MedPath

Study Evaluating Neratinib Plus Paclitaxel VS Trastuzumab Plus Paclitaxel In ErbB-2 Positive Advanced Breast Cancer

Phase 2
Completed
Conditions
Breast Cancer
Interventions
Registration Number
NCT00915018
Lead Sponsor
Puma Biotechnology, Inc.
Brief Summary

This study is investigating the effects of an experimental drug (neratinib) in combination with paclitaxel versus trastuzumab in combination with paclitaxel for the treatment of women who have not received previous treatment for erbB-2-positive locally recurrent or metastatic breast cancer. The study will compare the effectiveness of each regimen in shrinking tumors and extending the lives of women with erbB-2 (HER2) positive breast cancer. The study will also compare the safety of the two regimens and as well as the quality of life of subjects receiving either regimen.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
479
Inclusion Criteria
  • ErbB-2 positive locally recurrent or metastatic breast cancer
  • Eastern Cooperative Oncology Group (ECOG) 0-2
  • Measurable disease
  • Availability of tumor tissue for HER2 status confirmation
Exclusion Criteria
  • Prior systemic anti-cancer therapy other than endocrine therapy for locally recurrent or metastatic disease
  • Prior erbB-2 inhibitor other than trastuzumab or lapatinib in the neoadjuvant or adjuvant setting
  • Progression/recurrence within 12 months after completion of adjuvant or neoadjuvant therapy
  • History of heart disease
  • History of gastrointestinal disease

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
neratinib plus paclitaxelNeratinib-
trastuzumab plus paclitaxelTrastuzumab-
neratinib plus paclitaxelPaclitaxel-
trastuzumab plus paclitaxelPaclitaxel-
Primary Outcome Measures
NameTimeMethod
Progression-Free SurvivalFrom randomization to disease progression or death, assessed up to 5.3 years

Defined as the interval from the date of randomization until the first date on which recurrence or progression, or death due to any cause, is documented, censored at the last assessable evaluation or at the initiation of new anticancer therapy.

Secondary Outcome Measures
NameTimeMethod
Objective Response RateFrom randomization to disease progression or last tumor assessment, assessed up to 5.3 years

Defined as the percentage of subjects who achieved confirmed tumor response (complete or partial response) per Response Evaluation Criteria In Solid Tumors Criteria (RECIST) v1.0: Complete Response (CR), disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; and Non-Progressive Disease for non-target lesions, and no new lesions.

Duration of ResponseFrom first response to first PD or death, assessed up to 5.3 years after first subject randomized

Measured from the time at which measurement criteria were first met for CR or PR (whichever status was recorded first), until the date of first recurrence, disease progression (PD), or death was objectively documented, taking as a reference for PD the smallest measurements recorded since enrollment, per Response Evaluation Criteria In Solid Tumors Criteria (RECIST) v1.0: Complete Response (CR), disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; and Non-PD for non-target lesions, and no new lesions.

Clinical Benefit RateFrom randomization to disease progression or death, assessed up to 5.3 years

Defined as the proportion of patients who achieved overall tumor response (CR or PR) or SD for at least 24 weeks per Response Evaluation Criteria In Solid Tumors Criteria (RECIST) v1.0: Complete Response (CR), disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; and Non-PD for non-target lesions, and no new lesions; Stable Disease (SD), Neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for PD, taking as reference the smallest sum diameters while on study.

Symptomatic or Progressive Central Nervous System (CNS) LesionsFrom randomization to disease progression PD or last tumor assessment, assessed up to 5.3 years

Defined as the time interval from the date of randomization until the first date of CNS symptoms, the imaging examination shows CNS progression or is censored at the last assessable evaluation on study or prior to new anti-cancer therapy, if applicable.

If median time to Symptomatic or Progressive CNS Lesions is not estimable, cumulative incidence will be reported instead.

