumatic brain injury with loss of consciousness for longer than 5 minutes
  8. History of alcohol-related disorders, substance abuse, or addiction
  9. Family history of male breast cancer
  10. Subject who has severe complications
  11. Known hypersensitivity to some drugs and foods
  12. Subject who is not able to consent contraception during study period
  13. Participation in another registration clinical trial and administration of investigational drug during 120 days before informed consent
  14. Other Subjects whom a lead investigator or the patient's primary physician deems are not appropriate for this study

Study & Design

Study Type
INTERVENTIONAL
Study Design
CROSSOVER
Arm && Interventions
GroupInterventionDescription
Placebo and high dose twice per dayTTA-121Four weeks administrations of placebo twice per day in morning and evening. After four weeks washout, four weeks administrations of TTA-121 10U twice per day in morning and evening.
High dose once per day and placeboTTA-121Four weeks administrations of TTA-121 10U once per day in morning and placebo once per day in evening. After four weeks washout, four weeks administrations of placebo twice per day in morning and evening.
Low dose once per day and placeboTTA-121Four weeks administrations of TTA-121 3U once per day in morning and placebo once per day in evening. After four weeks washout, four weeks administrations of placebo twice per day in morning and evening.
Low dose twice per day and placeboTTA-121Four weeks administrations of TTA-121 3U twice per day in morning and evening. After four weeks washout, four weeks administrations of placebo twice per day in morning and evening.
Placebo and low dose once per dayTTA-121Four weeks administrations of placebo twice per day in morning and evening. After four weeks washout, four weeks administrations of TTA-121 3U once per day in morning and placebo once per day in evening.
Placebo and high dose once per dayTTA-121Four weeks administrations of placebo twice per day in morning and evening. After four weeks washout, four weeks administrations of TTA-121 10U once per day in morning and placebo once per day in evening.
Placebo and low dose twice per dayTTA-121Four weeks administrations of placebo twice per day in morning and evening. After four weeks washout, four weeks administrations of TTA-121 3U twice per day in morning and evening.
High dose twice per day and placeboTTA-121Four weeks administrations of TTA-121 10U twice per day in morning and evening. After four weeks washout, four weeks administrations of placebo twice per day in morning and evening.
Primary Outcome Measures
NameTimeMethod
Efficacy on autism spectrum social core symptom assessed by social reciprocity score on the Autism Diagnostic Observation Schedule module 4At baseline, which was before and on the same day as the first administration, and at endpoint, which was started approximately 15 min after the last drug administration

Changes in social reciprocity score (range: 0-14, Higher value represent a worth outcome) on Autism Diagnostic Observation Schedule module 4 between baseline and endpoint of each administration period

Secondary Outcome Measures
NameTimeMethod
Efficacy on autism spectrum core symptom assessed by communication score on the Autism Diagnostic Observation Schedule module 4At baseline, which was before and on the same day as the first administration, and at endpoint, which was started approximately 15 min after the last drug administration

Changes in communication score (range: 0-8, Higher value represent a worth outcome) on Autism Diagnostic Observation Schedule module 4 between baseline and endpoint of each administration period

Efficacy assessed by Global Assessment of FunctioningAt baseline, which was before and on the same day as the first administration, and at endpoint, which was assessed within 100 min after the last drug administration

Changes in Global Assessment of Functioning (range: 1-100, Higher value represent a better outcome) between baseline and endpoint of each administration period

Efficacy assessed by Clinical Global Impression-SeverityAt baseline, which was before and on the same day as the first administration, and at endpoint, which was assessed within 100 min after the last drug administration

Changes in Clinical Global Impression-Severity (range: 1-7, Higher value represent a worse outcome) between baseline and endpoint of each administration period

Efficacy on autism spectrum core symptom assessed by revised algorithm score of social affect on the Autism Diagnostic Observation Schedule module 4At baseline, which was before and on the same day as the first administration, and at endpoint, which was started approximately 15 min after the last drug administration

Changes in revised algorithm score of social affect (range: 0-20, Higher value represent a worth outcome) on Autism Diagnostic Observation Schedule module 4 between baseline and endpoint of each administration period

Efficacy on autism spectrum core symptom assessed by revised algorithm of repetitive and restricted behavior score on the Autism Diagnostic Observation Schedule module 4At baseline, which was before and on the same day as the first administration, and at endpoint, which was started approximately 15 min after the last drug administration

Changes in revised algorithm of repetitive and restricted behavior score (range: 0-10, Higher value represent a worth outcome) on Autism Diagnostic Observation Schedule module 4 between baseline and endpoint of each administration period

Efficacy assessed by Clinical Global Impression-ImprovementAt baseline, which was before and on the same day as the first administration, and at endpoint, which was assessed within 100 min after the last drug administration

Changes in Clinical Global Impression-Improvement (range: 1-7, Higher value represent a worse outcome) between baseline and endpoint of each administration period

Efficacy on autism spectrum core symptom assessed by repetitive and restricted behavior score on the Autism Diagnostic Observation Schedule module 4At baseline, which was before and on the same day as the first administration, and at endpoint, which was started approximately 15 min after the last drug administration

Changes in repetitive and restricted behavior score (range: 0-10, Higher value represent a worth outcome) on Autism Diagnostic Observation Schedule module 4 between baseline and endpoint of each administration period

Efficacy assessed by quantitative analysis of facial expressionAt baseline, which was before and on the same day as the first administration, and at endpoint, which was started approximately 15 min after the last drug administration

Changes in quantitative measure of facial expression on videos recorded during ADOS administration between baseline and endpoint of each administration period

Efficacy assessed by gaze fixation time on social regionAt baseline, which was before and on the same day as the first administration, and at endpoint, which was started approximately 60 min after the last drug administration

Changes in gaze fixation time on social region during being talked between baseline and endpoint of each administration period

Trial Locations

Locations (1)

Hamamatsu University School of Medicine

🇯🇵

Hamamatsu, Shizuoka, Japan

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