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European Sickle Cell Disease Cohort - Hydroxyurea

Completed
Conditions
Sickle Cell Disease
Registration Number
NCT02516579
Lead Sponsor
Theravia
Brief Summary

In the context of the Risk Management Plan (RMP), as requested from Addmedica by the EMEA, to collect information about long-term safety of Siklos® (hydroxycarbamide) when used in patients with Sickle Cell Disease.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
1906
Inclusion Criteria
  • Male or female ambulatory patients, aged 2 years and more (children, adolescents or adults)
  • With symptomatic sickle cell syndrome
  • Treated with Siklos®
  • Having been informed of the study by the initiating physician and consenting to participate to the cohort.
Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
% of Patient-years With MalignanciesDuring the follow-up of participant, up to 10 years
% of Patient-years With Skin UlcerationsDuring the follow-up of participant, up to 10 years

Patients with at least one skin ulceration

% of Patient-years With MyelosuppressionsDuring the follow-up of participant, up to 10 years

Patients with at least one myelosuppression

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (60)

CHU d'Amiens - Picardie - Site sud

🇫🇷

Amiens, France

Centre Hospitalier Robert Ballanger, pédiatrie et néonatalogie

🇫🇷

Aulnay-sous-Bois, France

Hôpital Avicenne; médecine interne

🇫🇷

Bobigny, France

Hôpital Jean Verdier; médecine interne

🇫🇷

Bondy, France

Hôpital Jean Verdier; pédiatrie

🇫🇷

Bondy, France

CHU Bordeaux, urgences pédiatriques

🇫🇷

Bordeaux, France

Hôpital Saint-André

🇫🇷

Bordeaux, France

CHU Estaing, pédiatrie

🇫🇷

Clermont Ferrand, France

Hôpital Louis Mourier; pédiatrie

🇫🇷

Colombes, France

Hôpital Louis Mourier; service de pédiatrie

🇫🇷

Colombes, France

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CHU d'Amiens - Picardie - Site sud
🇫🇷Amiens, France

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