Trial Locations

Locations (194)

Service d'Oncologie et de Radiotherapie, Polyclinique Francheville

🇫🇷

Perigueux, France

Institutul Oncologic Prof. Dr. Ion Chiricuţă

🇷🇴

Cluj-Napoca, Cluj, Romania

Hospital Universitario Fundación Alcorcón

🇪🇸

Alcorcon, Madrid, Spain

Meenakshi Mission Hospital and Research Centre

🇮🇳

Madurai, Tamil Nadu, India

Institution of Healthcare Grodno Regional Clinical Hospital

🇧🇾

Grodno, Belarus

Hopital Charles, LeMoyne Le Centre Intégré de Cancérologie de la Montérégie

🇨🇦

Greenfield Park, Quebec, Canada

National Hospital Organization Hokkaido Cancer Center

🇯🇵

Hokkaido, Sapporo-shi, Japan

Tohoku University Hospital

🇯🇵

Miyagi, Sendai-city, Japan

National Institute of Cancer Department of Conseravtive Methods of Treatment

🇺🇦

Kyiv, Ukraine

Assaf Harofeh Medical Center

🇮🇱

Zerifin, Israel

Tokyo Metropolitan Cancer and Infectious Disease Center, Komagome Hospital

🇯🇵

Tokyo, Bunkyo-ku, Japan

National Hospital Organization Kyushu Cancer Center

🇯🇵

Fukuoka, Fukuoka-shi, Japan

Tenessee Cancer Specialists

🇺🇸

Knoxville, Tennessee, United States

Medical University of South Carolina Hollings Cancer Center

🇺🇸

Charleston, South Carolina, United States

Healthcare Institution Vitebsk Regional Clinical Oncology Dispensary

🇧🇾

Vitebsk, Belarus

Queen Mary Hospital

🇭🇰

Hong Kong, Hong Kong

Kumamoto Municipal Hospital

🇯🇵

Kumamoto, Kumamoto-city, Japan

Niigata Cancer Center Hospital

🇯🇵

Niigata, Niigata-shi, Japan

CHRISTUS St. Frances Cabrini Hospital

🇺🇸

Alexandria, Louisiana, United States

Jawaharlal Nehru Cancer Hospital

🇮🇳

Bhopal, Madhya Pradesh, India

Fovarosi Onkormanyzat Szent Imre Korhaz Klinikai Onkologiai Profil

🇭🇺

Budapest, Hungary

UNIMED Medical Institute, Comprehensive Centre for Breast Diseases

🇭🇰

Wanchai, Hong Kong

National Hospital Organization Shikoku Cancer Center

🇯🇵

Ehime, Matsuyama-city, Japan

Tazuke Kofukai Medical Research Institute Kitano Hospital

🇯🇵

Osaka, Japan

Zakład Opieki Zdrowotnej MSW z Warmińsko, Mazurskim Centrum Onkologii

🇵🇱

Olsztyn, Warminsko-Mazurskie, Poland

Royal Melbourne Hospital

🇦🇺

Parkville, Victoria, Australia

District Dispensary for Oncology Diseases Internal Unit- Sofia EOOD

🇧🇬

Sofia, Bulgaria

National Hospital Organization Mito Medical Center

🇯🇵

Ibaraki, Higashiibaraki-gun, Japan

Aichi Cancer Center

🇯🇵

Aichi, Nagoya-shi, Japan

Kumamoto University Hospital

🇯🇵

Kumamoto, Japan

City Multifield Clinical Hospital

🇺🇦

Dnipropetrovsk, Ukraine

State Oncological Regional Treatment and Diagnostic Center

🇺🇦

Lviv, Ukraine

Hematology Oncology Services

🇺🇸

Metairie, Louisiana, United States

Santee Hematology Oncology

🇺🇸

Sumter, South Carolina, United States

National Hospital Organization Osaka National Hospital

🇯🇵

Osaka, Osaka-shi, Japan

Shinko Hospital

🇯🇵

Hyogo, Japan

Piejuras Hospital, Liepajas Oncological Clinic

🇱🇻

Liepaja, Latvia

Chang Gung Medical Foundation, Linkou Branch

🇨🇳

Taoyuan, Taiwan

Kanagawa Cancer Center

🇯🇵

Kanagawa, Yokohama-City, Japan

National Hospital Organization Tokyo Medical Center

🇯🇵

Tokyo, Japan

Institute of Oncology and Radiology of Serbia

🇷🇸

Belgrade, Serbia

Tianjin Cancer Hospital

🇨🇳

Tian Jin, China

Cancer Center of Central Connecticut

🇺🇸

Plainville, Connecticut, United States

Broward General Medical Center

🇺🇸

Fort Lauderdale, Florida, United States

Hematology Oncology Associates of Treasure Coast

🇺🇸

Port Saint Lucie, Florida, United States

Samaritan Hematology and Oncology Consultants

🇺🇸

Corvallis, Oregon, United States

Pawtucket Memorial Hospital

🇺🇸

Pawtucket, Rhode Island, United States

Warren Cancer Research Foundation

🇺🇸

Tulsa, Oklahoma, United States

Institution Gomel Regional Clinical Oncology Dispensary

🇧🇾

Gomel, Belarus

Specialised Hospital of ActiveTreatment in Oncology, Clinic of Chemotherapy

🇧🇬

Sofia, Bulgaria

Texas Oncology

🇺🇸

Bedford, Texas, United States

Centre Hospitalier Régional de Trois-Rivières

🇨🇦

Trois-Rivieres, Quebec, Canada

Charleston Area Medical Center, Health, Education, and Research Institute

🇺🇸

Charleston, West Virginia, United States

Affinity Research Limited

🇧🇸

Nassau, CB, Bahamas

N.N. Aleksandrov National Cancer Center of Belarus

🇧🇾

Lesnoy, Minsk Region, Belarus

Institut Jules Bordet

🇧🇪

Brussels, Belgium

District Dispensary for Oncology Diseases Internal Unit- Plovdiv EOOD

🇧🇬

Plovdiv, Bulgaria

Chinese People's Liberation Army General Hospital

🇨🇳

Beijing, China

Sun Yat-Sen University Cancer Center

🇨🇳

Guangzhou, Guangdong, China

Zhejiang Cancer Hospital

🇨🇳

Hangzhou, Zhejiang, China

Southern Medical University Nanfang Hospital

🇨🇳

Guangzhou, Guangdong, China

Cancer Hospital, Chinese Academy of Medical Sciences

🇨🇳

Beijing, China

The Hospital Affiliated Academy Military Medical Science, Chinese People's Liberation Army

🇨🇳

Beijing, China

Clinical Hospital Osijek, Department of Radiotherapy and Oncology

🇭🇷

Osijek, Croatia

Centre Leon Berard Departement de Cancerologie Medicale

🇫🇷

Lyon, France

Szegedi Tudomanyegyetem Onkoterapias Klinika

🇭🇺

Szeged, Hungary

Semmelweis Egyetem Radiologiai és Onkoterapias Klinika

🇭🇺

Budapest, Hungary

Sozialstiftung Bamberg Klinik fuer Haematologie und internistische Onkologie

🇩🇪

Bamberg, Germany

Hopital La Pitie-Salpetriere

🇫🇷

Paris, France

Fudan University Shanghai Cancer Center

🇨🇳

Shanghai, China

Groupe Hospitalier Paris Saint Joseph, Oncologie medicale

🇫🇷

Paris, France

University Hospital For Tumors

🇭🇷

Zagreb, Croatia

Centre Val d'Aurelle

🇫🇷

Montpellier, France

Rigshospitalet, Copenhagen, Onkologisk Klinik

🇩🇰

Copenhagen, Denmark

Pamela Youde Nethersole Eastern Hospital

🇭🇰

Chai Wan, Hong Kong

Hopital Hotel Dieu, Service d'Oncologie Medicale, Bat B2, 5ieme

🇫🇷

Paris, France

Clinique Armoricaine de Radiologie

🇫🇷

St. Brieuc, France

Central India Cancer Research Institute

🇮🇳

Nagpur, Maharashtra, India

Tata Memorial Centre

🇮🇳

Mumbai, Maharashtra, India

Curie Manavata Cancer Centre

🇮🇳

Nashik, Maharashtra, India

Kaposi Mor Oktato Korhoz Onkologiai Centrum

🇭🇺

Kaposvar, Hungary

Bacs-Kiskun Megyei Onkormanyzat Korhaza Onkoradiologiai Kozpont

🇭🇺

Kecskemet, Hungary

Sourasky Medical Center

🇮🇱

Tel Aviv, Israel

Borsod-Abaúj-Zemplén Megyei Kórház és Egyetemi Oktató Kórház

🇭🇺

Miskolc, Hungary

Orszagos Onkologiai Intezet "B" Belgyogyaszati osztaly

🇭🇺

Budapest, Hungary

Searoc Cancer Center

🇮🇳

Jaipur, Rajasthan, India

Institute Rotary Cancer Hospital, AIIMS

🇮🇳

New Delhi, Delhi, India

Deenanath Mangeshkar Hospital and Research Centre

🇮🇳

Pune, Maharashtra, India

Chiba Cancer Center

🇯🇵

Chiba, Chiba-shi, Japan

Policlinico di Modena Oncologia ed Ematologia

🇮🇹

Modena, Italy

Fondazione Salvatore Maugeri

🇮🇹

Pavia, Italy

Ospedale San Giovanni Battista-Molinette

🇮🇹

Torino, Italy

Hyogo Cancer Center

🇯🇵

Hyogo, Akashi-shi, Japan

Hakuaikai Medical Corporation Sagara Hospital

🇯🇵

Kagoshima, Kagoshima-city, Japan

National Cancer Center Hospital East

🇯🇵

Chiba, Kashiwa-shi, Japan

Saitama Cancer Center

🇯🇵

Saitama, Kitaadachi-gun, Japan

National Hospital Organization Nagoya Medical Center

🇯🇵

Aichi, Nagoya, Japan

Hiroshima University Hospital

🇯🇵

Hiroshima, Hiroshima-shi, Japan

Kurume Daiichi Social Insurance Hospital

🇯🇵

Fukuoka, Kurume-Shi, Japan

Osaka Medical Center for Cancer and Cardiovascular Diseases

🇯🇵

Osaka, Osaka-shi, Japan

Tenri Hospital

🇯🇵

Nara, Tenri-shi, Japan

Hiroshima City Hospital

🇯🇵

Hiroshima, Japan

National Hospital Organization Kure Medical Center and Chugoku Cancer Center

🇯🇵

Hiroshima, Japan

Asan Medical Center

🇰🇷

Seoul, Korea, Korea, Republic of

Nacionalinis Vezio Institutas, Vilniaus Universiteto Onkologijos Institutas

🇱🇹

Vilnius, Lithuania

Pauls Stradiņš Clinical University Hospital

🇱🇻

Riga, Latvia

National University Hospital, National Cancer Institute

🇸🇬

Singapore, Singapore

Korea University Guro Hospital

🇰🇷

Seoul, Korea, Korea, Republic of

Hospital of Lithuanian University of Health sciences

🇱🇹

Kaunas, Lithuania

Riga Eastern University Hospital

🇱🇻

Riga, Latvia

Sir Anthony Oncology Center

🇲🇹

Floriana, Malta

Samodzielny Publiczny Zaklad Opieki Zdrowotnej Szpital Wojewodzki Oddzial

🇵🇱

Jelenia Gora, Dolnoslaskie, Poland

Magodent

🇵🇱

Warszawa, Mazowieckie, Poland

Opolskie Centrum Onkologii

🇵🇱

Opole, Opolskie, Poland

Clinical centre Nis Clinic of Oncology

🇷🇸

Nis, Serbia

Sandton Oncology Centre

🇿🇦

Johannesburg, Gauteng, South Africa

Westridge Medical Centre

🇿🇦

Durban, KwaZulu Natal, South Africa

Białostockie Centrum Onkologii

🇵🇱

Bialystok, Poland

Hospital da Luz Servico de Oncologia Medica

🇵🇹

Lisboa, Portugal

SC Oncolab S.R.L.

🇷🇴

Craiova, Dolj, Romania

Spitalul Universitar de Urgenta Bucuresti

🇷🇴

Bucuresti, Romania

National Cancer Centre Singapore

🇸🇬

Singapore, Singapore

GVI Oncology

🇿🇦

Kraaifontein, Western Cape, South Africa

Hospital Universitari Arnau de Vilanova

🇪🇸

Lleida, Cataluna, Spain

Spital STS AG Onkologiezentrum Thun - Berner Oberland

🇨🇭

Thun, Switzerland

Kantonsspital Winterthur Medizinische Onkologie

🇨🇭

Winterthur, Switzerland

Komunalnyy Zaklad Cherkasskyy Oblasnyy Onkologichnyy Dyspanser

🇺🇦

Cherkassy, Ukraine

Centro Oncologico MD Anderson

🇪🇸

Madrid, Spain

Hospital Universitario 12 de Octubre

🇪🇸

Madrid, Spain

Ege Universitesi Tip Fakultesi Tulay Aktas Onkoloji Hastanesi

🇹🇷

Bornova, Izmir, Turkey

Donetsk Regional Antitumor Center Department of Pretumor Diseases and Tumor Treatment

🇺🇦

Donetsk, Ukraine

Chernivtsi Regional Oncology Centre Outpatient Department Bukovynian State Medical University Department of Oncology and Radiology

🇺🇦

Chernivtsi, Ukraine

Mariupil Oncological Center

🇺🇦

Mariupil, Ukraine

Guy's and St Thomas NHS Foundation Trust Management Offices 4th Floor Bermondsey Wing Guy's Hospital

🇬🇧

London, United Kingdom

Sumy Regional Clinical Oncology Centre

🇺🇦

Sumy, Ukraine

Hôpital Henri-Mondor

🇫🇷

Creteil, France

Centre de Radiothérapie, Clinique Sainte Anne, Service d'Oncologie Libérale

🇫🇷

Strasbourg, France

CHU Strasbourg Departement Oncologie & Hematologie Hopital Civil

🇫🇷

Strasbourg, France

Hospital Son Llàtzer

🇪🇸

Palma, Illes Balears, Spain

Complejo Hospitalario Universitario Santiago de Compostela

🇪🇸

Santiago de Compostela, Galicia, Spain

Florida Cancer Research Institute

🇺🇸

Plantation, Florida, United States

Mid Florida Cancer Centers

🇺🇸

Orange City, Florida, United States

Park Nicollet Institute

🇺🇸

Saint Louis Park, Minnesota, United States

Missouri Cancer Associates

🇺🇸

Columbia, Missouri, United States

St. John's Medical Research Institute

🇺🇸

Springfield, Missouri, United States

Ventura County Hematology-Oncology Specialists

🇺🇸

Oxnard, California, United States

North Broward Medical Center Cancer Center

🇺🇸

Deerfield Beach, Florida, United States

Palm Beach Institute of Hematology and Oncology

🇺🇸

Boynton Beach, Florida, United States

Dublin Hematology and Oncology Care

🇺🇸

Dublin, Georgia, United States

Phoebe Cancer Center

🇺🇸

Albany, Georgia, United States

Clintell

🇺🇸

Skokie, Illinois, United States

Presence Hematology and Oncology

🇺🇸

Skokie, Illinois, United States

Springfield Clinic

🇺🇸

Springfield, Illinois, United States

Washington University School of Medicine Siteman Cancer Center

🇺🇸

Saint Louis, Missouri, United States

The Valley Hospital, Luckow Pavilion Office of Oncology Clinical Trials

🇺🇸

Paramus, New Jersey, United States

Summa Health System Hospitals

🇺🇸

Akron, Ohio, United States

Gaston Hematology and Oncology Associates

🇺🇸

Gastonia, North Carolina, United States

Utah Cancer Specialists

🇺🇸

Salt Lake City, Utah, United States

Texas Oncology-Allison Cancer Center

🇺🇸

Midland, Texas, United States

Southlake Oncology

🇺🇸

Southlake, Texas, United States

Peking Union Medical College Hospital of Chinese Academy of Medical Sciences

🇨🇳

Beijing, China

CHU Bretonneau, Centre Henry Kaplan

🇫🇷

Tours, France

B P Poddar and Medical Research Ltd.

🇮🇳

Kolkata, West Bengal, India

Shatabdi Super Speciality Hospital

🇮🇳

Nashilk, Maharashtra, India

Kaplan Medical Center

🇮🇱

Rehovot, Israel

Policlinico Universitario Campus Bio-Medico

🇮🇹

Roma, Italy

Ospedale San Pietro Fatebenefratelli

🇮🇹

Roma, Italy

National Hospital Organization Beppu Medical Center

🇯🇵

Oita, Beppu-shi, Japan

Iwate Medical University Hospital

🇯🇵

Iwate, Morioka-shi, Japan

Kobe City Medical Center General Hospital

🇯🇵

Hyogo, Japan

Osaka University Hospital

🇯🇵

Osaka, Japan

Jichi Medical University Hospital

🇯🇵

Tochigi, Japan

Toranomon Hospital

🇯🇵

Tokyo, Japan

National Cancer Center, Center for Breast Cancer

🇰🇷

Goyang-si, Gyeonggi-do, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Korea, Republic of

Yonsei University Health System Severance Hospital

🇰🇷

Seoul, Seoul/Korea, Korea, Republic of

University Malaya Medical Centre

🇲🇾

Kuala Lumpur, Malaysia

The Medical Oncology Centre of Rosebank

🇿🇦

Johannesburg, Gauteng, South Africa

Eastleigh Breast Care Centre

🇿🇦

Pretoria, Gauteng, South Africa

University of Witwatersrand Oncology, Donald Gordon Medical Centre

🇿🇦

Johannesburg, Gauteng, South Africa

Hospital Puerta De Hierro

🇪🇸

Majadahonda, Madrid, Spain

Hospital Madrid Norte Sanchinarro Centro Integral Oncológico Clara Campal Ensayos Clínicos

🇪🇸

Sanchinarro, Madrid, Spain

Hospital Universitario Infanta Cristina

🇪🇸

Parla, Madrid, Spain

Hospital Costa del Sol

🇪🇸

Marbella, Malaga, Spain

Hospital de Cruces

🇪🇸

Baracaldo, Vizcaya, Spain

Tumor Center Hirslanden Medical Center

🇨🇭

Aarau, Switzerland

Hospital Universitario Ramón y Cajal

🇪🇸

Madrid, Spain

S.P. Grigoreva Institute of Medical Radiology Department of Chemotherapy

🇺🇦

Kharkiv, Ukraine

Nottingham University Hospital

🇬🇧

Nottingham, United Kingdom

Volyn Regional Oncological Center

🇺🇦

Lutsk, Ukraine

Family Cancer Care

🇺🇸

Memphis, Tennessee, United States

Redwood Regional Medical Group

🇺🇸

Santa Rosa, California, United States

El Paso Cancer Treatment Center

🇺🇸

El Paso, Texas, United States

The Queen Elizabeth Hospital

🇦🇺

North Adelaide, South Australia, Australia

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